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Search clinical trials for: hereditary
Total 2868 results
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Viridian Therapeutics, Inc.Recruiting
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Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
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Unity Biotechnology, Inc.RecruitingEye Diseases | Diabetes Mellitus | Retinal Degeneration | Retinal Diseases | Edema | Diabetic Retinopathy | Diabetic Macular Edema | Macular Edema | Retinal DiseaseUnited States
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Recursion Pharmaceuticals Inc.RecruitingSolid Tumor | APC Gene Mutation | AXIN1 Gene MutationUnited States
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University Hospital, AngersNot yet recruitingNicotinamide Adverse Reaction
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Shandong UniversityNot yet recruitingPeutz-Jeghers Syndrome | Small Bowel PolypChina
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Assiut UniversityRecruitingBehcet's Disease With Multisystem InvolvementEgypt
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Memorial Sloan Kettering Cancer CenterRecruitingSolid Tumor | Rhabdoid Tumor | Wilms Tumor | Nephroblastoma | Malignant Peripheral Nerve Sheath Tumors | MPNST | XPO1 Gene MutationUnited States
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Hoffmann-La RocheRecruitingThyroid Eye Disease | TEDJapan, Australia, Singapore, United States, Argentina, Germany, Italy, Hong Kong
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Istanbul University - Cerrahpasa (IUC)Recruiting
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Laurent ServaisSYSNAVRecruitingDuchenne Muscular Dystrophy | Myotonic Dystrophy 1 | Congenital Muscular Dystrophy | Centronuclear Myopathy | Charcot-Marie-Tooth | Fascioscapulohumeral Muscular DystrophyBelgium
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University Hospital, ToulouseNot yet recruiting
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Virginia Commonwealth UniversityNot yet recruitingAmyloidosis, HereditaryUnited States
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PERROD GuillaumeNot yet recruiting
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University Hospital, AntwerpKom Op Tegen Kanker; Stichting tegen KankerRecruitingEsophageal Cancer | Ovarian Cancer | Pancreas Cancer | Liver CancerBelgium
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OcugenRecruitingStargardt DiseaseUnited States
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Institut National de la Santé Et de la Recherche...RecruitingNeurofibromatosis Type 1 | Ichthyosis | Ectodermal Dysplasia | Albinism | Pemphigus | Mucous Membrane Pemphigoid | Inherited Epidermolysis Bullosa | Palmoplantar Keratoderma | Incontinentia PigmentiFrance
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Hospices Civils de LyonRecruitingHereditary Hemorrhagic Telangiectasia | Rendu Osler DiseaseFrance
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Institut National de la Santé Et de la Recherche...RecruitingMicrophthalmia | Aniridia | Anophthalmia | Anterior Segment Dysgenesis 6, Peters Anomaly Subtype | Anterior Segment Dysgenesis 3, Rieger SubtypeFrance
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Beijing Tiantan HospitalRecruiting
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RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis | Guillain-Barre Syndrome | Chronic Inflammatory Demyelinating PolyneuropathyUnited Kingdom
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CSL BehringRecruiting
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EuroBloodNet AssociationNot yet recruitingHereditary Red Blood Cell Disorder (Disorder)Denmark, Netherlands
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Odense University HospitalRecruitingTelangiectasia, Hereditary Hemorrhagic | Intracranial Arteriovenous MalformationsDenmark
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Institut National de la Santé Et de la Recherche...Recruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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Fog Pharmaceuticals, Inc.RecruitingCancer | Gastric Cancer | Colorectal Cancer | Solid Tumor | Metastatic Cancer | Adenomatous Polyposis Coli | Non-small Cell Lung Cancer | Non-small Cell Lung Cancer Metastatic | Non-small Cell Carcinoma | Locally Advanced Solid Tumor | Non-small Cell Lung Cancer Stage IIIB | Gastroesophageal-junction Cancer | Non-Small... and other conditionsUnited States
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Shanghai Fosun Pharmaceutical Industrial Development...RecruitingNeurofibromatosis 1 | NF1 | Plexiform NeurofibromaChina
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University of ArkansasRecruitingNeurofibromatosis 1United States
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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University of Southern CaliforniaNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Ultrasound Therapy; Complications
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
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Piazza della Vittoria 14 Studio Medico - Ginecologia...Not yet recruitingLynch Syndrome | ContraceptionItaly
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HuidaGene Therapeutics Co., Ltd.Cholgene Therapeutics, Inc.RecruitingLeber Congenital Amaurosis | Inherited Retinal Diseases Caused by RPE65 MutationsUnited States, China
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University of MinnesotaRecruiting
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PT. Prodia Stem Cell IndonesiaRecruitingRetinitis PigmentosaIndonesia
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Santé Arménie French-Armenian Research CenterRecruitingRheumatoid Arthritis | Celiac Disease | Giant Cell Arteritis | Sjogren's Syndrome | Takayasu Arteritis | Primary Antiphospholipid Syndrome | Behcet Disease | Antineutrophil Cytoplasmic Antibody (ANCA) Positive Vasculitis | Hereditary and Acquired AngioedemaArmenia
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Hereditary Neuropathy FoundationRecruitingCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease, Type IA | Charcot-Marie-Tooth Disease Type 2A | Charcot-Marie-Tooth | Charcot-Marie-Tooth Disease, Type IB | Charcot-Marie-Tooth Disease Type 2 | Charcot-Marie-Tooth Disease, Type 2C | Charcot-Marie-Tooth Disease Type 2A2B | Charcot-Marie-Tooth... and other conditionsUnited States
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AstraZenecaRecruitingNeurofibromaRussian Federation
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University of Sao Paulo General HospitalGlaxoSmithKlineRecruitingRheumatoid Arthritis | Systemic Lupus Erythematosus | Systemic Sclerosis | Juvenile Idiopathic Arthritis | Sjogren's Syndrome | Spondylitis, Ankylosing | Spondyloarthritis | Behçet Disease | Idiopathic Inflammatory Myopathies | Vasculitis, Systemic | Dermatomyositis, JuvenileBrazil
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Maxima Medical CenterRecruitingChronic Pain Syndrome | Nerve Entrapment Syndrome | Anterior Cutaneous Nerve Entrapment SyndromeNetherlands
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University; Henan Provincial People's HospitalRecruitingX-Linked Retinitis PigmentosaChina
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Rennes University HospitalRecruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryFrance
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Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex Associated Neuropsychiatric DiseaseUnited States, United Kingdom, Poland
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Adam Fedyk, MD, FACSAlcon ResearchRecruitingCataract | Fuchs DystrophyUnited States
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Eye & ENT Hospital of Fudan UniversityFudan UniversityRecruiting
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Power Life Sciences Inc.Not yet recruitingRetinitis Pigmentosa