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Search clinical trials for: Acid Lipase Deficiency
Total 35923 results
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BioMarin PharmaceuticalCompleted
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletedUrea Cycle Disorders, Inborn | Urea Cycle Disorder | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
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National Institute of Allergy and Infectious Diseases...National Institute on Drug Abuse (NIDA); Eunice Kennedy Shriver National Institute... and other collaboratorsCompletedHIV InfectionsZimbabwe, South Africa, Tanzania, Uganda
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Rajagopal V SekharNational Institute on Aging (NIA)Completed
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsUnited States, South Africa, Thailand
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CENTOGENE GmbH RostockWithdrawnMetabolic Disorders | Tyrosinosis | Hepatorenal Tyrosinemia | Fumarylacetoacetase Deficiency | Fah DeficiencyGermany, Sri Lanka, India
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CENTOGENE GmbH RostockWithdrawnIntellectual Disability | Developmental Delay | Intractable Epilepsy | Movement Disorder | Behavioral DisorderIndia, Sri Lanka, Egypt
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CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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National Institute of Allergy and Infectious Diseases...Microbicide Trials NetworkCompleted
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Peking Union Medical College HospitalGilead SciencesActive, not recruiting
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National Institute of Allergy and Infectious Diseases...Active, not recruitingHIV InfectionsSouth Africa, Uganda, Malawi, Zimbabwe
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Ultragenyx Pharmaceutical IncCompletedOrnithine Transcarbamylase (OTC) DeficiencyUnited Kingdom, United States, Canada, Spain
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Johns Hopkins UniversityNational Institute of Allergy and Infectious Diseases (NIAID); CONRADCompletedHIV/AIDS | HIV PreventionUnited States
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Ira FoxTerminated
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Radboud University Medical CenterCompletedEpilepsy | Ketogenic Dieting | Lactic Acid Blood Increased | GLUT1DS1 | GLUT1 Deficiency Syndrome | GLUT1DS2Netherlands
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsUnited States, South Africa, Thailand, Botswana, Brazil, Tanzania, Zimbabwe, India, Uganda
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Ultragenyx Pharmaceutical IncTerminatedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States
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Columbia UniversityTerminated
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Ottawa Hospital Research InstituteGilead Sciences; CIHR Canadian HIV Trials NetworkCompletedHepatitis C, Chronic | Human Immunodeficiency VirusCanada
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Arrowhead Regional Medical CenterCompletedBurns | Ascorbic Acid Deficiency | Fluid and Electrolyte Imbalance | Burn Degree Second | Burn Degree Third | Burn ShockUnited States
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Instituto de Investigación Sanitaria de la Fundación...Completed
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University Medical Centre LjubljanaCompletedCerebral Palsy | Metabolism, Inborn Errors | Developmental Delay | Genetic DiseaseSlovenia
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Johns Hopkins UniversityNational Institute of Allergy and Infectious Diseases (NIAID)CompletedHuman Immunodeficiency VirusUnited States
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Fenway Community HealthMerck Sharp & Dohme LLCCompleted
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Johns Hopkins Bloomberg School of Public HealthJohns Hopkins University; United States Agency for International Development... and other collaboratorsCompletedPreterm Birth | Low Birth Weight | Infant Mortality | Perinatal Mortality | Neonatal MortalityUnited States, Bangladesh
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Merck Sharp & Dohme LLCWithdrawnHuman Immunodeficiency Virus (HIV) Infections
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National Heart, Lung, and Blood Institute (NHLBI)CompletedArterial Calcification | CD73 DeficiencyUnited States
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Royal Surrey County Hospital NHS Foundation TrustCompletedColorectal Cancer | Sarcopenia | Surgery | Surgery--Complications | Surgical Site Infection | Nutritional Deficiency | Complication, Postoperative | Infected Wound | Phagocytic DysfunctionUnited Kingdom
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Janssen Sciences Ireland UCCompletedImmunodeficiency Virus Type 1, HumanUnited States, France, Poland, United Kingdom, Belgium, Germany, Spain, Canada, Russian Federation, Puerto Rico
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National Center for Women and Children's Health...National Center for AIDS/STD Control and Prevention, China CDC; Guangdong Provincial... and other collaboratorsCompleted
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHIV InfectionsMalawi, South Africa, Zimbabwe, Uganda
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HIV Prevention Trials NetworkCompletedHIV InfectionsUnited States, South Africa, Thailand
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SanofiApproved for marketing
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The University of The West IndiesInternational Atomic Energy AgencyCompletedNutrition Deficiency Due to A Particular Kind of FoodJamaica
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Enrique GinzburgGrifols Biologicals, LLCTerminatedCovid19 | Antithrombin III DeficiencyUnited States
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Galderma R&DCompletedVolume Deficiency of the MidfaceGermany, Italy, United Kingdom
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Pompe DiseaseUnited States
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University Hospital, AkershusOslo University Hospital; University Hospital of North Norway; University of... and other collaboratorsActive, not recruitingAtaxia TelangiectasiaNorway
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University of CincinnatiGilead Sciences; AbbottCompleted
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Beth Israel Deaconess Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)TerminatedShock | Cardiac Arrest | Lactic Acidosis | Thiamin DeficiencyUnited States
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Fresenius KabiWithdrawnMalnutrition | Pediatric ALL | Neurocognitive Deficit | Parenteral Nutrition Associated Liver Disease | Essential Fatty Acid Deficiency
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Wits Health Consortium (Pty) LtdLondon School of Hygiene and Tropical Medicine; King's College London; Karolinska... and other collaboratorsCompleted
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Radboud University Medical CenterA-T Children's Project; Twan foundation (https://twanfoundation.nl)CompletedAtaxia Telangiectasia | ATM Gene MutationNetherlands
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedHIV InfectionsUnited States, Puerto Rico, Thailand, Botswana, Argentina, Brazil, Tanzania, South Africa
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedIron-deficiency | Anemia | Iron Deficiency Anemia | Iron Deficiency Anemia Treatment | Blood Loss Anemia | Erythropoiesis AbnormalItaly
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Homology Medicines, IncEnrolling by invitationPhenylketonuria | PAH DeficiencyUnited States
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Johnson & Johnson Pte LtdTerminatedHuman Immunodeficiency Virus InfectionsIndia
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Fundacion SEIMC-GESIDAJanssen-Cilag, S.A.Completed