Clinical Trials Sponsored by Orphan Therapeutics
Total 6636 results
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University of Southern CaliforniaNational Institute on Aging (NIA); Northern California Institute of Research... and other collaboratorsCompletedMild Cognitive Impairment (MCI) | Alzheimer's Disease (AD) | Significant Memory Concern (SMC) | Early Mild Cognitive Impairment (EMCI) | Late Mild Cognitive Impairment (LMCI)United States, Canada
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Yale UniversityNational Institute of Mental Health (NIMH); University of Pennsylvania; Columbia... and other collaboratorsActive, not recruitingEarly Course Schizophrenia Spectrum DisorderUnited States
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Memorial Sloan Kettering Cancer CenterMerck Sharp & Dohme LLC; Mirati Therapeutics Inc.; Astex Pharmaceuticals, Inc.; Stand Up To Cancer and other collaboratorsActive, not recruiting
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Cyprium Therapeutics, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedMenkes Disease | Occipital Horn Syndrome | Unexplained Copper DeficiencyUnited States
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University of Southern CaliforniaNational Institute on Aging (NIA); Northern California Institute of Research... and other collaboratorsRecruitingDementia | Alzheimer Disease | Mild Cognitive ImpairmentUnited States, Canada
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University of OxfordOxford Brookes University; Oxford University Hospitals NHS Trust; Scholar Rock... and other collaboratorsNot yet recruiting
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Invex Therapeutics Ltd.Premier Research Group plc; University Hospitals Birmingham Neuro Ophthalmology... and other collaboratorsTerminatedIdiopathic Intracranial HypertensionIsrael, Germany, Australia, United States, United Kingdom, New Zealand
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Better TherapeuticsUniversity of Colorado, Denver; CPC Clinical Research; Ascension Health; Department... and other collaboratorsActive, not recruiting
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The Queen Elizabeth HospitalUniversity of Adelaide; University of South Australia; Basil Hetzel Institute... and other collaboratorsCompletedSmoking | AddictionAustralia
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University Hospital, LilleRegional Agency of Sante Nord Pas-de-Calais; OméDIT (Observatory of Medicines...Not yet recruitingAcute Renal Failure | Patient Acceptance of Health Care
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University of Southern CaliforniaNational Institute on Aging (NIA); Northern California Institute of Research... and other collaboratorsRecruitingMild Cognitive Impairment (MCI) | Alzheimer's Disease (AD)United States, Canada
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University of OxfordCancer Institute and Hospital, Chinese Academy of Medical Sciences; Qidong... and other collaboratorsCompletedLiver Diseases | Hepatitis B | Liver NeoplasmsUnited Kingdom, China
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Addis Ababa UniversityCenter for Innovative Drug Development and Therapeutic Trials for Africa,... and other collaboratorsNot yet recruiting
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Universitaire Ziekenhuizen KU LeuvenKU Leuven; Hospital Clinic of Barcelona; MDx Health; Biomedical Research Foundation... and other collaboratorsNot yet recruiting
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Cambridge University Hospitals NHS Foundation TrustGlaxoSmithKline; National Institute for Health Research, United Kingdom; Kidney... and other collaboratorsRecruiting
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William LeeMedical University of South Carolina; National Institute of Diabetes and Digestive... and other collaboratorsCompletedAcute Liver Failure | Acute Liver InjuryUnited States
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Morten Mau-SoerensenHospices Civils de Lyon; Gustave Roussy, Cancer Campus, Grand Paris; Institut... and other collaboratorsUnknownThymoma | Advanced Thymic Epithelial TumourDenmark, France
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University of Southern CaliforniaMedical University of South Carolina; National Institute on Aging (NIA); Alzheimer... and other collaboratorsRecruitingDementia | AgitationUnited States
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National Institute of Allergy and Infectious Diseases...National Heart, Lung, and Blood Institute (NHLBI); Genentech, Inc.; Rho Federal... and other collaboratorsTerminatedCardiac Allograft Vasculopathy | Heart Transplant RecipientsUnited States
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Talaris Therapeutics Inc.Duke University; University of Florida; St. Christopher's Hospital for Children; Hahnemann University Hospital and other collaboratorsCompletedSickle Cell DiseaseUnited States
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University of Colorado, DenverEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingMental Disorders | Autism Spectrum DisorderUnited States
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University Health Network, TorontoBayer; AstraZeneca; Amgen; AnHeart Therapeutics Inc.; Applied Health Research Centre and other collaboratorsRecruitingCancer | Malignancies Multiple | Malignant Solid Tumor | Cancer, Therapy-Related | Molecular Sequence Variation | Genetic Alteration | Gene Fusion | Receptor Tyrosine Kinase Gene Mutation | RTK Family Gene Mutation | Ras (Kras or Nras) Gene MutationCanada
