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- US Clinical Trials Registry
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Search clinical trials for: hereditary retinal dystrophies
Total 7529 results
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National Eye Institute (NEI)Active, not recruitingRetinitis Pigmentosa | Inherited Ophthalmic DiseasesUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Nanoscope Therapeutics Inc.CompletedEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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Nacuity Pharmaceuticals, Inc.Foundation Fighting BlindnessActive, not recruitingUsher SyndromesAustralia
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Endogena Therapeutics, IncActive, not recruitingRetinitis Pigmentosa | Retinitis Pigmentosa SyndromeUnited States
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4D Molecular TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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University of California, Santa BarbaraJohns Hopkins University; National Eye Institute (NEI); University of Michigan; University of MinnesotaCompleted
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GenSight BiologicsNo longer availableLeber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
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Nanoscope Therapeutics Inc.CompletedRetinitis Pigmentosa | Retinal DystrophyUnited States, Puerto Rico
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Sun Yat-sen UniversityCompletedRetinitis Pigmentosa | Inherited Retinal Dystrophy | Retina DisorderChina
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Novartis PharmaceuticalsActive, not recruitingRetinitis PigmentosaSweden
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University of California, DavisActive, not recruitingDiabetic Retinopathy | Retinitis Pigmentosa | Non-exudative Age-related Macular Degeneration | Retina Vein Occlusion | Hereditary Macular DegenerationUnited States
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Janssen Research & Development, LLCCompletedInterstitial Cystitis | Pigmentary Retinopathy | Pigmentary MaculopathyUnited States
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Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Jaeb Center for Health ResearchUsher 1F Collaborative; Marjorie C. Adams FoundationActive, not recruitingRetinal Degeneration | Retinitis Pigmentosa | Eye Diseases, HereditarySwitzerland, United States, Germany, Netherlands, Canada, France, Israel
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University of Campania "Luigi Vanvitelli"Retina Italia OnlusCompletedLeber Congenital Amaurosis 2 | Retinitis Pigmentosa 20Italy
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Centre d'Etude des Cellules SouchesActive, not recruitingRetinitis PigmentosaFrance
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AbbVieActive, not recruitingAdvanced Retinitis PigmentosaUnited States
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STZ eyetrialEnrolling by invitationRetinitis PigmentosaGermany
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Columbia UniversityActive, not recruitingAge-related Macular Degeneration | Retinitis Pigmentosa | Vitelliform Macular Dystrophy | Choroidal Ischemia | Central Serous RetinopathyUnited States
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Johns Hopkins UniversityActive, not recruiting
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jCyte, IncCalifornia Institute for Regenerative Medicine (CIRM)CompletedRetinitis PigmentosaUnited States
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Nanoscope Therapeutics Inc.Enrolling by invitationRetinal Degeneration | Retinitis Pigmentosa | Retinal DiseaseIndia
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jCyte, IncCalifornia Institute for Regenerative Medicine (CIRM)CompletedRetinitis PigmentosaUnited States
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ReNeuron LimitedActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Spain
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Batman Training and Research HospitalCompletedCorneal Dystrophy | Macular Dystrophy | Hyperemesis Gravidarum - SevereTurkey
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PT. Prodia Stem Cell IndonesiaEnrolling by invitationRetinitis PigmentosaIndonesia
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Nova Southeastern UniversityNational Eye Institute (NEI)Active, not recruitingRetinitis PigmentosaUnited States
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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MeiraGTx UK II LtdJanssen, LPActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Canada
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Second Sight Medical ProductsCompletedRetinitis PigmentosaUnited States
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Ankara Universitesi TeknokentCompleted
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Center for Eye Research AustraliaAustralian National University; Commonwealth Scientific and Industrial Research... and other collaboratorsEnrolling by invitation
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Nano RetinaMedPass InternationalTerminatedRetinal Degeneration | Retinitis PigmentosaBelgium, Israel, Italy
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Neurotech PharmaceuticalsUniversity of California, San FranciscoCompletedRetinitis Pigmentosa | Usher Syndrome Type 2 | Usher Syndrome Type 3United States
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NightstaRx Ltd, a Biogen CompanyCompletedX-Linked Retinitis PigmentosaUnited States, France, United Kingdom, Finland, Netherlands, Germany, Canada
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Acibadem UniversityCompletedRetinitis Pigmentosa | Stem Cell TransplantTurkey
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ProQR TherapeuticsTerminatedEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, United Kingdom
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Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
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Applied Genetic Technologies CorpCompletedX-Linked Retinitis PigmentosaUnited States
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedRetinitis Pigmentosa | Dry Age-related Macular DegenerationItaly
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ProQR TherapeuticsTerminatedRetinitis Pigmentosa | Usher Syndrome Type 2United States, Canada, France
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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Johns Hopkins UniversityCompleted
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Minnesota HealthSolutionsJohns Hopkins University; Second Sight Medical ProductsCompleted
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ProQR TherapeuticsActive, not recruitingEye Diseases | Retinitis Pigmentosa | Eye Diseases, Hereditary | Vision Disorders | Retinal Disease | Eye Disorders Congenital | Usher Syndrome Type 2 | Deaf BlindUnited States, Netherlands, United Kingdom, Germany