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Search clinical trials for: Retroviral-Mediated Gene Transfer
Total 270387 results
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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Martin JaničkoF.D. Roosevelt Teaching Hospital with Policlinic Banska BystricaWithdrawnLiver Failure | CirrhosisSlovakia
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Sarepta Therapeutics, Inc.Active, not recruiting
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David WilliamsUniversity of California, Los Angeles; Boston Children's Hospital; Children's...CompletedSevere Combined ImmunodeficiencyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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Aristotle University Of ThessalonikiGeneral Hospital of Naoussa; Private Orthopedics Practice P. SymeonidisEnrolling by invitationAchilles Tendon Rupture | Achilles Tendon Injury | Achilles Tendon SurgeryGreece
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Memorial Sloan Kettering Cancer CenterSanofi; Duke University; Weill Medical College of Cornell University; New York...Active, not recruiting
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Unity Health TorontoTerminatedAlcohol Withdrawal | Alcohol Withdrawal Delirium | Alcohol Withdrawal SeizuresCanada
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Spark TherapeuticsActive, not recruitingLysosomal Storage Diseases | Glycogen Storage Disease Type II | Glycogen Storage Disease Type 2 | Pompe Disease (Late-onset) | Pompe Disease | LOPD | Acid Maltase DeficiencyUnited States, Canada, Netherlands, France, Denmark, Germany, Italy, United Kingdom
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National Institute of Allergy and Infectious Diseases...Active, not recruitingHIV-1 Infected Adults With Controlled ViremiaUnited States
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Instituto Valenciano de Infertilidad, IVI VALENCIACompleted
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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Iovance Biotherapeutics, Inc.CompletedSquamous Cell Carcinoma of the Head and NeckUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Adverum Biotechnologies, Inc.CompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Medical University of WarsawHuman Biome Institute S.A.Active, not recruitingParkinson DiseasePoland
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Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
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National Cancer Institute (NCI)CompletedProstate CancerUnited States
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Sarepta Therapeutics, Inc.Active, not recruiting
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NewAmsterdam PharmaActive, not recruitingDyslipidemias | Hypercholesterolemia | Familial Hypercholesterolemia | Atherosclerotic Cardiovascular Disease | High CholesterolUnited States, Poland, Denmark, Czechia, China, Netherlands, Japan, Georgia
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Alliance for Clinical Trials in OncologyNational Cancer Institute (NCI)Active, not recruiting
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Fundacion para la Investigacion Biomedica del Hospital...Merck Sharp & Dohme LLCCompleted
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Neuraptive Therapeutics Inc.TerminatedFacial ParalysisUnited States
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Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
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Amicus TherapeuticsActive, not recruiting
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Dartmouth-Hitchcock Medical CenterActive, not recruitingStroke, Ischemic | Stroke Hemorrhagic | Spastic HemiparesisUnited States
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Germans Trias i Pujol HospitalCarlos III Health InstituteCompleted
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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David WilliamsActive, not recruitingWiskott-Aldrich SyndromeUnited States
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David WilliamsActive, not recruiting
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Providence Health & ServicesActive, not recruitingMalignant Epithelial NeoplasmsUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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VA Office of Research and DevelopmentCompletedAdverse Drug Event | Cost | Patient ReadmissionUnited States
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Brown UniversityJohns Hopkins University; National Institute of Mental Health (NIMH); NYU Langone... and other collaboratorsActive, not recruitingHypertension | Diabetes | HIV/AIDS | Noncommunicable DiseasesKenya
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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City of Hope Medical CenterNational Cancer Institute (NCI)TerminatedSarcoma | Lymphoma | Kidney Cancer | Unspecified Childhood Solid Tumor, Protocol Specific | Testicular Germ Cell Tumor | Ovarian Cancer | Brain and Central Nervous System Tumors | Neuroblastoma | Liver Cancer | Extragonadal Germ Cell Tumor | Childhood Germ Cell TumorUnited States
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Iovance Biotherapeutics, Inc.Active, not recruitingMetastatic MelanomaUnited States, Spain, Germany, United Kingdom, France, Hungary, Italy, Switzerland
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Istituto Clinico HumanitasCompletedPregnancy Related | Ovarian Hyperstimulation Syndrome
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Sykehuset i Vestfold HFHospital Pharmacy Enterprise, South Eastern NorwayCompleted
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Sarepta Therapeutics, Inc.Nationwide Children's HospitalCompleted
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University of CalgaryAlberta Health services; University of AlbertaCompletedStroke | Epilepsy | Autoimmune Diseases | Endocrine System Diseases | Diabetes | Hematologic Diseases | Genetic Diseases, Inborn | Traumatic Brain Injury | Autism Spectrum Disorder | Respiratory Disease | Cardiac Disease | Metabolic Disease | Renal Disease | Neuro-Degenerative Disease | Fetal Alcohol Spectrum Disorders | Gastro-Intestinal DisorderCanada
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MeiraGTx, LLCEnrolling by invitationParkinson DiseaseUnited States
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Providence Health & ServicesCelldex TherapeuticsEnrolling by invitationMalignant Epithelial NeoplasmsUnited States
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French Innovative Leukemia OrganisationAmgenCompletedRichter SyndromeFrance
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University Hospital, GrenobleActive, not recruitingClinical Transfer of a Vulnerable Atherosclerotic Plaque Tracer : 99mTc-cAbVCAM1-5 (ATHENA) (ATHENA)Cardiovascular Diseases | AtherosclerosisFrance
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Tan Tock Seng HospitalNanyang Technological UniversityCompletedStroke | Spinal Cord Injuries | Acquired Brain Injury | Traumatic Brain Injury With Loss of Consciousness | Joint Replacement SurgerySingapore
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Yale UniversityNational Diaper Bank Network; Yale New Haven Health Primary Care ConsortiumCompletedStress | Urinary Tract Infections | Depressive Symptoms | Infection | Diaper DermatitisUnited States
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States