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- US Clinical Trials Registry
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Search clinical trials for: Glycogen Storage Disorders
Total 146361 results
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Masonic Cancer Center, University of MinnesotaCompletedWolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Sanfilippo Syndrome | GM1 Gangliosidosis | Globoid Cell Leukodystrophy | Tay Sachs Disease | Sandhoffs Disease | I-Cell DiseaseUnited States
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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Duke UniversityCompleted
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Duke UniversityCompleted
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Dwight Koeberl, M.D., Ph.D.Completed
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University of MinnesotaGenzyme, a Sanofi CompanyWithdrawnNeuropathic Pain | Fabry DiseaseUnited States
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Rigshospitalet, DenmarkCompleted
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PfizerTerminatedCardiovascular DiseaseUnited States, Finland, Netherlands, Spain, Belgium, Germany, Czechia, Switzerland, Denmark, Australia, United Kingdom, Korea, Republic of, Hungary, Israel, Poland, Taiwan, Mexico, Turkey, Ireland, Canada, New Zealand, South Africa, Brazi... and more
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University of MinnesotaGE HealthcareCompletedParkinson Disease | Gaucher Disease | Idiopathic Rapid Eye Movement Sleep DisorderUnited States
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National Taiwan University HospitalActelionUnknown
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Nationwide Children's HospitalOhio State UniversityCompletedHernia | Sleep Disordered Breathing | Hypospadias | Tonsillitis | Hydrocele | Circumcision | Undescended TesticleUnited States
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University of California, IrvineGenzyme, a Sanofi CompanyCompletedPompe DiseaseUnited States
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Groupe Hospitalier Diaconesses Croix Saint-SimonTerminated
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Amicus TherapeuticsTerminatedLate-onset Pompe DiseaseUnited States, Canada, Australia, Belgium
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Alexion PharmaceuticalsCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited Kingdom, France, United States, Egypt, Ireland
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Orpha LabsUnknownGlycogen Storage Disease, Type 14Turkey
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Lysosomal and Rare Disorders Research and Treatment...UnknownParkinson Disease | Gaucher DiseaseUnited States
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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Lysosomal and Rare Disorders Research and Treatment...UnknownLysosomal Storage DiseasesUnited States
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Lysosomal and Rare Disorders Research and Treatment...UnknownLysosomal Storage DiseasesUnited States
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National Cancer Institute (NCI)WithdrawnMultiple Myeloma | Non-Hodgkin Lymphoma | Acute Leukemias | Chronic Myelogous Leukemia/Other Leukemia | MDS/MPS
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Amicus TherapeuticsCompletedFabry DiseaseCanada, Belgium, United States, Australia, Netherlands
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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University of FloridaAmicus TherapeuticsTerminatedPompe Disease | Hypersensitivity Reaction
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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Amicus TherapeuticsCompletedFabry DiseaseFrance, Austria, United States, Belgium, Japan, United Kingdom, Denmark, Brazil, Australia, Italy
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Amicus TherapeuticsCompletedFabry DiseaseAustralia, Brazil
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Mansoura University Children HospitalUnknownHCV | Gaucher DiseaseEgypt
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Italy, Spain, Turkey, Brazil, Canada, United Kingdom, France, Poland, Australia, Egypt, Argentina, Denmark
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Amicus TherapeuticsCompletedFabry DiseaseUnited States
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Ulla Feldt-RasmussenCompleted
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Ulla Feldt-RasmussenCompleted
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
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Amicus TherapeuticsTerminatedFabry DiseaseAustralia, United States, Italy, Spain, Belgium, Turkey, Brazil, Argentina, United Kingdom, Denmark, France, Canada, Egypt
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Amicus TherapeuticsCompleted
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
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PfizerNo longer availableGaucher DiseaseUnited States, Israel
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Amicus TherapeuticsCompletedFabry DiseaseFrance, United Kingdom
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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Rennes University HospitalCompleted
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Amicus TherapeuticsTerminated
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited Kingdom, Israel, South Africa, United States