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Search clinical trials for: inoperable, progressive/symptomatic plexiform neurofibromas (PN) without any alternative therapeutic
Total 92581 results
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University of Alabama at BirminghamChildren's Hospital of Philadelphia; Congressionally Directed Medical Research...Not yet recruitingNeurofibromatosis 1 | Plexiform Neurofibroma
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Saint Vincent's Hospital, KoreaRecruitingCoronary Artery Disease | Dyslipidemias | Primary PreventionKorea, Republic of
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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AstraZenecaRecruitingNeurofibroma, PlexiformChina
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Nanjing First Hospital, Nanjing Medical UniversityRecruiting
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Hanmi Pharmaceutical Company LimitedNot yet recruiting
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Hopital Nord Franche-ComteRecruitingDiabete Mellitus | Insulin Dependent DiabetesFrance
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iRegene Therapeutics Co., Ltd.Recruiting
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Verve Therapeutics, Inc.RecruitingHeterozygous Familial Hypercholesterolemia | Premature Coronary Heart DiseaseUnited Kingdom, Canada
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Johns Hopkins UniversityNeurofibromatosis Therapeutic Acceleration ProgramRecruitingCutaneous Neurofibroma | NF1 | MonotherapyUnited States
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Kinnov TherapeuticsNot yet recruitingAlcohol Use Disorder
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Mitsubishi Tanabe Pharma America Inc.RecruitingErythropoietic Protoporphyria (EPP) | X-Linked Protoporphyria (XLP)Spain, United States, France, Japan, United Kingdom, Italy, Australia, Poland, Bulgaria, Czechia, Netherlands
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Eli Lilly and CompanyRecruiting
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Natural Wellness EgyptNot yet recruitingDiabetes Mellitus, Type 2
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PYC TherapeuticsRecruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Ikaria Bioscience Pty LtdSHANGHAI RONA Therapeutics Co.,Ltd.RecruitingTo Reduce the LDL-C Level in Hypercholesteremia PatientsChina
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Dr. med. Marcus HerdenerUniversity of Zurich; University of Vienna; University of Campania "Luigi Vanvitelli...RecruitingCocaine Use Disorder | Cocaine DependenceSwitzerland
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Trishula Therapeutics, Inc.AbbVieRecruitingPancreatic CancerUnited States, Korea, Republic of
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Shanghai Juncell TherapeuticsRecruitingMelanoma | Efficacy | Adverse Drug Event | Safety | Tumor Infiltrating LymphocytesChina
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, Germany
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AceLink Therapeutics, Inc.Tigermed Consulting Co., LtdRecruiting
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Eli Lilly and CompanyRecruitingType 2 DiabetesUnited States, Japan, China, Puerto Rico, Romania, Brazil
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Memorial Sloan Kettering Cancer CenterRecruitingSolid Tumor | Neuroblastoma | Solid Tumor, Adult | Primary Brain Tumor | Solid Carcinoma | Low-grade Glioma | Central Nervous System Tumor | Refractory Cancer | CNS Tumor, Adult | CNS Tumors | NF1 | Plexiform Neurofibroma | CNS Tumor, Childhood | Optic Pathway Gliomas | MAP Kinase Family Gene MutationUnited States
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Instituto Nacional de Ciencias Medicas y Nutricion...Not yet recruitingObesity | Iron Deficiency Anemia
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Genentech, Inc.RecruitingHepatocellular CarcinomaUnited States, Puerto Rico
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Department of Nephrology Clinic Ottakring ViennaRecruitingDiabetes Mellitus | Chronic Kidney Diseases | PreDiabetes | Overweight and ObesityAustria
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Sigrid Therapeutics ABRecruitingOverweight or ObesitySlovakia, Poland, Romania
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Starton Therapeutics, IncRecruitingMultiple MyelomaUnited States
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Cancer Institute and Hospital, Chinese Academy...The First Affiliated Hospital with Nanjing Medical University; Fujian Cancer... and other collaboratorsRecruitingEsophageal NeoplasmsChina
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Gilead SciencesRecruitingSolid TumorsAustralia, United States, Canada
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Yale UniversityNational Institute on Alcohol Abuse and Alcoholism (NIAAA)Not yet recruitingAlcohol-Related Disorders | Alcohol Use | Alcohol Use Disorder (AUD)United States
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Fayoum UniversityCairo University; NewGiza UniversityNot yet recruitingDiabetes Mellitus Without Complication
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Jerry Vockley, MD, PhDAcer Therapeutics Inc.RecruitingMedium-chain Acyl-CoA Dehydrogenase DeficiencyUnited States
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Assistance Publique - Hôpitaux de ParisRecruitingAdult Patients Who Declare an Allergy to Penicillin During Anaesthetic Consultation Without Any Allergy Work up That Could Confirm This Declaration | Good Comprehension of French LanguageFrance
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Fondazione Policlinico Universitario Agostino Gemelli...Not yet recruiting
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Novo Nordisk A/SRecruitingType 2 Diabetes MellitusKorea, Republic of, United States, Hungary, Serbia, Spain, China, Australia, Finland, United Kingdom, Italy, Denmark, Canada, Taiwan, Poland, Germany, Sweden, South Africa, India, Argentina, Brazil, Bulgaria, Japan, Mexico, Turkey, Greece, Colomb... and more
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University Hospital of FerraraRecruitingAortic Stenosis, Severe | Amyloidosis CardiacItaly
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Carmot Therapeutics, Inc.RecruitingOverweight | Type 1 Diabetes Mellitus | ObeseUnited States
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Peking University Third HospitalRecruitingDiabetic Foot | TherapeuticsChina
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Action Against Hunger USAUniversity of Washington; Ethiopian Public Health InstituteNot yet recruitingSevere Acute Malnutrition
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Federico II UniversityRecruitingType 2 DiabetesItaly
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Urica Therapeutics Inc.RecruitingHyperuricemia | GoutUnited States
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Action Against Hunger USAUniversity of Washington; Ethiopian Public Health InstituteNot yet recruitingModerate Acute Malnutrition
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Rise Therapeutics LLCRecruitingDiabetes Mellitus, Type 1 | Type 1 Diabetes | Type 1 Diabetes (Juvenile Onset)United States
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Astellas Pharma Global Development, Inc.Recruiting