- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Congenital Malformations
Total 9272 results
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Edimer PharmaceuticalsCompletedX-linked Hypohidrotic Ectodermal DysplasiaUnited States
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Tel-Aviv Sourasky Medical CenterUnknownCraniosynostosis Repair | Untethering of Cord
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Emory UniversityTerminatedCongenital DisordersUnited States
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Iron Overload | Hemoglobinopathies | Thalassemia | Beta-Thalassemia | Hemochromatosis | Anemia (Iron-Loading)
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Tel-Aviv Sourasky Medical CenterUnknownStridor | Laryngomalacia
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Shire Regenerative Medicine, Inc.TerminatedEpidermolysis BullosaUnited States, Spain, Austria, Canada, France, Germany, Poland, Portugal
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Emory UniversityCompletedPrimary Condition: Heart Defects Requiring Surgery With CPBUnited States
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Emory UniversityCompletedChildren With Heart DefectsUnited States
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Mayo ClinicCompleted
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Tongji HospitalCompletedHirschsprung Disease
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The Catholic University of KoreaCompletedPain | Side EffectsKorea, Republic of
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Applied GeneticsUnknownPrecancerous ConditionUnited States, Germany, United Kingdom
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Taipei Medical University WanFang HospitalCompleted
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University Hospital, MontpellierMinistry of Health, FranceCompletedAutosomal Dominant Retinitis PigmentosaFrance
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Massachusetts General HospitalNational Institutes of Health (NIH)UnknownHealthy | Fragile X SyndromeUnited States
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Taipei Medical University WanFang HospitalCompletedPolycystic Ovary Syndrome, | Insulin Resistance, | Cardiovascular Disease. | Hyperandrogenism, | Metabolic Syndrome,Taiwan
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University of AarhusDanish Cancer Society; Arvid-Nilsson FoundationUnknown
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SangartWithdrawnSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseFrance, United Kingdom, Netherlands, Turkey, Bahrain, Belgium, Brazil, Lebanon, Qatar
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University of CalgaryUniversity of Alberta; Heart and Stroke Foundation of CanadaUnknownStroke | Cerebral PalsyCanada
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Centre Hospitalier Universitaire DijonUnknown
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Janssen-Cilag TurkeyCompleted
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UCSF Benioff Children's Hospital OaklandDepartment of Health and Human Services; FDA Office of Orphan Products DevelopmentCompleted
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Emory UniversityTerminatedSALT: Alternative Donor Bone Marrow and Cord Blood Transplantation for High Risk Sickle Cell DiseaseSickle Cell DiseaseUnited States
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University Hospital Schleswig-HolsteinWithdrawnDisorders of Sex Development | Congenital Adrenal Hyperplasia | Adrenal Insufficiency | Congenital Adrenal Hypoplasia | Mineralocorticoid Deficiency | Intersex
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Tongji HospitalAnhui Provincial HospitalCompletedProbiotics | Hirschsprung's Disease Associated Enterocolitis
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Meir Medical CenterWithdrawn
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The Hospital for Sick ChildrenCompleted
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Cancer Research UKUnknownLymphoma | Kidney Cancer | Pancreatic Cancer | Esophageal Cancer | Brain and Central Nervous System Tumors | Bladder Cancer | Intraocular Melanoma | Melanoma (Skin) | Transitional Cell Cancer of the Renal Pelvis and UreterUnited Kingdom
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National Taiwan University HospitalCompleted
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SangartCompletedSickle Cell Disease | Anemia, Sickle Cell | Sickle Cell Anemia | Hemoglobin SC Disease | Sickle Cell Disorders | Sickle Cell Hemoglobin C DiseaseUnited Kingdom, France, Jamaica, Lebanon
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Ellipse Technologies, Inc.CompletedThoracic Insufficiency SyndromeHong Kong, New Zealand, Finland, Turkey, Egypt, Italy, United Kingdom
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The Hospital for Sick ChildrenThe Physicians' Services Incorporated FoundationCompleted
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Dhanunjaya Lakkireddy, MD, FACCCompletedLeft Ventricular Pacing LeadsUnited States
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Children's Hospital Medical Center, CincinnatiWithdrawn
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Assistance Publique - Hôpitaux de ParisCompletedDrepanocytic Men Treated by Hydroxyurea for the First TimeFrance
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Children's Hospitals and Clinics of MinnesotaUnknown
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Assistance Publique - Hôpitaux de ParisMallinckrodtCompletedSickle Cell Disease | Acute Chest SyndromeFrance
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Janssen-Cilag International NVCompletedSchizophreniaPoland, Israel, Romania, Germany, Lithuania, Croatia, France
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Seaside Therapeutics, Inc.Completed
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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UCSF Benioff Children's Hospital OaklandCompletedVaso-occlusive Pain EpisodesUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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University of MinnesotaNovartisCompleted
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Connecticut Children's Medical CenterCompletedPain | Sickle Cell DiseaseUnited States
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Dana-Farber Cancer InstituteMassachusetts General Hospital; Beth Israel Deaconess Medical Center; Emory University and other collaboratorsCompletedSickle Cell Disease | Hemoglobinopathies | ThalassemiaUnited States
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Connecticut Children's Medical CenterCompleted