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Search clinical trials for: genetic condition
Total 439443 results
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Eye & ENT Hospital of Fudan UniversityShanghai Rehabilitation Institute for the Exceptional ChildrenRecruitingHearing Loss | Genetic Disease | Speech PerceptionChina
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Assiut UniversityNot yet recruiting
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Chinese University of Hong KongRecruiting
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Mahidol UniversityRecruitingLaxity; SkinThailand
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Centre Hospitalier Universitaire de LiegeCentre Hospitalier Régional de la Citadelle; SYSNAVRecruitingAngelman SyndromeBelgium
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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Tenaya TherapeuticsJohns Hopkins University; Mayo ClinicRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States
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Gene SolutionsRecruitingBreast Cancer | Gastric Cancer | Colorectal Cancer | Non Small Cell Lung Cancer | Advanced Cancer | Liver Cancer | Immune Checkpoint InhibitorVietnam
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Swedish Orphan BiovitrumRecruitingHereditary Tyrosinemia, Type IChina
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Hospices Civils de LyonRecruitingPatients With PH1 Treated With Lumasiran in FranceFrance
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University of CambridgeSanofiRecruiting
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Institut de Recerca Biomèdica de LleidaISCIIIRecruitingMetabolic Syndrome | Weight Loss | Obesity, Morbid | Bariatric Surgery Candidate | Genetic PredispositionSpain
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Radboud University Medical CenterSolve FSHDRecruitingMuscular Dystrophy, FacioscapulohumeralNetherlands
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Lassen Therapeutics Inc.RecruitingEye Diseases | Endocrine System Diseases | Thyroid Eye Disease | Graves Ophthalmopathy | Orbital Diseases | Thyroid Associated Ophthalmopathy | Graves Orbitopathy | ProptosisUnited States, United Kingdom, Spain
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Papworth Hospital NHS Foundation TrustInnovate UK; Cystic Fibrosis Trust; US Cystic Fibrosis FoundationRecruitingCystic FibrosisUnited Kingdom
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Sardocor Corp.Not yet recruitingDMD-Associated Dilated Cardiomyopathy
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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BayerRecruitingHemophilia A | Prophylaxis of Bleeding | Treatment of BleedingKorea, Republic of
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SanofiRecruitingDermatitis AtopicJapan, Chile, Canada, Argentina, United States, Turkey, China
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AmgenRecruitingAtopic DermatitisUnited States, Canada
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University College, LondonNot yet recruiting
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy 1France, Canada
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Nanfang Hospital, Southern Medical UniversityRecruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome | Adult ALL | Philadelphia-Positive ALL | IKZF1 Gene MutationChina
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Fondazione Policlinico Universitario Agostino Gemelli...Not yet recruitingPostoperative Complications | Surgical Procedure, Unspecified | Hyperlactatemia | Abdomen DiseaseItaly
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National Cancer Institute (NCI)Not yet recruitingNeurofibromatosis 1 | Nerve Sheath NeoplasmsUnited States
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Shanghai Vitalgen BioPharma Co., Ltd.RecruitingGlutaric Acidemia Type I | Glutaric Aciduria Type IChina
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Samsung Medical CenterNot yet recruitingCharcot-Marie-Tooth Disease, Type 1
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Institute of Hematology & Blood Diseases Hospital...Kanglin BiotechRecruitingTransfusion-dependent Beta-ThalassemiaChina
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Tampere University HospitalTampere UniversityRecruitingLynch Syndrome | Urothelial CarcinomaCanada, Finland
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Boston University Charles River CampusBoston Children's HospitalNot yet recruiting
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Genrix (Shanghai) Biopharmaceutical Co., Ltd.Not yet recruiting
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Boston Children's HospitalCystic Fibrosis FoundationRecruitingCystic FibrosisUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruitingAcute Chest SyndromeFrance
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Luye Pharma Group Ltd.RecruitingTardive Dyskinesia | Huntington DiseaseChina
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University of PennsylvaniaRecruitingLCAT DeficiencyUnited States
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Assistance Publique Hopitaux De MarseilleAix Marseille Université; ALPHENYXNot yet recruitingPsoriasis | Atopic Dermatitis
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Hospices Civils de LyonRecruiting
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Rocket Pharmaceuticals Inc.Recruiting
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Spain, Canada, France, Japan, Australia, Italy, Argentina, Brazil, Germany, United Kingdom
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Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
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Reem Ali ShakerRecruiting
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Atamyo TherapeuticsNot yet recruiting
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Hemab ApSRecruitingGlanzmann ThrombastheniaUnited States, Belgium, France, Italy, Netherlands, United Kingdom
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Foundation For Rare Disease ResearchInstitute for Asthma & Allergy; Virant Diagnostics, Inc.; MedBio Reference Laboratories...Not yet recruitingAngioedema | Urticaria | C1 Inhibitor Deficiency | Angioedemas, Hereditary | Mastocytosis | Indolent Systemic Mastocytosis | Systemic Mastocytoses | ACE Inhibitor-Induced Angioedema
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Diakonhjemmet HospitalRecruiting
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Children's Hospital of Fudan UniversityNot yet recruiting
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Perha PharmaceuticalsFondation Jérôme Lejeune; European Innovation Council; France 2030 programRecruitingHealthy Volunteers | Down Syndrome | Alzheimer's DiseaseFrance
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Thammasat UniversityNot yet recruiting