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Search clinical trials for: Genetic association study
Total 137734 results
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M.D. Anderson Cancer CenterNovartis PharmaceuticalsNot yet recruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome-PositiveUnited States
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argenxRecruitingThyroid Eye DiseaseUnited States
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BioMarin PharmaceuticalRecruitingIdiopathic Short StatureUnited States
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argenxRecruitingThyroid Eye DiseaseUnited States
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
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Bioray LaboratoriesFirst Affiliated Hospital of Guangxi Medical UniversityNot yet recruiting
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Children's Hospital Medical Center, CincinnatiMakerere University; Ministry of Health, Uganda; Mulago Hospital, UgandaRecruiting
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Viracta Therapeutics, Inc.Recruiting
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Kind Pharmaceuticals LLCNot yet recruiting
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States
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ARTHEx Biotech S.L.Recruiting
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Chia Tai Tianqing Pharmaceutical Group Nanjing...Not yet recruiting
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Bioray LaboratoriesXiangya Hospital of Central South University; Sun Yat-Sen Memorial Hospital... and other collaboratorsNot yet recruiting
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Spark Therapeutics, Inc.Recruiting
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qinxiu zhangNot yet recruitingDiet Habit | Endometrial Polyp | Women
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI); Cystic Fibrosis FoundationRecruitingCystic Fibrosis | Parenthood StatusUnited States
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Merck Sharp & Dohme LLCRecruiting
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Zhongmou TherapeuticsNot yet recruitingRetinitis PigmentosaChina
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Suzhou Municipal HospitalNot yet recruitingFamilial Hypercholesterolemia | Refractory Hypercholesterolemia
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CorrectSequence Therapeutics Co., LtdRecruitingBeta-Thalassemia MajorChina
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Rege Nephro Co., Ltd.RecruitingAutosomal Dominant Polycystic Kidney Disease (ADPKD)Japan
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Not yet recruitingMuscular Dystrophy | Exercise | Duchenne Muscular Dystrophy | Vasodilation | DMD | Muscular Dystrophy in Children | Duchenne Disease
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South Egypt Cancer InstituteAssiut University; Shefa Al-orman Children Cancer HospitalRecruiting
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Asklepios Biopharmaceutical, Inc.BayerNot yet recruiting
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Bioray LaboratoriesInstitute of Hematology & Hospital of Blood Diseases, Chinese Academy of...Not yet recruiting
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Agios Pharmaceuticals, Inc.Not yet recruitingSickle Cell Disease | Nephropathy
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Bioray LaboratoriesNanfang Hospital, Southern Medical UniversityNot yet recruitingSickle Cell Disease
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Huazhong University of Science and TechnologyNot yet recruitingFrailty | Acute Postoperative PainChina
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The Lymphoma Academic Research OrganisationGrupo Español de Linfomas y Transplante Autólogo de Médula Ósea; Swiss Group... and other collaboratorsRecruitingFollicular LymphomaBelgium, France, Germany, Portugal, Spain
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Bavarian Cancer RegistryBavarian Association of Statutory Health Insurance Accredited PhysiciansNot yet recruitingNeuroendocrine Neoplasm of Lung | Neuroendocrine Neoplasm of Gastrointestinal Tract (Disorder)
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University of Texas Southwestern Medical CenterRecruiting
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, Turkey, United Kingdom, Italy
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Kanglin Biotechnology (Hangzhou) Co., Ltd.Not yet recruitingTransfusion-dependent Beta-ThalassemiaChina
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Yuhan CorporationRecruitingEssential HypertensionKorea, Republic of
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Eli Lilly and CompanyRecruitingAtopic DermatitisChina, Korea, Republic of
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LetolabNot yet recruiting
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Institut National de la Santé Et de la Recherche...RecruitingInfections | Autoimmune Diseases | Diagnosis | Immune DeficiencyFrance, United States, Australia, Belgium, Japan, Netherlands
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Keymed Biosciences Co.LtdNot yet recruiting
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Lynk Pharmaceuticals Co., LtdRecruitingAtopic DermatitisChina
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Viatris Inc.Not yet recruitingBioequivalence StudyThailand
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University College, LondonUniversity of North Carolina, Chapel Hill; NYU Grossman School of MedicineRecruitingDentatorubral-Pallidoluysian AtrophyUnited States, United Kingdom
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Genetic Disease InvestigatorsNot yet recruitingDry Eye | Dry Eye Disease
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...Recruiting
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UniQure Biopharma B.V.RecruitingFabry DiseaseUnited States
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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The Lymphoma Academic Research OrganisationLymphoma Study AssociationNot yet recruitingRefractory High Grade B-Cell Lymphoma | Diffuse Large B-cell Lymphoma Refractory | Refractory Transformed B-cell Non-Hodgkin Lymphoma | Refractory Primary Mediastinal Large B-Cell LymphomaFrance