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Search clinical trials for: GNE myopathy
Total 337 results
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Mads Peter Godtfeldt StemmerikRecruiting
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Eduardo N. ChiniRecruitingMitochondrial MyopathyUnited States
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Children's Hospital of PhiladelphiaUnited States Department of DefenseRecruitingMitochondrial Diseases | Mitochondrial MyopathiesUnited States
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyUnited States, Germany, Spain, Korea, Republic of, Austria, Turkey, Lithuania, Australia, Thailand, Serbia, Poland, Italy, France, Netherlands, Argentina, United Kingdom, Georgia, Belgium, Bulgaria, Canada, Cyprus, Denmark, Greece, Hu... and more
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Qilu Hospital of Shandong UniversityRecruitingConnective Tissue Diseases | Interstitial Lung Disease | PirfenidoneChina
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University Hospital, Clermont-FerrandRecruitingMetabolic MyopathyFrance
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Peking University People's HospitalRecruitingIdiopathic Inflammatory MyopathiesChina
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Centre Hospitalier Universitaire de NiceRecruitingMitochondrial MyopathiesFrance
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Malaysia, China, Japan, Italy, Singapore, United Kingdom, France, Australia, Thailand, Denmark, United States
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McGill University Health Centre/Research Institute...RecruitingInterstitial Lung Disease | Myopathy, InflammatoryCanada
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Texas Tech University Health Sciences CenterRecruiting
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Children's Hospital of PhiladelphiaUniversity of Pennsylvania; National Institutes of Health (NIH); United Mitochondrial...Recruiting
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RWTH Aachen UniversityRecruitingRespiratory Failure | Mechanical Ventilation Complication | Diaphragm Issues | Intensive Care (ICU) MyopathyGermany
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Institut de Myologie, FranceRecruitingMuscular Dystrophies | Mitochondrial Myopathies | Glycogen Storage Disease | Idiopathic Inflammatory Myopathies | Congenital MyopathyFrance
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Maastricht UniversityRecruiting
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University of Texas at AustinRecruitingStroke | Multiple Sclerosis | Healthy | Muscular Diseases | Movement Disorders | Motor Neuron Disease | Traumatic Brain Injury | Spinal Cord Injuries | Motor DisordersUnited States
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingIdiopathic Inflammatory Myopathy | Interstitial Lung DiseaseChina
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University Hospital HeidelbergDeutsche José Carreras Leukämie-StiftungRecruitingGraft Vs Host DiseaseGermany
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Federal University of Espirito SantoNot yet recruitingIdiopathic Inflammatory Myopathy | Dermatomyositis | PolymyositisBrazil
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First Affiliated Hospital of Chongqing Medical...Not yet recruiting
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Centre Hospitalier Universitaire de NiceRecruitingMitochondrial DiseasesFrance
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University Hospital, Strasbourg, FranceRecruitingSystemic Sclerosis | Inflammatory MyopathiesFrance
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James DowlingCanadian Institutes of Health Research (CIHR); Cures Within Reach; The Joshua... and other collaboratorsRecruitingX Linked Myotubular MyopathyUnited Kingdom, Canada, United States
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University Hospital, BrestRecruiting
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Hospices Civils de LyonRecruitingEmbolic Stroke of Undetermined SourceFrance
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Tulane University School of MedicinePreventice; SamsungNot yet recruitingAtrial FibrillationUnited States
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University of Sao PauloRecruiting
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Hospices Civils de LyonRecruitingRare Diseases | Toxic Epidermal NecrolysesFrance
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CairnSurgical, Inc.RecruitingBreast Cancer FemaleUnited States, Canada, United Kingdom
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Koç UniversityRecruitingMuscular Dystrophies | Telemedicine | Proximal MyopathyTurkey
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial MyopathiesUnited States
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
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University Hospital, MontpellierRecruitingGenetic Disease | Myopathy | Phenotypic AbnormalityFrance
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Technical University of MunichCharite University, Berlin, Germany; Helmholtz Zentrum MünchenRecruitingCritical Illness | Muscle Weakness | Critical Illness Myopathy | Critical Care | Critical Illness Polyneuropathy | Metabolomics | Intensive Care (ICU) MyopathyGermany
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Barts & The London NHS TrustQueen Mary University of LondonRecruitingRespiratory Failure | Acute Respiratory Distress Syndrome | Critical Illness Myopathy | Intensive Care Unit Syndrome | Cardiac Failure | Intensive Care (ICU) Myopathy | Intensive Care NeuropathyUnited Kingdom
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University of Sao PauloRecruitingNeurologic Manifestations | Myopathy | ElectroPhys: MyopathyBrazil
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Christian Müller, MDUniversity Hospital Inselspital, Berne; Medical University Innsbruck; University... and other collaboratorsRecruitingMuscle Weakness | Muscle Atrophy | Muscle Spasticity | Muscle Cramp | Muscle Soreness | Muscle Damage | Myopathy | Muscle InjurySwitzerland, Austria
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University of Sao PauloRecruitingIdiopathic Inflammatory MyopathiesBrazil
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Hospital Clinic of BarcelonaRecruitingCritical Illness MyopathySpain
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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University of NebraskaRecruitingPeripheral Arterial DiseaseUnited States
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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University Hospital, BrestRecruiting
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophies | Inherited Neuromuscular Conditions | Inherited Neuropathies | Muscle Myopathies | Hereditary Spastic ParaplegiasUnited States