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Search clinical trials for: hereditary
Total 2868 results
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Therapeutic Advances in Childhood Leukemia ConsortiumRecruitingNeurofibromatosis 1 | JMML | Leukemia, Juvenile Myelomonocytic | JCML | CBL SyndromeUnited States
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University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
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Peking Union Medical College HospitalNot yet recruitingAneurysm | Behcet Syndrome, Vascular TypeChina
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2C Tech CorpORA, Inc.Not yet recruitingRetinitis Pigmentosa
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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Hospital Universitari Vall d'Hebron Research InstituteHospital Universitario La PazNot yet recruitingHereditary Angioedema With C1 Esterase Inhibitor DeficiencySpain
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Kowa Research Institute, Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States, United Kingdom, Spain, Germany, Canada, Denmark
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Vico Therapeutics B. V.RecruitingHuntington Disease | Spinocerebellar Ataxia Type 3 | Spinocerebellar Ataxia Type 1Israel, Germany, United Kingdom, Poland, Denmark, Netherlands, France
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CSL BehringRecruitingHereditary Angioedema (HAE)United States, Germany, Israel, Australia, Canada
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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National Taiwan University HospitalRecruiting
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Columbia UniversityNational Eye Institute (NEI); Centre Hospitalier National d'Ophtalmologie des... and other collaboratorsRecruitingRetinitis Pigmentosa | Best Vitelliform Macular DystrophyUnited States, Germany, France
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Peking University Third HospitalRecruitingSafety and Tolerability Study of Gene Editing Drug ZVS203e in Participants With Retinitis PigmentosaRetinitis PigmentosaChina
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Complement TherapeuticsRecruitingEye Diseases | Macular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal Disease | Macular AtrophyUnited Kingdom, United States
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Kowa Research Institute, Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States, Germany, Spain, Canada, United Kingdom, Denmark
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Istituto Superiore di SanitàFondazione G.B. Bietti, IRCCS; Ospedale Pediatrico Bambin GesùRecruitingRetinitis Pigmentosa | Macular Dystrophy | Inherited Retinal DystrophyItaly
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Cardiff UniversityUniversity of CanterburyRecruitingCleft Lip and Palate | Parenting | Neurofibromatoses | Skin Condition | Alopecia | Craniofacial | Limb DifferenceUnited Kingdom
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The Third Xiangya Hospital of Central South UniversityNot yet recruitingCharcot-Marie-Tooth Disease (CMT)
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University Hospital, GrenobleRecruitingAngio Edema HereditaryFrance
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingMalignant Solid Neoplasm | Hematopoietic and Lymphoid System Neoplasm | Hereditary Malignant NeoplasmUnited States
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AmgenRecruitingJuvenile Psoriatic Arthritis | Behçet's DiseaseSpain, Turkey, Israel, Greece
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); University of South FloridaRecruiting
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Children's Hospital of Fudan UniversityFirst Affiliated Hospital, Sun Yat-Sen University; Shandong Provincial Hospital and other collaboratorsRecruitingKidney Diseases | Proteinuria | Hereditary NephropathyChina
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Calico Life Sciences LLCAbbVieRecruitingVanishing White Matter DiseaseUnited States, Netherlands
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DeuterOncologyRecruitingAdult Solid Tumor | Lung Cancer | Advanced Solid Tumor | Non-small Cell Lung Cancer | Non-small Cell Carcinoma | Refractory Tumor | Hereditary Renal Papillary CancerFrance, Belgium, Netherlands
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SparingVisionRecruiting
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University of California, San FranciscoUniversity of California Pancreatic Cancer Consortium (UCPCC)RecruitingPancreatic Neuroendocrine NeoplasmUnited States
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Centre Hospitalier Universitaire de Saint EtienneKyoto University, Graduate School of MedicineNot yet recruitingCorneal DystrophiesFrance
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Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingAcute Myeloid Leukemia | Juvenile Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | AML | Acute Leukemia | Neurofibromatosis 1 | Hematologic Malignancy | Myelodysplasia | Minimal Residual Disease | Chromosome Abnormality | Monosomy 7 | Remission | Somatic Mutation | Cytogenetic Abnormality | TP53 | Fetal Hemoglobin | Intrachromosomal Amplification of Chromosome... and other conditionsUnited States
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Birmingham Women's and Children's NHS Foundation...Children's Cancer and Leukaemia GroupNot yet recruitingRenal Cancer | Wilms TumorUnited Kingdom
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San Raffaele UniversityFondazione IRCCS Istituto Nazionale dei Tumori di Milano, Milan, Italy; Ospedale... and other collaboratorsRecruitingColorectal Cancer | Diet Habit | Risk Reduction | Early Onset Colorectal CancerUnited States, Finland, Germany, Italy, Norway, Spain
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Associazione Italiana per lo Studio del PancreasGeneral and Pancreatic Surgery Unit, University of Verona; Fondazione Valsecchi and other collaboratorsRecruitingCandidates for Hereditary Pancreatic Cancer TestingItaly
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Gazi UniversityNot yet recruitingSleep Quality | Behçet Disease
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Maastricht University Medical CenterNot yet recruitingIntraocular Pressure | Fuchs' Endothelial Dystrophy | Pseudophakic Bullous Keratopathy
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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San Raffaele UniversityUnita' di Gastroenterologia - Policlinico Universitario di Bari; Unita' di... and other collaboratorsRecruitingLynch Syndrome | MLH1 Gene Mutation | MSH2 Gene Mutation | MSH6 Gene Mutation | PMS2 Gene Mutation | Lynch Syndrome II | Small Bowel Adenocarcinoma | Lynch Syndrome IItaly
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University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
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Shanghai Vitalgen BioPharma Co., Ltd.Not yet recruitingBietti Crystalline DystrophyChina
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M.D. Anderson Cancer CenterRecruitingBreast Cancer | Colorectal CancerUnited States
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Astria Therapeutics, Inc.RecruitingHereditary AngioedemaUnited States, United Kingdom, Canada, Germany, Bulgaria, Czechia
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H. Lee Moffitt Cancer Center and Research InstituteRecruitingLynch Syndrome | Pancreatic Ductal Adenocarcinoma | Chronic Pancreatitis | Pancreatic Cyst | Ataxia Telangiectasia | FAP | Peutz-Jeghers Syndrome | PALB2 Gene Mutation | BRCA Mutation | Fatty Pancreas | Genetic Pancreatic Cancer | Genetic Pancreatitis | Familial Atypical Multiple Mole-MelanomaUnited States
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ADARx Pharmaceuticals, Inc.RecruitingHereditary AngioedemaAustralia
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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Leiden University Medical CenterRecruiting
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Massachusetts General HospitalUnited States Department of Defense; Recordati Rare DiseasesRecruitingPain, Chronic | Schwannomatosis | SchwannomasUnited States
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AlexionRecruiting