Search clinical trials for: Peroxisomal storage diseases
Total 376523 results
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ZevraDenmarkActive, not recruitingNiemann-Pick Disease, Type CUnited States, Spain, United Kingdom, Denmark, France, Germany, Italy, Poland, Switzerland
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University Hospital Birmingham NHS Foundation TrustNorthern Care Alliance NHS Foundation Trust; Cambridge University Hospitals... and other collaboratorsActive, not recruitingArrhythmia Burden, Risk of Sudden Cardiac Death and Stroke in Patients With Fabry Disease (RaILRoAD)Fabry DiseaseUnited Kingdom, Australia
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CinnagenCompletedMucopolysaccharidosis Type 1Iran, Islamic Republic of
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University of AarhusThe Danish Dairy Research Foundation, DenmarkCompleted
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Sangamo TherapeuticsActive, not recruitingFabry DiseaseUnited States, United Kingdom, Taiwan, Australia, Germany, Italy, Canada
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ShireActive, not recruiting
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X4 PharmaceuticalsActive, not recruiting
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ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
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ShireCompletedHunter SyndromeUnited States, Spain, Canada, United Kingdom, Mexico, Australia, France
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PfizerArena is a wholly owned subsidiary of PfizerCompletedEosinophilic EsophagitisUnited States, Spain, Switzerland, Australia, Belgium, Netherlands, Canada, Germany
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruiting
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IA | Von Gierke's Disease (GSD Type Ia)Netherlands, United States, Canada, Spain
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Sangamo TherapeuticsActive, not recruitingHemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis IIUnited States
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Vastra Gotaland RegionKarolinska University Hospital; Göteborg University; Uppsala University HospitalCompleted
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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Sanguine BiosciencesTerminatedGlycogen Storage Disease Type IBUnited States
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Massachusetts General HospitalActive, not recruiting
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University Health Network, TorontoOzmosis Research Inc.Completed
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Shoshana VilkGenzyme, a Sanofi CompanyCompletedGaucher Disease | Patient Reported OutcomeIsrael
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); Dana-Farber Cancer Institute and other collaboratorsCompletedSickle Cell DiseaseUnited States
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Ultragenyx Pharmaceutical IncTerminatedGlycogen Storage Disease Type IIIUnited States, Spain, Italy
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Green Cross CorporationCompleted
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Sangamo TherapeuticsEnrolling by invitationFabry Disease | Fabry Disease, Cardiac VariantUnited States, Australia, United Kingdom
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Genzyme, a Sanofi CompanyTerminatedFabry Disease | Alpha Galactosidase A DeficiencyUnited States, Austria, United Kingdom
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4D Molecular TherapeuticsActive, not recruiting
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4D Molecular TherapeuticsActive, not recruitingFabry DiseaseUnited States
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Amicus TherapeuticsActive, not recruitingPompe DiseaseUnited States, Netherlands, United Kingdom, Australia, Germany, New Zealand
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TakedaAvailableHunter SyndromeUnited States, Australia, Mexico, Spain, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II;Pompe's DiseaseCzechia, Taiwan, Belgium, Germany, Korea, Republic of, United States, Argentina, Australia, Austria, Brazil, Canada, Denmark, France, Hungary, Italy, Japan, Mexico, Netherlands, Poland, Portugal, Russian Federation, Spain, Switzerland, Turk... and more
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Amicus TherapeuticsEngage Health Inc.CompletedFabry DiseaseUnited States
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Phoenix NestNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationSanfilippo Syndrome Type DUnited States
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TakedaCompletedGaucher DiseaseUnited States
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University Hospital, BordeauxMinistry for Health and Solidarity, FranceCompletedBrain Injury | Atrial Fibrillation | Venous Thromboembolism | Valvular Heart Disease | Inappropriate Prescribing | Anticoagulant Drugs | Healthcare Quality IndicatorsFrance
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IAUnited States, Brazil, Canada, Denmark, Germany, Italy, Netherlands, Spain
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Prevail TherapeuticsEli Lilly and CompanyActive, not recruitingGaucher Disease, Type 2United States, United Kingdom
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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Haukeland University HospitalNorwegian Armed Forces Medical ServiceCompletedTrauma | Austere Environment | Blood Bank | Buddy TransfusionNorway
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Genzyme, a Sanofi CompanyCompleted
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IUnited States, Brazil, Japan
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIJapan
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Region SkaneLund University; Skane University HospitalEnrolling by invitationNon-ischaemic Heart Preservation Versus Standard Cold Storage in Human Heart Transplantation (NIHP2)Transplant; Failure, HeartSweden
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Bio Sidus SACompleted
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Leipzig University Medical CenterEuropean Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyGermany
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Temple UniversityMerck Sharp & Dohme LLCCompletedChronic Obstructive Pulmonary Disease | Neuromuscular BlockadeUnited States
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Caroline Michaela KistorpRigshospitalet, Denmark; Amicus TherapeuticsActive, not recruiting
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IntraBio IncCompletedGM2 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Germany, Spain, United Kingdom
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Genzyme, a Sanofi CompanyActive, not recruiting
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Cedars-Sinai Medical CenterActive, not recruiting
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SanofiCompletedFabry DiseaseUnited Arab Emirates
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico