- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Enzyme Replacement Therapy
Total 95089 results
-
VA Office of Research and DevelopmentCompletedSmoking | Human Immunodeficiency VirusUnited States
-
Amicus TherapeuticsCompletedFabry DiseaseJapan, Taiwan, Turkey, United States, Brazil
-
PfizerCompleted
-
Sara ThønningsWithdrawn
-
Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedNasopharyngeal Carcinoma | Current Smoker | Head and Neck Squamous Cell Carcinoma | Oropharyngeal Squamous Cell Carcinoma | Hypopharyngeal Squamous Cell Carcinoma | Laryngeal Squamous Cell Carcinoma | Oral Cavity Squamous Cell CarcinomaUnited States
-
Damascus UniversityUnipharma, HamaPharma, Almujtahed hospitalCompleted
-
Shaare Zedek Medical CenterCompletedGaucher Disease, Type 1Israel
-
Galenicum HealthCompletedDiabetes Mellitus, Type 2 | BioequivalenceCanada
-
SanofiApproved for marketing
-
National Taiwan University HospitalSanofiCompleted
-
M.D. Anderson Cancer CenterCompletedProstate Adenocarcinoma | Stage IIIA Prostate Cancer AJCC v8 | Stage IIC Prostate Cancer AJCC v8 | Stage IIIC Prostate Cancer AJCC v8 | Stage IIB Prostate Cancer AJCC v8United States
-
Nottingham University Hospitals NHS TrustUniversity of Washington; Seattle Children's Hospital; The Leeds Teaching Hospitals... and other collaboratorsActive, not recruitingLung Diseases | Cystic Fibrosis | Digestive System Disease | Pancreatic Disease | Distal Intestinal Obstruction Syndrome | Pancreatic Enzyme Abnormality | Gastrointestinal System DiseaseUnited Kingdom
-
First Wave Bio, Inc.CompletedCystic Fibrosis (CF) | Exocrine Pancreatic Insufficiency (EPI)United States, Poland
-
University of Pharmacy, YangonCompletedCryptococcal MeningitisMyanmar
-
Organon and CoCompleted
-
Federal Research and Clinical Center of Physical-Chemical...Moscow State University of Medicine and DentistryCompletedChronic Pancreatitis | Pancreatic Exocrine InsufficiencyRussian Federation
-
HK inno.N CorporationCompletedHelicobacter Pylori InfectionKorea, Republic of
-
University of Maryland, BaltimoreCompletedRenal Insufficiency | Renal Failure | Acute Kidney Injury | PharmacokineticsUnited States
-
University Hospital, GhentKom Op Tegen Kanker; Anticancer Fund, BelgiumCompletedStudy of Pembrolizumab, Radiation and Immune Modulatory Cocktail in Cervical/Uterine Cancer (PRIMMO)Cervical Cancer | Endometrial Cancer | Uterine CancerBelgium
-
Hasan Kalyoncu UniversityCompleted
-
ShireCompletedFabry DiseaseCanada, United States
-
BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
-
Gachon University Gil Oriental Medical HospitalCatholic Kwandong UniversityCompletedTotal Knee Replacement | ManipulationKorea, Republic of
-
ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
-
ShireCompleted
-
ShireCompleted
-
ShireCompletedGaucher DiseaseIsrael, Romania, Serbia
-
ShireCompletedGaucher Disease, Type 3Egypt, India, Tunisia
-
ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
-
ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
-
ShireCompletedGaucher Disease, Type 1United States, Israel, Argentina, India, Korea, Republic of, Paraguay, Poland, Russian Federation, Spain, Tunisia, United Kingdom
-
ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
-
ShireCompletedGaucher DiseaseUnited States, Israel, United Kingdom, Poland, Spain
-
ShireCompleted
-
ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
-
ShireCompletedSanfilippo SyndromeUnited States, Spain, United Kingdom, Argentina, France, Germany, Italy, Netherlands
-
ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
-
ShireCompletedFabry DiseaseUnited States, Slovenia, Australia, Finland, Poland, Czechia, United Kingdom
-
ShireCovance; PRA Health Sciences; PharmaNetCompletedMucopolysaccharidosis II | Hunter Syndrome | MPS IIBrazil, Poland, Taiwan
-
ShireNo longer available
-
ShireApproved for marketingGaucher Disease, Type 1United States
-
Duke UniversityCompletedAlcohol Drinking | Smoking CessationUnited States
-
Julio RamirezUniversity of LouisvilleTerminatedOsteomyelitisUnited States
-
AbbVieVIVUS LLC; Cystic Fibrosis Foundation; Digestive Care, Inc.; Nestle Health ScienceTerminated
-
Assistance Publique - Hôpitaux de ParisAction Research Group; Bristol-Meyers Squibb & PfizerCompletedSymptomatic Aortic Stenosis | Eligible for Transcatheter Aortic Valve ReplacementFrance, Germany, Italy, Spain
-
Columbia UniversityAlpha-1 Foundation; Stony Wold-Herbert Fund, Inc.CompletedChronic Obstructive Pulmonary Disease | Emphysema | Alpha-1 Antitrypsin DeficiencyUnited States
-
Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
-
AbbVieJanssen Research & Development, LLC; Forest LaboratoriesCompleted
-
The Royal Wolverhampton Hospitals NHS TrustCompletedEnd Stage Renal Disease (ESRD) | Chronic Kidney Disease (CKD) | Acute Kidney Injury (AKI) | Estimated Glomerular Filtration Rate (eGFR) | Neutrophil Gelatinase-associated Lipocalin (NGAL) | Serum Creatinine (SCr) | Urine Creatinine (UCr) | Urine Albumin (UAlb)United Kingdom