- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: PCT sporadic or familial
Total 206990 results
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HomozygousGreece, Lebanon, Turkey, France, Canada, Malaysia, Netherlands, United States
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Kyowa Kirin Co., Ltd.Kyowa Hakko Kirin Pharma, Inc.Completed
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Ultragenyx Pharmaceutical IncKyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia | Hypophosphatemic RicketsUnited States, Brazil, Argentina, Canada, Chile, Colombia
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Columbia UniversityActive, not recruitingSickle Cell Disease | Beta ThalassemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of MiamiNational Institute on Drug Abuse (NIDA)CompletedDrug Use | Sexual Risk Behavior | Family FunctioningUnited States
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Washington University School of MedicineHoffmann-La Roche; Genentech, Inc.; National Institute on Aging (NIA); Alzheimer...SuspendedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, Italy, France, Spain, Ireland, Argentina, Australia, Colombia, Germany, Mexico, Netherlands, Puerto Rico, United Kingdom
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National Human Genome Research Institute (NHGRI)CompletedGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets Type2United States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)SuspendedLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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Regeneron PharmaceuticalsTerminatedFamilial Partial Lipodystrophy | Metabolic AbnormalitiesUnited States, France, Spain, Turkey
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Merck Sharp & Dohme LLCActive, not recruitingPulmonary Arterial Hypertension | Hypertension, PulmonaryUnited States, Argentina, Australia, Belgium, Canada, Colombia, France, Germany, Greece, Israel, Italy, Mexico, New Zealand, Poland, Russian Federation, Sweden, Turkey, United Kingdom
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AOP Orphan Pharmaceuticals AGEnrolling by invitationPulmonary Arterial HypertensionFrance, Spain, Germany, Italy, Hungary, Austria, Czechia, Poland, Romania
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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Diane GeorgeActive, not recruitingAcute Lymphoblastic Leukemia (ALL) | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML) | Chronic Myeloid Leukemia (CML) | Juvenile Myelomonocytic Leukemia (JMML) | Lymphoma (Hodgkin's and Non-Hodgkin's)United States
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Ultragenyx Pharmaceutical IncKyowa Kirin Co., Ltd.AvailableX-linked Hypophosphatemia | Tumor-Induced Osteomalacia
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University of PittsburghNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedHypertension | Diabetes Mellitus | High Blood Pressure | High Blood SugarUnited States
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University of PittsburghBoston University; National Heart, Lung, and Blood Institute (NHLBI); Northeastern...CompletedPathologic Processes | Heart Diseases | Atrial Fibrillation | Arrythmia, Cardiac | Familial Atrial FibrillationUnited States
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Inozyme PharmaActive, not recruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, Canada, Germany, France, United Kingdom
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AmgenCompletedHomozygous Familial Hypercholesterolemia HoFHIndia
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Mirum Pharmaceuticals, Inc.Active, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)United States, Argentina, France, Singapore, United Kingdom, Belgium, Turkey, Austria, Brazil, Canada, Colombia, Germany, Italy, Lebanon, Mexico, Poland
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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National Cancer Institute (NCI)CompletedFamilial Ovarian Cancer | Familial Breast Cancer | BRCA1-associate Malignancies | BRCA2-associated MalignanciesUnited States
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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White Plains HospitalActive, not recruitingPancreatic Cancer | Pancreatic Adenocarcinoma | Lynch Syndrome | Pancreas Cancer | HNPCC | Familial Pancreatic Cancer | Hereditary Pancreatitis | BRCA 1/2 | FAMMM | Familial Atypical Multiple Mole Melanoma | Peutz Jeghers SyndromeUnited States
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United TherapeuticsEnrolling by invitationCardiovascular Diseases | Vascular Diseases | Lung Diseases | Hypertension | Connective Tissue Diseases | Pulmonary Arterial Hypertension | Familial Primary Pulmonary Hypertension | Hypertension, Pulmonary | Pulmonary Hypertension | PAH | Respiratory Tract DiseaseUnited States, Spain, Australia, Taiwan, Canada, Singapore, United Kingdom, Italy, Germany, China, Mexico, Argentina, Korea, Republic of, Austria, Greece, Sweden, Portugal, Belgium, Brazil, Bulgaria, Chile, Croatia, Czechia, Denmark, Fr... and more
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University of OregonNational Institute on Drug Abuse (NIDA)Active, not recruitingDepression | Stress | Parent-Child Relations | Parenting | Executive Function | Opioid Use Disorder | Opioid Misuse | Parenting Self-efficacyUnited States
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Washington University School of MedicineHoffmann-La Roche; National Institute on Aging (NIA); Alzheimer's AssociationTerminatedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, France, Spain, Ireland, Canada, Australia, Puerto Rico, United Kingdom
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Janssen-Cilag S.p.A.CompletedPulmonary Arterial HypertensionItaly
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Northwestern UniversityNational Institute on Aging (NIA)Active, not recruitingCognitive Impairment | Alzheimer DiseaseUnited States
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Organon and CoMerck Sharp & Dohme LLCCompleted
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Alnylam PharmaceuticalsApproved for marketingAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
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National Cancer Institute (NCI)Active, not recruitingSmoldering Multiple Myeloma | Refractory Multiple Myeloma | DS Stage I Multiple Myeloma | DS Stage II Multiple Myeloma | DS Stage III Multiple MyelomaUnited States
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaColombia, Israel, Taiwan, United States, Argentina, China, Germany, Italy, Japan, Korea, Republic of, Mexico, South Africa, Spain, Turkey
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Organon and CoCompletedHypercholesterolemia | Familial Hypercholesterolemia
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State University of New York - Upstate Medical...National Institute of Mental Health (NIMH)CompletedMental Disorders | Mental Disorders Diagnosed in Childhood | Psychological Disorders | Psychiatric, DiagnosisUnited States
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Organon and CoCompleted
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Organon and CoCompletedHypercholesterolemia | Heterozygous Familial Hypercholesterolemia
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PfizerCompletedPolyneuropathy | Hereditary Transthyretin Amyloidosis (ATTRv)Spain
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Universitätsklinikum Hamburg-EppendorfFederal Joint Committee; aQua-Institut GmbH, Germany; Leibniz-Institut für Resilienzforschung... and other collaboratorsActive, not recruitingDisabled or Chronically Ill Children in Need of CareGermany
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Centre Hospitalier Henri Duffaut - AvignonTerminatedCOVID-19 Acute Respiratory Distress SyndromeFrance
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Johns Hopkins UniversityPentax MedicalActive, not recruitingFamilial Adenomatous Polyposis | Duodenal AdenomasUnited States
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HighTide Biopharma Pty LtdShenzhen HighTide Biopharmaceutical Ltd.Completed
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Organon and CoCompleted
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University of Texas at AustinBoys & Girls Clubs of the Austin AreaActive, not recruiting'Food, Fun, Fresh, Family' Program for Healthy Eating and Growth for Elementary-age Children. (FUEL)Diet, Healthy GrowthUnited States
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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Merck Sharp & Dohme LLCActive, not recruitingPulmonary Arterial HypertensionJapan