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- US Clinical Trials Registry
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Search clinical trials for: Heredodegenerative Disorders of the Nervous System
Total 475708 results
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Spaulding Rehabilitation HospitalMassachusetts General HospitalWithdrawnHereditary Spastic Paraplegia
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Roger PackerWithdrawnNeurofibromatosis Type 1 | Tumors of the Central Nervous SystemUnited States
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University of MinnesotaCompletedTourette Syndrome | Tic Disorders | Tics | Tourette Syndrome in Children | Tourette Syndrome in Adolescence | Tic Disorder, Childhood | Tic, MotorUnited States
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Novartis PharmaceuticalsCompletedEarly Manifest Huntington DiseaseCanada, Germany, France, Spain, Hungary
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Ankara City Hospital BilkentCompletedLow Back Pain | Radiofrequency Ablation | Nerve Entrapment SyndromeTurkey
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Emalex Biosciences Inc.CompletedTourette Syndrome in Children | Tourette Syndrome in AdolescenceUnited States, Poland, France, Canada, Germany
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Ariel UniversityASST Santi Paolo e CarloCompleted
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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Kuopio University HospitalActive, not recruitingParkinson Disease | Neurodegenerative Diseases | Amyotrophic Lateral Sclerosis | Alzheimer Disease | Lewy Body Disease | Multiple System Atrophy | Corticobasal Degeneration | Frontotemporal Dementia | Vascular Dementia | Progressive Supranuclear Palsy | Huntington DiseaseFinland
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National Cancer Institute (NCI)CompletedNeurofibromatosis Type 1 | Recurrent Childhood Pilocytic Astrocytoma | Recurrent Childhood Visual Pathway GliomaUnited States, Canada, Australia, New Zealand
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Luye Pharma Group Ltd.CompletedTardive Dyskinesia | Huntington DiseaseChina
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
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Ovid Therapeutics Inc.CompletedFragile X Syndrome (FXS)United States
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GenSight BiologicsNo longer availableLeber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
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The University of Texas Health Science Center,...Cures Within ReachCompletedIrritability | Huntington DiseaseUnited States
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Neurocrine BiosciencesHuntington Study GroupActive, not recruitingChorea, HuntingtonUnited States, Canada
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Sarcoma Alliance for Research through CollaborationUnited States Department of Defense; AstraZenecaCompletedNeurofibromatosis 1 | Malignant Peripheral Nerve Sheath TumorsUnited States
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The University of Texas Health Science Center,...Texas Neurofibromatosis FoundationCompletedNeurofibromatosis 1United States
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JCR Pharmaceuticals Co., Ltd.Enrolling by invitationMucopolysaccharidosis IIUnited States
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University of California, Los AngelesNational Institute of Mental Health (NIMH)CompletedTourette's DisorderUnited States
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Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
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Institut de Myologie, FranceEnrolling by invitationMyotonic Dystrophy Type 1France
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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St. Justine's HospitalCHU de Quebec-Universite Laval; Montreal Children's Hospital of the MUHCActive, not recruitingLow-grade Glioma | Plexiform Neurofibroma | Central Nervous System GliomaCanada
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Washington University School of MedicineNational Institute of Mental Health (NIMH)CompletedTourette Syndrome | Tic Disorders | Tourette's Disorder | Chronic Motor or Vocal Tic Disorder | Transient Tic Disorder | Provisional Tic DisorderUnited States
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Sanguine BiosciencesCompletedMultiple Sclerosis | Parkinson's Disease | Amyotrophic Lateral Sclerosis (ALS) | Alzheimer's Disease | Huntington's DiseaseUnited States
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinUnited States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Brazil
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REGENXBIO Inc.Active, not recruitingMucopolysaccharidosis Type II (MPS II)United States, Canada
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NFlection Therapeutics, Inc.CompletedNeurofibromatosis 1 | Cutaneous NeurofibromaUnited States
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National Cancer Institute (NCI)Children's Oncology GroupActive, not recruitingJuvenile Myelomonocytic Leukemia | Neurofibromatosis Type 1United States
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Massachusetts General HospitalJohns Hopkins UniversityActive, not recruitingCutaneous NeurofibromaUnited States
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Johns Hopkins UniversityCompletedTourette Syndrome | Tic Disorders | Tics | Habit Reversal Training | Comprehensive Behavioral Intervention for TicsUnited States
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Berta AlemanyInstitut d'Investigació Biomèdica de Girona Dr. Josep Trueta; Universitat de... and other collaboratorsCompleted
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Shanghai Fosun Pharmaceutical Industrial Development...Active, not recruitingNeurofibromatosis 1 | NF1 | Plexiform NeurofibromaUnited States, China, Spain
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Neurocrine BiosciencesHuntington Study GroupCompletedChorea, HuntingtonUnited States, Canada
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Washington University School of MedicineNational Center for Advancing Translational Sciences (NCATS)CompletedTourette Syndrome | Tic Disorder, Chronic Motor or VocalUnited States
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Emalex Biosciences Inc.CompletedTourette SyndromeUnited States, Poland, France, Canada, Germany
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National Human Genome Research Institute (NHGRI)CompletedHuntington's DiseaseUnited States
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Cyprium Therapeutics, Inc.Enrolling by invitation
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Huntington Study GroupCompletedHuntington DiseaseUnited States
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Virginia Commonwealth UniversityCompletedNeurofibromatosis 1 | Neurocognitive Deficit | Mental Health ImpairmentUnited States
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Hôpital Necker-Enfants MaladesEuropean Georges Pompidou Hospital; CLAIROPCompletedSafety Issues | Efficacy, SelfFrance
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SwanBio Therapeutics, Inc.Active, not recruitingAMN | AMN Gene Mutation | X-ALDUnited States, Netherlands, Germany
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University of Alabama at BirminghamMemorial Sloan Kettering Cancer CenterActive, not recruitingNeurofibromatosis 2 | Progressive Vestibular Schwannoma (VS)United States