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Search clinical trials for: serotype Rh10 AAV
Total 441 results
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Sarepta Therapeutics, Inc.Hansa Biopharma ABActive, not recruitingDuchenne Muscular DystrophySpain
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PfizerActive, not recruitingHemophilia ASpain, Taiwan, Australia, United States, Japan, France, Turkey, Germany, Korea, Republic of, United Kingdom, Saudi Arabia, Canada, Greece, Sweden, Brazil, Italy
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Janssen Vaccines & Prevention B.V.Completed
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LimFlow, Inc.Active, not recruitingVascular Diseases | Arterial Occlusive Diseases | Peripheral Arterial Disease | Peripheral Vascular Disease | Peripheral Artery Disease | Critical Limb Ischemia | Arterial Disease | Arterial Occlusion | Critical Lower Limb Ischemia | Chronic Limb-Threatening Ischemia | Peripheral Artery Occlusion | Peripheral...United States, Puerto Rico
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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Spark TherapeuticsCompletedHematologic Diseases | Blood Coagulation Disorders, Inherited | Coagulation Protein Disorders | Hemorrhagic Disorders | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Gene Therapy | Blood Coagulation Disorder | Gene Transfer | Adeno-Associated Virus (AAV) | Factor VIII (FVIII) | Factor VIII (FVIII)... and other conditionsUnited States
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BiogenCompletedChoroideremiaUnited States, Germany, France
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Daiichi Sankyo Europe, GmbH, a Daiichi Sankyo CompanyCompletedCardiovascular Diseases | Dyslipidemia | Hypercholesterolemia | Atherosclerotic Cardiovascular DiseaseFinland, Netherlands, Spain, Belgium, Sweden, Austria, United Kingdom, Switzerland, Denmark, France, Germany, Portugal, Italy, Ireland
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Cairo UniversityActive, not recruitingPhantom Pain Following Amputation of Lower LimbEgypt
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University of PennsylvaniaNational Heart, Lung, and Blood Institute (NHLBI); National Institute of Arthritis... and other collaboratorsActive, not recruitingGranulomatosis With PolyangiitisUnited States, Canada
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PfizerActive, not recruiting
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Janssen Vaccines & Prevention B.V.CompletedRespiratory Syncytial Viruses | Lower Respiratory Tract DiseaseUnited States, Taiwan, Thailand, Canada, Poland, United Kingdom, Brazil, Chile, New Zealand, Estonia, Finland, South Africa, Australia, China
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Brixsana Private Clinic - Centro di Chirurgia Plastica...Ludwig Boltzmann Institute for Traumatology - The research center in cooperation... and other collaboratorsCompletedAmputation | Phantom Pain | Targeted Sensory ReinervationAustria, Italy
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Baxalta now part of ShireActive, not recruiting
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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LimFlow SAActive, not recruitingCritical Limb IschemiaUnited Kingdom
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LimFlow SAActive, not recruiting
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BiogenCompletedX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Spark TherapeuticsCompletedHemophilia AUnited States, Australia, Canada, Israel, Thailand
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Adverum Biotechnologies, Inc.ParexelActive, not recruitingNeovascular Age-related Macular DegenerationUnited States, France, United Kingdom
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GenSight BiologicsNo longer availableLeber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
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Serum Institute of India Pvt. Ltd.PPD Australia Pty LtdCompleted
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Janssen Vaccines & Prevention B.V.Bavarian Nordic GmbHTerminatedHemorrhagic Fever, EbolaFrance, United Kingdom, Kenya, United States, Uganda, Burkina Faso, Tanzania
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Astellas Gene TherapiesActive, not recruitingX-Linked Myotubular MyopathyUnited States, Canada, France, Germany
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Neurocrine BiosciencesVoyager TherapeuticsCompletedParkinson's DiseaseUnited States
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BioMarin PharmaceuticalActive, not recruiting
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Neurocrine BiosciencesVoyager TherapeuticsActive, not recruitingParkinson's DiseaseUnited States
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Terence FlotteMassachusetts General Hospital; University of Massachusetts, WorcesterActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States
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Nanoscope Therapeutics Inc.Enrolling by invitationEye Diseases | Retinal Degeneration | Retinal Diseases | Retinitis Pigmentosa | Retinitis | Eye Diseases, Hereditary | Retinal DystrophiesUnited States, Puerto Rico
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Dr Cipto Mangunkusumo General HospitalEijkman Institute for Molecular BiologyCompletedPneumonia, BacterialIndonesia
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Janssen Vaccines & Prevention B.V.Completed
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Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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Benjamin GreenbergActive, not recruiting
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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AmgenNovartisCompletedEpisodic MigraineBelgium, United States, Spain, Czechia, Finland, United Kingdom, Israel, Ireland, Netherlands, Argentina, Austria, France, Germany, Greece, Italy, Poland, Portugal, Slovakia
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Lexeo TherapeuticsWeill Medical College of Cornell University; Alzheimer's Drug Discovery FoundationActive, not recruitingAlzheimer Disease | Early Onset Alzheimer DiseaseUnited States
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Janssen Vaccines & Prevention B.V.CompletedRespiratory Syncytial VirusCanada, United Kingdom, Spain, Brazil, Sweden, Poland, Australia, Finland
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National Institute of Allergy and Infectious Diseases...Active, not recruitingHIV-1 Infected Adults With Controlled ViremiaUnited States
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Crucell Holland BVCompleted
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Johns Hopkins Bloomberg School of Public HealthPfizer; Maulana Azad Medical CollegeCompleted
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Homology Medicines, IncTerminatedPhenylketonuria | Phenylketonurias | PAH DeficiencyUnited States
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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PfizerCompletedImmunogenicity, VaccineChina
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Istari Oncology, Inc.National Cancer Institute (NCI); Duke University; Brain Tumor Research Charity...CompletedGlioma | Glioblastoma | Malignant Glioma | GBMUnited States
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States