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Search clinical trials for: Adenoassociated Virus (AAV)
Total 25308 results
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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AerasSanofi Pasteur, a Sanofi CompanyCompleted
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InflaRx GmbHIqvia Pty LtdTerminatedGranulomatosis With Polyangiitis (GPA) | Microscopic Polyangiitis (MPA)United States, Canada
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Regeneron PharmaceuticalsRecruitingCongenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)Spain, United Kingdom, United States
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Kala Pharmaceuticals, Inc.CompletedBlepharitisUnited States
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Tacere Therapeutics, Inc.TerminatedHepatitis CUnited States
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Tacere Therapeutics, Inc.CompletedHepatitis CUnited States
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyCompletedFamilial Lipoprotein Lipase DeficiencyCanada
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National Institute of Diabetes and Digestive and...University of FloridaCompleted
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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GenethonCompletedLimb Girdle Muscular Dystrophy Type 2C | Gamma-sarcoglycanopathyFrance
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Amsterdam Molecular TherapeuticsInternational Antiviral Therapy Evaluation CenterUnknownFamilial Lipoprotein Lipase DeficiencyCanada
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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Merck Sharp & Dohme LLCCompleted
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IA | Von Gierke's Disease (GSD Type Ia)Netherlands, United States, Canada, Spain
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Brain Neurotherapy Bio, Inc.California Institute for Regenerative Medicine (CIRM); Asklepios Biopharmaceutical...Active, not recruiting
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Spark TherapeuticsChildren's Hospital of Philadelphia; University of Pittsburgh; St. James's Hospital... and other collaboratorsTerminated
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University of PennsylvaniaNational Heart, Lung, and Blood Institute (NHLBI); National Institute of Arthritis... and other collaboratorsActive, not recruitingGranulomatosis With PolyangiitisUnited States, Canada
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Brain Neurotherapy Bio, Inc.Recruiting
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PfizerActive, not recruitingHemophilia ASpain, Taiwan, Australia, United States, Japan, France, Turkey, Germany, Korea, Republic of, United Kingdom, Saudi Arabia, Canada, Greece, Sweden, Brazil, Italy
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Radboud University Medical CenterDutch Cancer SocietyCompletedHypertension | Cancer | Endothelial DysfunctionNetherlands
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Lori GawronPlanned Parenthood Association of UtahRecruitingEmergency ContraceptionUnited States
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St. Jude Children's Research HospitalRecruitingSickle Cell DiseaseUnited States
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Mercy Health OhioTerminatedOpen Fracture | Post-Op Wound InfectionUnited States
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Tenaya TherapeuticsJohns Hopkins University; Mayo ClinicRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States
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Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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Neurocrine BiosciencesVoyager TherapeuticsCompletedParkinson's DiseaseUnited States
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Neurocrine BiosciencesVoyager TherapeuticsActive, not recruitingParkinson's DiseaseUnited States
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AviadoBio LtdRecruitingFrontotemporal Dementia | FTD | FTD-GRN | Dementia, FrontotemporalNetherlands, Spain, Poland, United States
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University of ZurichCompleted
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GenSight BiologicsRecruitingNon-syndromic Retinitis PigmentosaUnited States, France, United Kingdom
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Shanghai Mental Health CenterUnknownTreatment-resistant SchizophreniaChina
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Tianjin Anding HospitalRecruitingBPSD | Amisulpride | Olanzapine | Dementia of the Alzheimer TypeChina
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Brainvectis, a subsidiary of Asklepios BioPharmaceutical...Active, not recruitingHuntington DiseaseFrance
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BayerUltragenix pharmaceuticalActive, not recruitingHemophilia ANetherlands, United States, Germany, United Kingdom, France, Bulgaria
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Lions Eye Institute, Perth, Western AustraliaAdverum Biotechnologies, Inc.CompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Retinal Neovascularization | Age-related Maculopathies | Age-related Maculopathy | Maculopathies,Age-related | Maculopathy,Age-relatedAustralia
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Spark TherapeuticsCompletedHemophilia AUnited States, Australia, Canada, Israel, Thailand
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Aspa TherapeuticsRecruiting
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University of South FloridaBristol-Myers Squibb; University of Pennsylvania; National Institute of Arthritis... and other collaboratorsActive, not recruitingWegener's Granulomatosis | Granulomatosis With Polyangiitis | ANCA-Associated Vasculitis | Granulomatosis With Polyangiitis (Wegener's)United States, United Kingdom, Ireland, Canada, Germany
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University of South FloridaNational Heart, Lung, and Blood Institute (NHLBI); National Institute of Arthritis... and other collaboratorsActive, not recruitingVasculitis | Granulomatosis With Polyangiitis | Wegener GranulomatosisUnited States
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Alpine Immune Sciences, Inc.RecruitingLupus Nephritis | Immunoglobulin A Nephropathy | Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis | Membranous NephropathyUnited States, Australia, Korea, Republic of, Austria, Norway, Spain, United Kingdom
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University of VigoHospital Clinico Universitario de Santiago; Xunta de Galicia; Ministerio de Educacion...Completed
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National Cancer Institute (NCI)Active, not recruitingGanglioneuroblastoma | High Risk NeuroblastomaUnited States, New Zealand, Australia
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MAXVAX Biotechnology Limited Liability CompanyNot yet recruiting