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Search clinical trials for: Lysosomal acid lipase deficiency
Total 36860 results
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Galderma R&DCompletedMidface Volume DeficitChina
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University of PennsylvaniaJohns Hopkins University; Eunice Kennedy Shriver National Institute of Child... and other collaboratorsCompletedHIV/AIDS | HIV PreventionUnited States
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Azafaros A.G.Active, not recruitingGM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Brazil, France, Germany, Italy, United Kingdom
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Liverpool John Moores UniversityCompletedEnergy Supply; Deficiency | Carbohydrate AvailabilityUnited Kingdom
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Merck Sharp & Dohme LLCActive, not recruitingProphylaxis | Human Immunodeficiency Virus Type 1 | HIV-IUnited States, South Africa, Uganda
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Saint Michael's Medical CenterViiV HealthcareActive, not recruitingHuman Immunodeficiency VirusUnited States
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Homology Medicines, IncTerminatedPhenylketonuria | Phenylketonurias | PAH DeficiencyUnited States
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Merck Sharp & Dohme LLCCompleted
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University of NebraskaCompletedCholestasis | Parenteral Nutrition Associated Liver Disease PNALDUnited States
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Fundação Bahiana de InfectologiaGlaxoSmithKlineCompletedHIV Infections | Pregnancy Related | Mother to Child TransmissionBrazil
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Boston Medical CenterViiV HealthcareCompletedHIV InfectionsUnited States
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Hospitales Universitarios Virgen del RocíoInstituto de Biomedicina de SevillaEnrolling by invitationHepatitis, Viral, Human | HIV Infection Primary | Sexually Transmitted Infections, Excluding HIV and HepatitisSpain
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ViiV HealthcareJanssen Research and DevelopmentCompletedHuman Immunodeficiency Virus Type 1 (HIV-1)Germany, Spain, United States, Italy, Canada, Argentina, Sweden
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Centre For International HealthTribhuvan University, Nepal; NORCE Norwegian Research Centre ASActive, not recruitingDevelopment | Malnutrition | Vitamin DeficiencyNepal
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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IntraBio IncActive, not recruitingNiemann-Pick Disease, Type CUnited States, Australia, United Kingdom, Germany, Slovakia, Netherlands, Czechia, Switzerland
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Greenwood Genetic CenterCompletedGalactosialidosis | Sialidosis | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Beta Mannosidosis | Mucolipidosis II | Mucolipidosis III | Schindler DiseaseUnited States
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ProtalixChiesi Farmaceutici S.p.A.CompletedFabry DiseaseUnited States, Serbia, Spain, United Kingdom, Australia, Paraguay
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Fundacion para la Investigacion Biomedica del Hospital...Completed
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Daniel BenjaminEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHeart Failure | Epilepsy | Pain | Pneumonia | Sepsis | Inflammation | Hypertension | Chronic Kidney Diseases | Hemophilia | Schizophrenia | Central Nervous System Infections | Nosocomial Pneumonia | Insomnia | Anxiety | Bipolar Disorder | Neutropenia | Staphylococcal Infections | Bradycardia | Seizures | Urinary Tract Infections | Pulmonary... and other conditionsUnited States, Canada, United Kingdom, Israel, Singapore
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Groupe Maladies hémorragiques de BretagneCompletedFactor VIII Deficiency | Desmopressin | Carrier of Hemophilia AFrance
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AlexionAchillion, a wholly owned subsidiary of AlexionCompletedHIV InfectionsUnited States, Puerto Rico
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Homology Medicines, IncTerminated
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AlexionAchillion, a wholly owned subsidiary of AlexionCompletedHIV InfectionsUnited States
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ViiV HealthcareGlaxoSmithKline; PPDCompletedHIV Infections | Infection, Human Immunodeficiency VirusTaiwan, France, Germany, Belgium, United States, Canada, Netherlands, Spain, Korea, Republic of, Italy, Australia, United Kingdom, Russian Federation, Portugal, Argentina, South Africa, Romania, Mexico
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ViiV HealthcareCompletedHIV InfectionsUnited States
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Oklahoma State University Center for Health SciencesActive, not recruiting
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University of California, San FranciscoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Tufts... and other collaboratorsCompletedVitamin B1 Deficiency | Thiamine DeficiencyUnited States
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AlexionAchillion, a wholly owned subsidiary of AlexionCompletedHIV InfectionsUnited States
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AlexionAchillion, a wholly owned subsidiary of AlexionCompletedHuman Immunodeficiency Virus (HIV)-1 InfectionUnited States, Spain, Germany, Dominican Republic
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National Institute of Allergy and Infectious Diseases...ViiV HealthcareSuspendedHIV Infection | LTBIUnited States, Haiti, Botswana, Brazil, Thailand, Zimbabwe, Malawi, Peru, South Africa
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsSouth Africa, Uganda, Malawi, Zimbabwe
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Ultragenyx Pharmaceutical IncCompletedCarnitine Palmitoyltransferase (CPT I or CPT II) Deficiency | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine-acylcarnitine Translocase (CACT) DeficiencyUnited States, United Kingdom
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University of Alabama at BirminghamCompletedFolic Acid Deficiency | Neural Tube Defects | FortificationUnited States
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Chiesi Farmaceutici S.p.A.Completed
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Chiesi Farmaceutici S.p.A.CompletedAlpha-MannosidosisFrance
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Aeglea BiotherapeuticsTerminatedHomocystinuria Due to Cystathionine Beta-Synthase DeficiencyUnited States, United Kingdom, Australia
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Augusta UniversityCompletedVascular Diseases | Body Weight Changes | Cardiovascular Abnormalities | HIV-1-infection | Body Fat Disorder | HIV-Associated Lipodystrophy Syndrome | Antiviral Drug Adverse Reaction | Abnormality of Adipose TissueUnited States
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Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Italy, Canada, France, United Kingdom, Austria, Germany
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Kirby InstituteActive, not recruitingHIV InfectionsMalaysia, Zimbabwe, India, South Africa, Thailand
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Thomas Jefferson UniversityCompletedGender Dysphoria | Transgender Women | Transgender Health | Human Immunodeficiency VirusUnited States
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Merck Sharp & Dohme LLCCompletedHuman Immunodeficiency Virus (HIV) InfectionUnited States
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National Institute of Allergy and Infectious Diseases...CompletedHIV InfectionsSouth Africa
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Medical University of South CarolinaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedChronic PancreatitisUnited States
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Boston UniversityNational Institute on Alcohol Abuse and Alcoholism (NIAAA)CompletedHIV Infection | Alcohol Consumption | Falls | Falls, AccidentalUnited States
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedHIV InfectionsUnited States, South Africa, Thailand, Botswana
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom