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Search clinical trials for: Late Onset Lysosomal Acid Lipase Deficiency (CESD)
Total 42347 results
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Sidney Kimmel Comprehensive Cancer Center at Johns...RecruitingPrimary Immune Deficiency Disorder | Bone Marrow Failure | Immune Deficiency DiseaseUnited States
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Massachusetts General HospitalNational Institute of Allergy and Infectious Diseases (NIAID); AIDS Healthcare...RecruitingSTI | Contraceptive Usage | Pre-Exposure ProphylaxisSouth Africa
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Institut de Médecine et d'Epidémiologie Appliquée...Pierre and Marie Curie UniversityRecruiting
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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AmgenRecruitingAdvanced Solid Tumors | Kirsten Rat Sarcoma (KRAS) pG12C MutationUnited States, Italy, Taiwan, Spain, United Kingdom, Australia, Austria, Germany, Belgium, Japan, Netherlands, Korea, Republic of, Canada
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Erasmus Medical CenterRecruiting
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ProgenaBiomeRecruitingAlzheimer Disease | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | Alzheimer Disease 1 | Alzheimer Disease 2 | Alzheimer Disease 3 | Alzheimer Disease 4 | Alzheimer Disease 7 | Alzheimer Disease 17 | Alzheimer Disease 5 | Alzheimer Disease 6 | Alzheimer Disease 8 | Alzheimer Disease 10 | Alzheimer... and other conditionsUnited States
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First Affiliated Hospital, Sun Yat-Sen UniversityRecruitingStroke | G6PD DeficiencyChina
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Michael MorowitzEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMicrobial Colonization | Late-Onset Neonatal Sepsis | Necrotizing Enterocolitis of Newborn | Extreme Prematurity | Death; Neonatal | Early-Onset Neonatal SepsisUnited States, Canada
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Wrightington, Wigan and Leigh NHS Foundation TrustTRB ChemedicaRecruitingLateral Epicondylitis | Tennis Elbow | Elbows TendonitisUnited Kingdom
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University of Colorado, DenverRecruitingDiabetes Mellitus, Type 2 | Diabetes | Diabetes Complications | Type 2 Diabetes Mellitus | Diabetic Kidney Disease | Diabetic Nephropathies | Type2 Diabetes | HyperuricemiaUnited States
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CSL BehringRecruitingAcute-graft-versus-host DiseaseUnited States, Korea, Republic of, Spain, Australia, Germany, Italy, Turkey, Japan
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingTuberculosis | Human Immunodeficiency Virus | CoinfectionGhana
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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University of OuluOulu University HospitalRecruitingSurfactant Deficiency Syndrome NeonatalFinland
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University of Maryland, BaltimoreVA Maryland Health Care SystemRecruitingAccidental FallsUnited States
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Centers for Disease Control and PreventionJohns Hopkins University; Sanofi; University of Stellenbosch; University of Cape... and other collaboratorsRecruiting
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Huilian ZhuNot yet recruiting
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Capital Medical UniversityPeking University First Hospital; The First Affiliated Hospital of Anhui Medical... and other collaboratorsRecruitingAlzheimer Disease, Late Onset | Mild Cognitive Impairment(MCI) | Familial Alzheimer Disease (FAD) | Vascular Dementia (VaD) | Normal Control | Non-Alzheimer Degenerative DementiaChina
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National Institute of Allergy and Infectious Diseases...ViiV HealthcareRecruitingHIV InfectionsUnited States, Puerto Rico
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Beijing Children's HospitalHopital Universitaire Robert-Debre; Shandong University; Rennes University HospitalRecruiting
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Radboud University Medical CenterMaastricht University Medical Center; Erasmus Medical Center; Catharina Ziekenhuis... and other collaboratorsRecruitingEndometrial Cancer Recurrent | Endometrial Cancer Stage III | Endometrial Cancer Stage IVNetherlands
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Baylor College of MedicineThe Methodist Hospital Research InstituteRecruiting
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Centers for Disease Control and PreventionBritish Medical Research CouncilRecruitingLatent TuberculosisAustralia, United States, Canada, South Africa
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Washington University School of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingNiemann-Pick Disease, Type CUnited States
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University of NebraskaRecruitingRheumatoid ArthritisUnited States
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Unity Health TorontoCanadian Institutes of Health Research (CIHR); CIHR Canadian HIV Trials NetworkRecruiting
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Groupe Francophone des MyelodysplasiesRecruitingMyelodysplastic SyndromesFrance
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University of California, San FranciscoMassachusetts General HospitalRecruitingCardiovascular Diseases | HIV Infections | DyslipidemiasUnited States
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AB ScienceRecruitingAmyotrophic Lateral SclerosisFrance, Spain, United States, Sweden, Denmark, Portugal, Italy, Israel, Germany, Norway, Poland, Russian Federation, Slovenia, Ukraine, Greece, Belgium, Serbia
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ANRS, Emerging Infectious DiseasesRecruiting
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Travere Therapeutics, Inc.RecruitingNatural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)Homocystinuria Due to CBS DeficiencyIreland, Qatar, United States, United Kingdom
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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Assistance Publique - Hôpitaux de ParisRecruiting
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MD Stem CellsRecruitingStroke | Nervous System Diseases | Diabetic Neuropathies | Neurodegenerative Diseases | Cognitive Impairment | Amyotrophic Lateral Sclerosis | Dementia | Neurological Disorders | Alzheimer Disease | ALS | Traumatic Brain Injury | Cerebral Infarction | Lewy Body Disease | Cerebral Hemorrhage | Frontotemporal Dementia | Progressive... and other conditionsUnited States, United Arab Emirates
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Mayo ClinicRecruitingCystinuria | Hyperoxaluria | Dent Disease | Lowe Syndrome | Adenine Phosphoribosyltransferase DeficiencyUnited States, Canada, Iceland, Israel
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Ataxia Study GroupGerman Center for Neurodegenerative Diseases (DZNE)RecruitingLate Onset Sporadic Cerebellar AtaxiaNorway, Austria, Germany, Netherlands, Italy
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Nemours Children's ClinicRecruitingCharcot-Marie-Tooth Disease | Motor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Muscular Atrophy | Neuromuscular Disease | Spinal Muscular Atrophy With Respiratory Distress 1 | Peroneal Muscular AtrophyUnited States
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Tel-Aviv Sourasky Medical CenterRambam Health Care Campus; Rabin Medical Center; Sheba Medical Center; Soroka University...Not yet recruitingLynch Syndrome I (Site-specific Colonic Cancer)Israel
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Pascoe Pharmazeutische Praeparate GmbHRecruitingChronic Disease | Acute Disease | Vitamin C DeficiencyGermany
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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Gilead SciencesRecruitingHIV Infections | Acquired Immune Deficiency Syndrome (AIDS)United States, South Africa, Argentina, Panama, Thailand, Zimbabwe, United Kingdom, Uganda
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Johns Hopkins UniversityNational Cancer Institute (NCI); National Institutes of Health (NIH); ChiRhoClin...RecruitingLynch Syndrome | Pancreas Cancer | Gene Mutation | Peutz-Jeghers Syndrome (PJS) | Germline Mutation CarrierUnited States
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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National Cancer Institute (NCI)RecruitingMDS | Immunodeficiency | GATA2United States
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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National Eye Institute (NEI)RecruitingRetinal Degeneration | Retinitis Pigmentosa | Retinal Disease | AMDUnited States
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States