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University Hospital Southampton NHS Foundation...Cancer Research UK; The Christie NHS Foundation Trust; Celldex Therapeutics; Oxford... and other collaboratorsActive, not recruitingB Cell LymphomaUnited Kingdom
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Frontera TherapeuticsPeking Union Medical College Hospital; The First Affiliated Hospital of Soochow... and other collaboratorsNot yet recruitingNeovascular Age-related Macular Degeneration
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Xuanwu Hospital, BeijingH. Lundbeck A/S; Hoffmann-La Roche; Genentech, Inc.; Life Molecular Imaging SA; APRINOIA... and other collaboratorsRecruitingAlzheimer DiseaseChina
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Frantz Viral Therapeutics, LLCM.D. Anderson Cancer Center; University of Michigan; The Cleveland Clinic; Amarex... and other collaboratorsRecruitingHPV Infection | CIN 2/3 | Cervical Dysplasia | Pre-Cancerous Dysplasia | HPV Related DiseaseUnited States
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National Institute of Dental and Craniofacial Research...National Institute of Neurological Disorders and Stroke (NINDS); Sorrento Therapeutics...RecruitingPalliative Care | Intractable PainUnited States
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Minneamrita Therapeutics LLCCancer Research UK; Barts & The London NHS Trust; Queen Mary University of London and other collaboratorsCompletedPancreatic CancerUnited States
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PIQUR Therapeutics AGHospital Universitari Vall d'Hebron Research Institute; Institut Català d'Oncologia and other collaboratorsCompletedMetastatic Breast CancerSpain, United Kingdom
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...CompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Public Health Service South LimburgMaastricht University; National Institute for Public Health and the Environment... and other collaboratorsEnrolling by invitation
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University of California, Los AngelesNational Institute of Allergy and Infectious Diseases (NIAID); National Heart... and other collaboratorsCompleted
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsApproved for marketingDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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ScandiBio Therapeutics ABGöteborg University; Helsinki University Central Hospital; Sahlgrenska University... and other collaboratorsUnknownNon-alcoholic Fatty Liver Disease (NAFLD)Turkey
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... and other collaboratorsActive, not recruitingMucopolysaccharidosis Type IIIAUnited Kingdom
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsTerminatedDiGeorge Anomaly
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | DiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge SyndromeUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Anomaly | Complete DiGeorge Anomaly | Complete DiGeorge Syndrome | Complete Atypical DiGeorge Anomaly | Complete Atypical DiGeorge SyndromeUnited States
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Enzyvant Therapeutics GmBHNational Institute of Allergy and Infectious Diseases (NIAID); Eunice Kennedy... and other collaboratorsCompletedDiGeorge Syndrome | Complete Typical DiGeorge AnomalyUnited States
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Omar JawdatRare Diseases Clinical Research Network; Terra Biological LLC; Clinical Research...Unknown
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Tuscaloosa Research & Education Advancement CorporationBaylor College of Medicine; James J. Peters Veterans Affairs Medical Center; Acorda... and other collaboratorsCompletedPosttraumatic Stress DisorderUnited States
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Johns Hopkins UniversityEli Lilly and Company; National Heart, Lung, and Blood Institute (NHLBI); The... and other collaboratorsCompletedSystemic Sclerosis | Pulmonary Arterial Hypertension | Pulmonary Hypertension | Connective Tissue Disease | Scleroderma Spectrum of DiseasesUnited States
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Pharmacotherapies for Alcohol and Substance Use...Yale University; United States Department of Defense; VA Connecticut Healthcare... and other collaboratorsNot yet recruitingEffect of Sublingual Formulation of Dexmedetomidine Hydrochloride (HCl) (BXCL501) - Outpatient StudyPost Traumatic Stress Disorder (PTSD) | Alcohol Use Disorder (AUD)United States
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Pharmacotherapies for Alcohol and Substance Use...Yale University; United States Department of Defense; VA Connecticut Healthcare... and other collaboratorsCompletedPost Traumatic Stress Disorder (PTSD) | Alcohol Use Disorder (AUD)United States
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ERP Biomarker Qualification ConsortiumMerck Sharp & Dohme LLC; Novartis; Takeda; H. Lundbeck A/S; Astellas Pharma Inc; Alkermes... and other collaboratorsCompleted
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Canadian Cancer Trials GroupCanadian Cancer Society (CCS); ATGen Canada Inc; Ontario Institute for Cancer... and other collaboratorsActive, not recruiting
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GCP-Service International West GmbHSaint-Louis Hospital, Paris, France; University of Florence; Medical University... and other collaboratorsNot yet recruitingLow Risk Myelodysplastic SyndromesSpain, Poland, Italy, Germany, France