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Search clinical trials for: genetic disorders
Total 154527 results
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Chang Gung UniversityRecruiting
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University of MalagaNot yet recruitingMuscular Dystrophy | Duchenne Muscular Dystrophy | Becker Muscular DystrophySpain
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Fondazione SISA (Societa Italiana per lo Studio...RecruitingFamilial Hypercholesterolemia | Genetic DisorderItaly
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Seoul National University HospitalNot yet recruitingMuscular Dystrophy, Duchenne | Upper Extremity | Orthotic DevicesKorea, Republic of
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AstraZenecaNot yet recruitingNeurofibromatosis 1 | Neurofibroma, Plexiform
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Xuanwu Hospital, BeijingNot yet recruiting
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Assistance Publique - Hôpitaux de ParisVaincre la MucoviscidoseNot yet recruiting
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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Institut de Myologie, FranceAssociation Française contre les Myopathies (AFM), ParisNot yet recruitingMerosin Deficient Congenital Muscular DystrophyFrance
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CHU de ReimsRecruitingPrimary Immunodeficiency | Common Variable Immunodeficiency | Igg Subclass Deficiency | Selective IgM DeficiencyFrance
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SensorionNot yet recruitingSensorineural Hearing Loss, BilateralFrance
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Hasan Kalyoncu UniversityRecruitingDown SyndromeTurkey
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University Hospital, BonnSwedish Orphan BiovitrumRecruitingHaemophilia A | Synovitis | Hemophilia Arthropathy | SonographyGermany
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Equilibra Bioscience LLCRecruitingHemophilia A | Hemophilia B | Healthy ParticipantsUnited States
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Federico II University; Istituto Auxologico Italiano; Università degli Studi...RecruitingBeckwith-Wiedemann SyndromeItaly
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IRCCS Fondazione Stella MarisAzienda USL Toscana Nord Ovest; University of Dublin, Trinity College; Meyer...Recruiting
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John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
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Children's Hospital ColoradoUniversity of Colorado, Denver; University of Pennsylvania; University of Alabama... and other collaboratorsRecruiting
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Fondation Ophtalmologique Adolphe de RothschildNot yet recruitingAlbinism, Ocular
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Huntington Study GroupRoche Products LimitedRecruitingHuntington DiseaseUnited States
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Roswell Park Cancer InstituteRecruitingRecurrent Mantle Cell Lymphoma | Recurrent Diffuse Large B-Cell Lymphoma | Refractory Diffuse Large B-Cell Lymphoma | Refractory Chronic Lymphocytic Leukemia | Refractory Mantle Cell Lymphoma | Recurrent High Grade B-Cell Lymphoma | Recurrent Transformed Follicular Lymphoma to Diffuse Large B-Cell... and other conditionsUnited States
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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Washington University School of MedicineNational Cancer Institute (NCI); The Foundation for Barnes-Jewish HospitalRecruitingMultiple Myeloma | Rectal Cancer | Cholangiocarcinoma | Colon CancerUnited States
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Rett Syndrome Research TrustNot yet recruitingRett SyndromeUnited States
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IRCCS Eugenio MedeaRecruiting
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IRCCS San RaffaeleRecruiting
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GCS Ramsay Santé pour l'Enseignement et la RechercheNot yet recruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingAutism Spectrum DisorderFrance
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Centre Hospitalier Sud FrancilienNot yet recruiting
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Mahidol UniversityNot yet recruitingBMI | Metabolic Syndrome | Insulin Resistance | NAFLD | Genetic Polymorphism | Cardiovascular Disease (CVD) | MASLD | Daily Step Count
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Craig EricksonHealx LimitedRecruitingFragile X SyndromeUnited States
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CARsgen Therapeutics Co., Ltd.Not yet recruitingMultiple Myeloma | Primary Plasma Cell Leukemia
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Maastricht University Medical CenterRecruitingQuality of Life | Tuberous Sclerosis | Basal Cell Nevus Syndrome | Cutis Laxa | Epidermolysis Bullosa | Ichthyosis | Ectodermal Dysplasia | Albinism | Birt-Hogg-Dube Syndrome | Palmoplantar KeratosesNetherlands
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Recruiting
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Hospital do CoracaoUniversity of Sao Paulo; Instituto Dante Pazzanese de Cardiologia; National Institute...Not yet recruiting
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Siriraj HospitalNot yet recruiting
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Tampere UniversityProfessor Lauri Lehtimäki; Professor Mika Mäkelä; Professor Sanna Toppila-Salmi; Professor Ilkka JunttilaNot yet recruitingAsthma | Allergy | Rhinitis, Allergic | Asthma in Children | Atopic Dermatitis | Allergen ImmunotherapyFinland
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MinYoung Kim, MD, PhDNot yet recruitingAlzheimer Dementia (AD)
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ENCellRecruitingCharcot-Marie-Tooth Disease Type 1AKorea, Republic of
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Chiesi Farmaceutici S.p.A.ICON plcNot yet recruiting
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ENCellNot yet recruitingDuchenne Muscular DystrophyKorea, Republic of
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University Health Network, TorontoNot yet recruitingIrritable Bowel Syndrome | Gastrointestinal Dysfunction | Ehlers-Danlos Syndrome | Hypermobility SyndromeCanada
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Caroline Michaela KistorpSanofiNot yet recruitingChronic Kidney Diseases | Fabry DiseaseDenmark
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Chronic Granulomatous DiseaseUnited States
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University of AarhusAarhus University HospitalRecruitingCardiovascular Diseases | Inflammation | Lymphedema | Turner SyndromeDenmark
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The University of QueenslandNot yet recruitingAtaxia TelangiectasiaAustralia
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Dr. Sascha DrewloNot yet recruitingFetal Growth Retardation | Preeclampsia | Cervix; Pregnancy | Inherited Genetic Conditions (Diagnosis)
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Blueskin ASRecruitingPsoriasis | Atopic Dermatitis | Vitiligo | Alopecia AreataDenmark