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Clinical Trials Sponsored by PTC Therapeutics
Total 8240 results
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PYC TherapeuticsRecruitingRetinitis Pigmentosa | Eye Diseases, Hereditary | Retinal Dystrophies | Retinal Dystrophy Rod | Retinal Dystrophy Rod ProgressiveUnited States, Australia
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Nationwide Children's HospitalPTC TherapeuticsActive, not recruitingHigh Grade Glioma | Diffuse Intrinsic Pontine GliomaUnited States
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NYU Langone HealthPTC TherapeuticsCompleted
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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PYC TherapeuticsRecruitingRetinal Dystrophy | PRPF31 Mutationassociated Retinal Dystrophy | RP11United States
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University of OklahomaPTC TherapeuticsCompletedOvarian CancerUnited States
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PTC TherapeuticsCystic Fibrosis FoundationCompletedCystic FibrosisUnited States, France, Belgium, United Kingdom, Spain, Canada, Germany, Israel, Italy, Netherlands, Sweden
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PTC TherapeuticsICON Development SolutionsCompletedHealthy VolunteersUnited States
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PTC TherapeuticsCystic Fibrosis FoundationCompletedCystic FibrosisUnited States, France, Belgium, Spain, Canada, Germany, Israel, Italy, Netherlands, Sweden, United Kingdom
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PTC TherapeuticsAxio Research. LLCCompleted
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Hoffmann-La RochePTC TherapeuticsCompletedMuscular Atrophy, SpinalUnited States
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Silence Therapeutics plcRecruitingPolycythemia VeraUnited States, Australia, Malaysia, Bulgaria, Poland
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Silence Therapeutics plcActive, not recruitingCardiovascular Diseases | Atherosclerosis | Lipoprotein(a)Australia, Czechia, Denmark, Netherlands, Slovakia, South Africa, United Kingdom
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Silence Therapeutics plcWithdrawnNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic SyndromeUnited Kingdom, Bulgaria
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedHemophilia A | Hemophilia BUnited States, Canada, France, Italy
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Celsus Therapeutics PLCTerminatedAtopic DermatitisIsrael
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland
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Trek Therapeutics, PBCCompletedChronic Hepatitis C | Hepatitis C Genotype 1 | Hepatitis C (HCV) | Hepatitis C Viral InfectionUnited States, New Zealand
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Trek Therapeutics, PBCCompletedChronic Hepatitis C | Hepatitis C (HCV) | Hepatitis C Genotype 4 | Hepatitis C Viral InfectionUnited States
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Silence Therapeutics plcCompletedNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic Syndrome | Very-Low Risk Myelodysplastic SyndromeThailand, Israel, Jordan, United Kingdom, Germany, Italy, Malaysia
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Silence Therapeutics plcCompletedHealthy VolunteersUnited Kingdom
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e-Therapeutics PLCCompleted
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e-Therapeutics PLCCompletedMajor Depressive DisorderUnited Kingdom
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e-Therapeutics PLCCompletedCancer | Pharmacokinetics | Tolerability | SafetyUnited Kingdom
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e-Therapeutics PLCUnknownHepatocellular Carcinoma | Pancreatic CancerGermany, Poland, Spain, United Kingdom
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PTC TherapeuticsUnited States Department of DefenseCompletedMetastatic Breast CancerUnited States
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PTC TherapeuticsUnited States Department of DefenseTerminated
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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Mediar TherapeuticsICON plcRecruiting
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CytoMed Therapeutics Pte LtdUnknownSarcoma | Nasopharyngeal Carcinoma | Gastric Cancer | Colorectal Cancer | Prostate Cancer | Triple Negative Breast CancerMalaysia
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Cyto Therapeutics Pty LimitedUnknownParkinson DiseaseAustralia
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Havah Therapeutics Pty LtdCompletedMammographic DensityAustralia
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Diceros TherapeuticsDiceros Therapeutics Australia Pty LtdNot yet recruitingHealthy VolunteersAustralia
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Ripple Therapeutics Pty LtdNovotech (Australia) Pty LimitedActive, not recruitingDiabetic Macular Oedema | Retinal Vein Occlusion With Macular OedemaAustralia, New Zealand, Hong Kong, Canada
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Mozart Therapeutics Australia Pty LtdNot yet recruitingType 1 Diabetes | Celiac Disease | Healthy VolunteersAustralia
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Zhejiang UniversityUTC Therapeutics Inc.RecruitingMesothelin-positive Advanced Malignant Solid TumorsChina
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Ruijin HospitalUTC Therapeutics Inc.RecruitingRefractory Malignant Solid NeoplasmChina
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ES Therapeutics Australia Pty LtdRecruitingDrug Resistant EpilepsyAustralia
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United TherapeuticsLung Biotechnology PBCTerminatedChronic Obstructive Pulmonary Disease | Pulmonary HypertensionUnited States, Israel
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Silence Therapeutics plcMedpace, Inc.CompletedDyslipidemias | Hyperlipidemias | Elevated Lp(a)United States, Australia, United Kingdom, Netherlands
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ES Therapeutics Australia Pty LtdWithdrawn
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Havah Therapeutics Pty LtdGTxCompletedMammographic DensityAustralia
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Multitude Therapeutics (Australia) Pty LtdNot yet recruiting
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Multitude Therapeutics (Australia) Pty LtdRecruiting
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Intelligem Therapeutics Australia Pty Ltd.Not yet recruitingHyperuricemia | Hypouricemia, Renal