Clinical Trials Sponsored by PTC Therapeutics
Total 8240 results
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PTC TherapeuticsRecruitingA Study to Evaluate the Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)Huntington DiseaseUnited States, Austria, Spain, United Kingdom, Australia, France, Germany, Netherlands, Italy, New Zealand, Canada
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PTC TherapeuticsActive, not recruitingAmyotrophic Lateral SclerosisUnited States, Belgium, Spain, Australia, Germany, Italy, Czechia, France, Netherlands, Japan, Poland, Argentina, Sweden
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PTC TherapeuticsEnrolling by invitationInherited Mitochondrial DiseaseUnited States, France, Spain, United Kingdom, Italy, Poland, Japan
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PTC TherapeuticsCompletedNonsene Mutation Duchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedMitochondrial Diseases | Drug Resistant Epilepsy | Leigh Disease | Leigh Syndrome | Mitochondrial Encephalopathy (MELAS) | Pontocerebellar Hypoplasia Type 6 (PCH6) | Alpers Disease | Alpers SyndromeUnited States, Spain, United Kingdom, Canada, France, Italy, Poland, Sweden, Japan
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PTC TherapeuticsNo longer available
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PTC TherapeuticsCompletedBH4 Deficiency | HyperphenylalaninemiaUnited States
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PTC TherapeuticsTerminatedCOVID-19 | Pneumonia | CoronavirusSpain, United States, Australia, France, Brazil, Mexico, South Africa, Belgium, Colombia, Poland, Portugal
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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PTC TherapeuticsCompletedFriedreich's AtaxiaUnited States
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PTC TherapeuticsCompleted
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PTC TherapeuticsTerminatedCystic FibrosisUnited States, Spain, France, Belgium, United Kingdom, Australia, Brazil, Bulgaria, Canada, Germany, Israel, Italy, Netherlands, Poland, Argentina, Greece
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PTC TherapeuticsTerminatedCystic FibrosisUnited States, France, Spain, Belgium, Israel, Italy, Sweden
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PTC TherapeuticsCompleted
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PTC TherapeuticsWithdrawn
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PTC TherapeuticsCompleted
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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PTC TherapeuticsActive, not recruitingAADC DeficiencyUnited States, Israel, Taiwan
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedLeiomyosarcomaUnited States
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompleted
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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PTC TherapeuticsWithdrawnDuchenne Muscular Dystrophy
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PTC TherapeuticsCompletedHepatic ImpairmentUnited States
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PTC TherapeuticsCompletedHealthy VolunteersUnited States
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States
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PTC TherapeuticsRecruitingHuntington DiseaseAustralia, France, Germany, Netherlands, United Kingdom, Spain, Austria, Canada, Italy, New Zealand
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PTC TherapeuticsActive, not recruitingLeiomyosarcomaUnited States, United Kingdom, France, Italy, Netherlands, Spain, Australia, Canada, Brazil, Germany, Hungary, Poland
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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PTC TherapeuticsCompletedAniridiaUnited States, Canada
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PTC TherapeuticsTerminatedLeukemia, Myeloid, Acute | AMLUnited States
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PTC TherapeuticsCompletedAmyotrophic Lateral SclerosisUnited States
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedRenal ImpairmentUnited States
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PYC TherapeuticsRecruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia