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Search clinical trials for: Late Infantile Neuronal Lipofuscinosis
Total 12758 results
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Kantonsspital AarauRecruiting
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University of BernRecruitingChildhood Cancer | Late EffectSwitzerland
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University Hospital, GenevaRecruitingChildhood Cancer | Genetic Predisposition | Late EffectSwitzerland
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Polaryx Therapeutics, Inc.Not yet recruitingJuvenile Neuronal Ceroid Lipofuscinosis
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St. Jude Children's Research HospitalNational Cancer Institute (NCI)RecruitingInsomnia | Sleep | Childhood Cancer | Survivorship | Late Effect | Neurocognitive ImpairmentUnited States
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Duke UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingHeart Failure | Pain | Pneumonia | Hypertension | Edema | Hemophilia | Insomnia | Pulmonary Arterial Hypertension | Coagulation Disorder | Asthma in Children | Down Syndrome | Attention Deficit Hyperactivity Disorder | Bronchopulmonary Dysplasia | Hypokalemia | Hyperphosphatemia | Primary Hyperaldosteronism | Adrenal Insufficiency and other conditionsUnited States, Canada
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University Hospital TuebingenNot yet recruitingAcute Respiratory Distress SyndromeGermany
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St. Jude Children's Research HospitalNational Cancer Institute (NCI)RecruitingCancer | SurvivorshipUnited States
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Neurogene Inc.RecruitingCeroid Lipofuscinosis, Neuronal 5United States
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University of BernUniversity Hospital, Geneva; University Hospital, Basel, Switzerland; Luzerner... and other collaboratorsRecruitingCardiovascular Diseases | Childhood Cancer | Cardiac DysfunctionSwitzerland
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingBatten Disease | Juvenile Neuronal Ceroid Lipofuscinosis (CLN3)United States
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University of BernSwiss Pediatric Oncology GroupRecruiting
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Emily de los ReyesRecruitingBatten Disease | CLN6United States
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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University of RochesterRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3 | Neuronal Ceroid Lipofuscinosis CLN5 | Neuronal Ceroid Lipofuscinosis CLN1 | Neuronal Ceroid Lipofuscinosis CLN2 | Neuronal Ceroid Lipofuscinosis CLN7 | Neuronal Ceroid Lipofuscinosis... and other conditionsUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Leigh R. Hochberg, MD, PhD.National Institute of Neurological Disorders and Stroke (NINDS); US Department... and other collaboratorsRecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injuries | Tetraplegia | Brain Stem Infarctions | Locked in SyndromeUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Late Onset Tay-Sachs DiseaseUnited States
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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University of BernKrebsforschung Schweiz, Bern, SwitzerlandActive, not recruitingHearing Loss | Childhood CancerSwitzerland
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Beyond Batten Disease FoundationTheranexusActive, not recruitingBatten DiseaseUnited States
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Seattle Children's HospitalChildren's Hospital of Philadelphia; Northwestern University; New York University and other collaboratorsCompletedCraniofacial Microsomia | Goldenhar Syndrome | Microtia | Hemifacial Microsomia | Oculo-Auriculo-Vertebral-SyndromeUnited States
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Rutgers, The State University of New JerseyRowan UniversityActive, not recruitingAutism Spectrum Disorder | Autistic Disorder | Autism | Autistic BehaviorUnited States
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MD Stem CellsEnrolling by invitationAlzheimer Disease | Traumatic Brain Injury | Autism Spectrum Disorder | Lewy Body Disease | Vascular Dementia | Autism | Dementia, Mixed | Alzheimer Dementia | Dementia, Multi-Infarct | Cadasil | Parkinson-Dementia Syndrome | Chronic Traumatic Encephalopathy | Autistic Behavior | Lewy Body Dementia With Behavioral... and other conditionsUnited States, United Arab Emirates
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Northwell HealthEnrolling by invitationDischarge ReadinessUnited States
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CVSS studyUniv. Prof. Dr. med. Joerg Faber, Center for Pediatrics, Hematology, Oncology... and other collaboratorsActive, not recruitingChildhood and Adolescence Cancer (Survivors and Deceased)Germany
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Children's Hospital of Orange CountyActive, not recruitingNeuronal Ceroid-Lipofuscinoses | Neuronal Ceroid Lipofuscinosis CLN2 | Spinocerebellar Ataxia, Autosomal Recessive 7United States
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Sohag UniversityCompletedInfantile EsotropiaEgypt
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Acibadem UniversityCompleted
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Technical University of MunichLudwig-Maximilians - University of MunichEnrolling by invitationCardiovascular Diseases | Pediatric CancerGermany
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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David L Rogers, MDActive, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United States
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Amicus TherapeuticsActive, not recruiting
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Fundacion Clinic per a la Recerca BiomédicaHospital Clinic of BarcelonaActive, not recruitingInfant, Newborn, Diseases | Infant DevelopmentSpain
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St. Jude Children's Research HospitalNational Cancer Institute (NCI)Active, not recruitingHodgkin Lymphoma | Acute Lymphoblastic Leukemia | Brain TumorUnited States
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Norwegian University of Science and TechnologyOslo University Hospital; St. Olavs Hospital; Norwegian Cancer SocietyActive, not recruitingChildhood Acute Lymphoblastic Leukemia | Childhood Acute Myeloid Leukemia | Childhood Non-Hodgkin LymphomaNorway
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Washington University School of MedicineNational Heart, Lung, and Blood Institute (NHLBI)Completed
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Clene NanomedicineUniversity of Texas Southwestern Medical CenterWithdrawnAmyotrophic Lateral SclerosisUnited States
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The George Washington University Biostatistics...Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedPregnancy | Preterm Birth | Respiratory Distress Syndrome | Pregnancy OutcomesUnited States
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Politecnico di MilanoCompletedPrematurity | Neonatal Respiratory Distress SyndromeItaly
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Jessica ScherrBioMarin PharmaceuticalEnrolling by invitationBatten Disease | Neuronal Ceroid-Lipofuscinoses | CLN2United States
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Boston CollegeGrand Challenges Canada; InfaCare Pharmaceuticals Corporation, a Mallinckrodt... and other collaboratorsActive, not recruitingParent-Child Relations | Parenting | Child Development | Child MalnutritionRwanda
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Çanakkale Onsekiz Mart UniversityCompletedPosition | Comfort | Newborn, Infant, Disease | ResidualTurkey
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Amicus TherapeuticsActive, not recruitingBatten Disease | CLN6United States
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Prince Sattam Bin Abdulaziz UniversityCompletedAcute Respiratory Distress Syndrome | Burns Chest Left Lateral | Burns Chest Right LateralSaudi Arabia
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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Brigham and Women's HospitalChild TrendsCompletedPostpartum Depression | Infant Development | Preterm InfantUnited States