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Search clinical trials for: Late Onset Lysosomal Acid Lipase Deficiency (CESD)
Total 42362 results
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom, Germany, France, Italy, Portugal, Belgium, Netherlands
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BioMarin PharmaceuticalCompletedPompe DiseaseUnited States, United Kingdom, France, Australia, Germany
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Masonic Cancer Center, University of MinnesotaCompletedMucopolysaccharidosis | Hurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Krabbe Disease | Adrenoleukodystrophy (ALD) | Hunter Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Metachromatic Leukodystrophy (MLD) | Maroteaux-Lamy SyndromeUnited States
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Meir Medical CenterUnknownAntiphospholipid SyndromeIsrael
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionUnited States
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknownPompe Disease | Late Onset Pompe DiseaseSpain
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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Genzyme, a Sanofi CompanyTerminatedNiemann-Pick Disease | Acid Sphingomyelinase DeficiencyUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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Duke UniversityCompletedHemoglobinopathies | Thalassemia | Lysosomal Storage Disease | Immunodeficiencies | Inborn Errors of Metabolism | Sickle Cell | Non Malignant Disorders | Congenital Marrow FailuresUnited States
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Boehringer IngelheimCompleted
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedPompe Disease Late-Onset | Glycogen Storage Disease Type II GSD IIUnited States
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National Taiwan University HospitalUnknown
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Janssen R&D IrelandCompletedHIV Infections | Acquired Immunodeficiency SyndromeUnited States, France, Argentina, South Africa, Thailand
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National Institute of Allergy and Infectious Diseases...Completed
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Instituto Nacional de Salud Publica, MexicoInstituto Nacional de Ciencias Medicas y Nutricion Salvador Zubiran; Instituto...UnknownHuman Immunodeficiency Virus (HIV) | Tuberculosis (TB) | Latent Tuberculosis Infection (LTI)Mexico
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland...WithdrawnG(M2) Ganglioside | Tay-Sachs Disease Ganglioside | Sandhoff Disease GangliosideUnited States, Canada
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Juan A. ArnaizCompleted
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BayerWithdrawnHypogonadismRussian Federation, Italy, Latvia, Poland, Germany, United Kingdom
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University of North Carolina, Chapel HillTerminated
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University of North Carolina, Chapel HillNational Institute of Allergy and Infectious Diseases (NIAID); Merck Sharp... and other collaboratorsTerminatedHIV InfectionsUnited States
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Amsterdam Molecular TherapeuticsInternational Antiviral Therapy Evaluation CenterUnknownFamilial Lipoprotein Lipase DeficiencyCanada
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyCompletedFamilial Lipoprotein Lipase DeficiencyCanada
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EpicentreMédecins Sans Frontières, France; Embassy of France in Uganda; National Sleeping...TerminatedTrypanosomiasis, AfricanUganda
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingAromatic L-amino Acid Decarboxylase Deficiency
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University of North Carolina, Chapel HillNorth Carolina Translational and Clinical Sciences InstituteNot yet recruitingColorectal Cancer | Rectal Cancer | Rectal Neoplasms | Colon Cancer | Colon Adenocarcinoma | Colon Rectal Cancer | Hereditary Nonpolyposis Colon CancerUnited States
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Hospital Universitario 12 de OctubreNot yet recruitingShock | Vasopressor Adverse Reaction | Vasopressin Causing Adverse Effects in Therapeutic Use | Vasopressin DeficiencySpain
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King's College Hospital NHS TrustChiesi LimitedNot yet recruitingRespiratory Distress Syndrome | Surfactant Deficiency Syndrome Neonatal | Preterm Pregnancy
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University of ZurichSwiss HIV Cohort StudyRecruiting
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Policlinico HospitalRecruitingTransplantation | Ascorbic Acid DeficiencyItaly
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University of Missouri-ColumbiaGilead SciencesRecruitingHIV Infections | ART | Noncompliance, PatientUnited States
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McGill UniversityGlobal Affairs Canada; World Vision CanadaNot yet recruitingStunting | Diet; Deficiency | Empowerment | Acceptability of Health Care | Gender EqualityBangladesh, Kenya, Tanzania
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Lund UniversityRecruitingFemale | Sport Injury | Female Athlete Triad | Sports Accident | Ice-Skates AccidentSweden
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Jeremy KoppelNational Institute of Mental Health (NIMH)RecruitingLate Onset Schizophrenia | Delusional Disorder (Late Onset)United States
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Istituto Clinico HumanitasRecruiting
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The University of QueenslandNot yet recruitingAtaxia TelangiectasiaAustralia
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ViiV HealthcareRecruiting
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Assiut UniversityNot yet recruiting
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University of TorontoUnity Health TorontoRecruiting
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Fresenius KabiNot yet recruitingMalnutrition | Pediatric ALL | Essential Fatty Acid Deficiency | Parenteral Nutrition Associated Liver Disease (PNALD)
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S.LAB (SOLOWAYS)Center of New Medical TechnologiesRecruiting
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Lancashire Teaching Hospitals NHS Foundation TrustRecruitingStroke | Dementia | Late Onset EpilepsyUnited Kingdom
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Africa Health Research InstituteRecruitingHIV InfectionsSouth Africa
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Travere Therapeutics, Inc.Recruiting
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Erasmus Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; AI...Not yet recruiting
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany