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Search clinical trials for: X-linked myotubular myopathy
Total 445 results
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University of Sao PauloCompletedRheumatic Diseases | Myopathy | Electrical RemodelingBrazil
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University of Sao PauloCompletedPhysical Activity | Idiopathic Inflammatory MyopathiesBrazil
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)TerminatedAcute Graft Versus Host DiseaseUnited States
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National Human Genome Research Institute (NHGRI)CompletedMitochondrial Disease | Myopathy | NeurologyUnited States
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Eunice Kennedy Shriver National Institute of Child...Completed
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Oregon Health and Science UniversityCompletedIntensive Care (ICU) MyopathyUnited States
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McMaster UniversityLondon Health Sciences CentreCompletedDelirium | Critical Illness | Critical Illness Myopathy | Withdrawal Syndrome | Hospital Acquired ConditionCanada
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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University of HelsinkiHelsinki University Central Hospital; Institute for Molecular MedicineCompletedMitochondrial MyopathiesFinland
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Novartis PharmaceuticalsTerminatedPolymyositisHungary, Taiwan, United States, Canada, Czechia, Poland
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Assiut UniversityCompletedCritical Illness | Renal Function Disorder | Critical Illness MyopathyEgypt
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Acacia Pharma LtdCompleted
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Hospices Civils de LyonCompleted
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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Benha UniversityUnknownIdiopathic Inflammatory MyopathiesEgypt
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Newcastle UniversityUnknownHereditary Inclusion Body Myopathy | GNE MyopathyUnited Kingdom
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Technical University of MunichHelmholtz Zentrum MünchenCompletedCritical Illness | Muscle Weakness | Critical Illness Myopathy | Critical Care | Critical Illness Polyneuropathy | Metabolomics | Intensive Care (ICU) MyopathyGermany
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Assistance Publique - Hôpitaux de ParisTerminatedSelenoprotein N-related MyopathyFrance
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faida agiliUR17DN02 : Autoimmune Diseases Research UnitUnknownRheumatoid Arthritis | Systemic Lupus Erythematosus | SARS-CoV Infection | Sjogren's Syndrome | Sarcoidosis | Spondyloarthritis | Behçet Disease | Inflammatory Myopathy | Systemic DiseaseTunisia
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedErythropoietic Protoporphyria | EPP | X-linked Protoporphyria | XLPUnited States
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Jose Alberola-RubioCompletedPelvic Pain | Pelvic Floor Disorders | Pelvic Pain Syndrome | Electromyography | EMG Syndrome | EMG: Myopathy | ElectroPhys: MyopathySpain
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Hamilton Health Sciences CorporationCompletedCritical Illness | Critical Illness Myopathy | Thoracic Surgery | Cardiac Disease | Critical Illness PolyneuropathyCanada
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Stealth BioTherapeutics Inc.CompletedPrimary Mitochondrial DiseaseUnited States
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Reneo Pharma LtdTerminatedPrimary Mitochondrial MyopathyUnited Kingdom
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Gerald SupinskiTerminatedCritical Illness | Respiratory Failure | Myopathy | WeaknessUnited States
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Bicetre HospitalUnknownRare Diseases | X-linked HypophosphatemiaFrance
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHyperparathyroidism | Hypophosphatemia, FamilialUnited States
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Central Hospital, Nancy, FranceUnknown
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Vanderbilt University Medical CenterSociety of Critical Care MedicineCompletedPost-Intensive Care SyndromeUnited States, Australia
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Hartford HospitalUniversity of ConnecticutUnknown
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University of KentuckyCompletedCritical Illness | Muscle Weakness | Intensive Care (ICU) Myopathy | PICSUnited States
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Peking University People's HospitalUnknown
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...CompletedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Hemophagocytic Lymphohistiocytosis (HLH) | Non Hodgkins Lymphoma | Familial Hemophagocytic Lymphohistiocytosis (FLH) | Viral-associated Hemophagocytic Syndrome (VAHS) | X-linked Lymphoproliferative...United States
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Adana City Training and Research HospitalCompletedCritical Illness PolyneuromyopathyTurkey
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Stealth BioTherapeutics Inc.CompletedMitochondrial MyopathyUnited States
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National Institute of Nursing Research (NINR)Completed
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Università degli Studi di BresciaUnknownCritical Illness Myopathy | Critical Illness PolyneuropathyItaly
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National Human Genome Research Institute (NHGRI)CompletedHereditary Inclusion Body MyopathyUnited States
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Fatty Acid Oxidation DefectsDenmark
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National Eye Institute (NEI)CompletedRetinoschisis | X-LinkedUnited States
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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Vanderbilt University Medical CenterCompletedIntensive Care Unit Syndrome | Intensive Care Neurological Disorder | Intensive Care (ICU) Myopathy | Intensive Care Psychiatric Disorder (Diagnosis)United States
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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Shenzhen Geno-Immune Medical InstituteUnknown
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
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Peking University People's HospitalUnknownInflammatory Myopathy
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Kwong Wah HospitalTung Wah Group of HospitalsUnknownIdiopathic Inflammatory Myopathies | Osteoporosis, OsteopeniaHong Kong
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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Mackay Memorial HospitalTerminatedCritical Illness Myopathy | Chronic Respiratory FailureTaiwan