- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: Inherited mitochondrial disease
Total 383628 results
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National Human Genome Research Institute (NHGRI)RecruitingHermansky-Pudlak Syndrome (HPS)United States
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David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
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PfizerActive, not recruiting
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The Hospital for Sick ChildrenFoundation for Prader-Willi ResearchWithdrawn
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia ACzechia, Switzerland, Denmark, Canada, Australia, Austria, France, United Kingdom, Italy, Sweden, Belgium, Brazil, China, Colombia, Greece, Hungary, Norway, Poland, Portugal, Russian Federation, Slovenia, Spain
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Hoffmann-La RocheActive, not recruitingSevere Hemophilia ACanada, United States, United Kingdom, Belgium, Australia, Austria, Brazil, France, Germany, Israel, Italy, South Africa, Spain, Turkey
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National Human Genome Research Institute (NHGRI)CompletedUndiagnosed Disease | Healthy Volunteer (Adult With Typically Developing Child) | Inherited Neurodegenerative Disorders | Inherited Metabolic Disorders (Inborn Errors of Metabolism) | Alzheimer's Disease and Related DementiasUnited States
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East Carolina UniversityCompletedObesity | Sedentary Lifestyle | Insulin ResistanceUnited States
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Mayo ClinicAstellas Pharma Inc; Casimir, LLCCompletedMitochondrial Diseases | Mitochondrial Myopathies | Kearns-Sayre Syndrome | Mitochondrial DNA Mutation | Chronic Progressive External Ophthalmoplegia With MyopathyUnited States
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BayerActive, not recruitingHemophilia ACanada, Japan, Spain, United States, Germany, Sweden, Belgium, Brazil, Greece, Italy, Netherlands, Taiwan, Denmark, Kuwait, Saudi Arabia, United Arab Emirates, Norway, Colombia, Switzerland, Slovenia
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BayerActive, not recruitingHemophilia A | Children | Prophylaxis of Bleeding | Treatment of BleedingCanada, United States, Brazil, Italy, Turkey, Argentina, Norway
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Bioverativ, a Sanofi companyActive, not recruitingHemophilia AUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, China, France, Germany, Greece, Hungary, Ireland, Italy, Japan, Korea, Republic of, Netherlands, Spain, Sweden, Switzerland, Taiwan, Turkey, United Kingdom
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University Hospital, AngersFondation de l'AvenirActive, not recruitingAortic Aneurysm and DissectionFrance
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Astellas Pharma IncTerminatedPrimary Mitochondrial MyopathyUnited States
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Wonju Severance Christian HospitalNational Research Foundation of KoreaCompletedCritical Illness | Acute Kidney Injury | Surgery-ComplicationsKorea, Republic of
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Washington University School of MedicineHoffmann-La Roche; Genentech, Inc.; National Institute on Aging (NIA); Alzheimer...SuspendedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, France, Spain, Ireland, Argentina, Australia, Colombia, Germany, Mexico, Netherlands, Puerto Rico, United Kingdom
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OctapharmaActive, not recruitingVon Willebrand DiseaseUnited States, Moldova, Republic of, Czechia, Germany, North Macedonia, Russian Federation, Ukraine
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Novo Nordisk A/SActive, not recruitingHaemophilia A Without Inhibitors | Haemophilia B Without InhibitorsSpain, United States, Korea, Republic of, United Kingdom, Australia, Lithuania, France, Turkey, India, Estonia, Russian Federation, Ukraine, Mexico, Japan, Serbia, Canada, Croatia, Algeria, Bosnia and Herzegovina, Bulgaria, Denmark and more
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Novo Nordisk A/SActive, not recruitingHaemophilia A With Inhibitors | Haemophilia ASpain, Korea, Republic of, Canada, United Kingdom, United States, Germany, South Africa, Italy, Austria, Belgium, France, Japan
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Novo Nordisk A/SAvailableCongenital HaemophiliaUnited States, Bulgaria, Sweden
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Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...SuspendedEnd Stage Liver Disease | Mitochondrial Diseases | Acute Liver Failure | Respiratory Chain Deficiencies, Mitochondrial | Disorder of Fatty Acid OxidationUnited States, Canada
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BayerUltragenix pharmaceuticalActive, not recruitingHemophilia ANetherlands, United States, Germany, United Kingdom, France, Bulgaria
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Larimar Therapeutics, Inc.Enrolling by invitationFriedreich AtaxiaUnited States
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Genzyme, a Sanofi CompanyCompletedHemophilia A | Hemophilia BBulgaria, United States, United Kingdom, Russian Federation, Switzerland
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Cyclo Therapeutics, Inc.Active, not recruitingNiemann-Pick Disease, Type C1United States, Taiwan, United Kingdom, Israel, Spain, Brazil, Italy, Australia, Turkey, Saudi Arabia, Argentina, Poland, Germany
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Hoffmann-La RocheActive, not recruitingHemophilia A | Mild Hereditary Factor VIII Deficiency Disease Without Inhibitor | Moderate Hereditary Factor VIII Deficiency Disease Without InhibitorUnited States, Netherlands, Belgium, France, Germany, South Africa, Spain, Canada, United Kingdom, Poland
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Duke UniversityWithdrawnCOVID-19 Acute Respiratory Distress SyndromeUnited States
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BayerActive, not recruiting
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PharmasoftCompletedPrimary Open-Angle Glaucoma (POAG)Russian Federation
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St. Jude Children's Research HospitalChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsActive, not recruitingHemophilia BUnited States, United Kingdom
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Universiteit AntwerpenUniversity Hospital, Antwerp; Cliniques universitaires Saint-Luc- Université...CompletedHemophilia A | Hemophilia BBelgium
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CSL BehringEnrolling by invitation
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BayerActive, not recruitingHemophilia ACanada, Spain, United States, Belgium, Italy, Taiwan, Slovenia
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TakedaCompleted
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Vanderbilt University Medical CenterNashville VA Medical CenterActive, not recruitingChronic Kidney DiseasesUnited States
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Khondrion BVJulius Clinical; ProPharma Group; Europees Fonds voor Regionale Ontwikkeling... and other collaboratorsActive, not recruitingMitochondrial Diseases | MELAS | Mitochondrial DNA tRNALeu(UUR) m.3243A<G Mutation | Subacute Necrotizing EncephalomyelopathyNetherlands
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Reneo Pharma LtdTerminatedPrimary Mitochondrial MyopathySpain, Australia, Belgium, Denmark, Canada, United Kingdom, France, Germany, Hungary, Italy, Netherlands, New Zealand
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Investigación en Hemofilia y FisioterapiaCompleted
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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Yale UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Merck...CompletedHealthy ParticipantsUnited States
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Swedish Orphan BiovitrumSyneos HealthActive, not recruitingHemophilia A, SevereGermany, Spain, France, Czechia, Netherlands, Ireland, Austria, Croatia, Greece, Italy, Norway, Slovenia, Sweden, United Kingdom
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Novo Nordisk A/SActive, not recruiting
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Murdoch Childrens Research InstituteCompleted
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Washington University School of MedicineHoffmann-La Roche; National Institute on Aging (NIA); Alzheimer's AssociationTerminatedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, France, Spain, Ireland, Canada, Australia, Puerto Rico, United Kingdom
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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BayerActive, not recruitingHemophilia ASpain, Germany, Austria, Greece, Italy, Slovenia
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CSL BehringActive, not recruiting
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Medexus Pharma, Inc.CompletedHemophilia BTurkey, Brazil, Georgia, Moldova, Republic of, South Africa, Ukraine