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Search clinical trials for: Genetic lipids disorders
Total 158680 results
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Chung-Hsing WangSanofiNot yet recruiting
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Vital Signs Solutions LtdRecruiting
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The Affiliated Hospital of Xuzhou Medical UniversityRecruitingType 2 Diabetes Mellitus | Susceptibility, GeneticChina
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iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
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Seagen Inc.RecruitingLymphoma, Large B-Cell, Diffuse | Hodgkin Disease | Lymphoma, T-Cell, Peripheral | Lymphoma, Large-Cell, AnaplasticUnited States
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PTC TherapeuticsRecruitingHuntington DiseaseAustralia, France, Germany, Netherlands, United Kingdom, Spain, Austria, Canada, Italy, New Zealand
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Hospital Universitari Vall d'Hebron Research InstituteERN-EuroBloodNet (European Reference Network on Rare Hematological DiseasesRecruitingLeukemia | Anemia | Iron Metabolism Disorders | Anemia, Sickle Cell | Thalassemia | Bleeding Disorder | Myeloma | Lymphoid Neoplasm | Blood Cancer | Bone Marrow Failure | Red Cell Membrane and Enzyme Abnormalities | Myeloma, MalignantSpain
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Jimma UniversityRecruitingDilated CardiomyopathyEthiopia
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Hospices Civils de LyonNot yet recruitingX-Linked Hypophosphatemic Rickets
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St. Olavs HospitalUllevaal University Hospital; Oslo University Hospital; University Hospital of... and other collaboratorsRecruitingEpisodic MigraineNorway
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The Second Hospital of Hebei Medical UniversityRecruitingAcute Ischemic StrokeChina
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Ethos Research & DevelopmentRecruiting
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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ASST Fatebenefratelli SaccoNot yet recruitingGiant Cell Arteritis | Temporal Arteritis | Clonal Hematopoiesis of Indeterminate Potential | Horton Disease | Systemic Vasculitis Primary
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University of Veterinary and Animal Sciences, Lahore...Not yet recruiting
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Ningbo No. 1 HospitalRecruitingCardiovascular Diseases | Mental DisorderChina
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Institute of Hematology & Blood Diseases Hospital...Not yet recruiting
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AstraZenecaParexelRecruiting
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Suzhou Sanegene Bio Inc.Not yet recruiting
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Eye & ENT Hospital of Fudan UniversityShanghai Rehabilitation Institute for the Exceptional ChildrenRecruitingHearing Loss | Genetic Disease | Speech PerceptionChina
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Centre Hospitalier Universitaire de LiegeCentre Hospitalier Régional de la Citadelle; SYSNAVRecruitingAngelman SyndromeBelgium
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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University of CambridgeSanofiRecruiting
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Institut de Recerca Biomèdica de LleidaISCIIIRecruitingMetabolic Syndrome | Weight Loss | Obesity, Morbid | Bariatric Surgery Candidate | Genetic PredispositionSpain
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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First Affiliated Hospital of Wannan Medical CollegeBeijing Tiantan HospitalNot yet recruiting
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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Shanghai Cell Therapy Group Co.,LtdShanghai Mengchao Cancer HospitalNot yet recruitingHyperlipidemia | Sub-healthy | Toxic Metal Ions AccumulationChina
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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BayerRecruitingHemophilia A | Prophylaxis of Bleeding | Treatment of BleedingKorea, Republic of
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy 1France, Canada
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Nanfang Hospital, Southern Medical UniversityRecruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome | Adult ALL | Philadelphia-Positive ALL | IKZF1 Gene MutationChina
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National Cancer Institute (NCI)Not yet recruitingNeurofibromatosis 1 | Nerve Sheath NeoplasmsUnited States
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Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1
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Tampere University HospitalTampere UniversityRecruitingLynch Syndrome | Urothelial CarcinomaCanada, Finland
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Boston University Charles River CampusBoston Children's HospitalNot yet recruiting
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AstraZenecaParexelNot yet recruiting
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National University of SingaporeCollabring Pte LtdNot yet recruitingCardiovascular Diseases
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Assistance Publique - Hôpitaux de ParisNot yet recruitingAcute Chest SyndromeFrance
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Washington University School of MedicineKamuzu University of Health Sciences; Project Peanut Butter; Balchem CorpRecruiting
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Luye Pharma Group Ltd.RecruitingTardive Dyskinesia | Huntington DiseaseChina
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University of PennsylvaniaRecruitingLCAT DeficiencyUnited States
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Hospices Civils de LyonRecruiting
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Rocket Pharmaceuticals Inc.Recruiting
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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University of South AlabamaUniversity of Alabama at Birmingham; University of Nevada, Las Vegas; Rutgers... and other collaboratorsRecruitingDrug ToxicityUnited States
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Kafrelsheikh UniversityRecruiting
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Atamyo TherapeuticsNot yet recruiting