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Search clinical trials for: Metabolic abnormality
Total 77291 results
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Institut de Myologie, FranceRoche Pharma AGNot yet recruitingMuscular Atrophy, Spinal, Type II | Muscular Atrophy, Spinal, Type IIIFrance
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Hospital Universitari Vall d'Hebron Research InstituteHospital Universitario La PazNot yet recruitingHereditary Angioedema With C1 Esterase Inhibitor DeficiencySpain
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APR Applied Pharma Research s.a.Recruiting
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Phoenix NestAparito Ltd.; Vaincres Les Maladies Lysosomales; Association Sanfilippo SudNot yet recruitingSanfilippo Syndrome Type CUnited States, France
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King Faisal Specialist Hospital & Research Centre...RecruitingCongenital Heart Disease in Children | Post-cardiac Surgery | Malnutrition, InfantSaudi Arabia
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Hellenic Atherosclerosis SocietyNot yet recruitingFamilial Hypercholesterolemia
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CSL BehringRecruitingHereditary Angioedema (HAE)United States, Germany, Israel, Australia, Canada
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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University of LausanneRecruiting
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Assiut UniversityNot yet recruiting
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...RecruitingGoutUnited States, Georgia, Australia, Guatemala, Taiwan
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JW PharmaceuticalRecruitingGoutKorea, Republic of
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Katarzyna HolcmanRecruitingTransthyretin AmyloidosisPoland
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Washington University School of MedicinePolaris GroupRecruitingSoft Tissue Sarcoma | Sarcoma,Soft Tissue | StsUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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Qianfoshan HospitalRecruitingIron Deficiency Anemia of Pregnancy | Iron Storage DiseaseChina
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National Taiwan University HospitalMackay Memorial Hospital; Taipei Veterans General Hospital, Taiwan; Taiwan Adventist...Not yet recruitingPostpartum Depression | Gestational Diabetes Mellitus | Perinatal Depression
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RenJi HospitalWestlake TherapeuticsNot yet recruiting
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Central Hospital, Nancy, FranceNot yet recruitingAlzheimer Disease | Homocystinemia
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Assiut UniversityNot yet recruitingClinical Outcome in WILSON Disease
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GeneCradle IncRecruitingPompe Disease Infantile-OnsetChina
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Children's Hospital of Fudan UniversityRecruitingPrader-Willi SyndromeChina
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Amir MoheetCystic Fibrosis FoundationRecruiting
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Massachusetts General HospitalRecruiting
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Centre Hospitalier Universitaire de Pointe-a-PitreDirection Générale de l'Offre de SoinsRecruitingDyslipidemia | Sickle Cell Disease | ComplicationFrance
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Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
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Bispebjerg HospitalRecruitingErythropoietic ProtoporphyriaDenmark
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Assiut UniversityNot yet recruitingThalassemia Major
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Istituto Auxologico ItalianoRecruitingPrader-Willi SyndromeItaly
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Medical University of South CarolinaRecruitingSoft Tissue SarcomaUnited States
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University Hospital, GrenobleRecruitingAngio Edema HereditaryFrance
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University Hospital Inselspital, BerneRecruitingCerebral Small Vessel Diseases | Intracerebral Hemorrhage | CAA - Cerebral Amyloid AngiopathySwitzerland
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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Emory UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingCystic Fibrosis | Cystic Fibrosis-related DiabetesUnited States
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Istituto Ortopedico RizzoliRecruitingScoliosis Idiopathic | Genu Varum | Flat Feet | Hyperlordosis | Hyperkyphosis | Laxity of Ligament | Genu Valgus | Cavus Foot | Varus; Talipes | Valgus, Talipes | Angular Limb DeformityItaly
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Azienda Ospedaliero-Universitaria CareggiRecruitingSoft Tissue SarcomaItaly
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Odense University HospitalRecruitingAtherosclerosis | Familial HypercholesterolemiaDenmark
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Aswan University HospitalRecruiting
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Baylor College of MedicineRecruitingObesity, Childhood | Genetic DiseaseUnited States
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büşra başpınarRecruitingGlucose Metabolism Disorders | Cystic FibrosisTurkey
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Centre Hospitalier Saint Joseph Saint Luc de LyonRecruitingGout ArthritisFrance
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ProtalixRecruiting
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Centre Leon BerardRecruiting
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Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
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Inozyme PharmaRecruitingPseudoxanthoma Elasticum | Generalized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 Deficiency | ATP-Binding Cassette Subfamily C Member 6 DeficiencyUnited States, United Kingdom, Spain
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University of AberdeenNot yet recruitingCancer | Sickle Cell Disease | Immunosuppression | Inborn Errors of Metabolism | Organ Transplant | COPD Asthma
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University Hospital Inselspital, BerneRecruitingCerebral Amyloid Angiopathy | Cadasil | Small Vessel Cerebrovascular Disease | CAA - Cerebral Amyloid AngiopathySwitzerland