- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: To identify genetic alterations with prognostic relevance.
Total 480663 results
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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University of California, Los AngelesRecruitingTuberous SclerosisUnited States
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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University Hospital, ToulouseNot yet recruitingFamilial Adenomatous PolyposisFrance
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M.D. Anderson Cancer CenterNovartis PharmaceuticalsNot yet recruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome-PositiveUnited States
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argenxRecruitingThyroid Eye DiseaseUnited States
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BioMarin PharmaceuticalRecruitingIdiopathic Short StatureUnited States
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Hangzhou Yirui Pharmaceutical Technology Co., LtdNot yet recruitingAtopic DermatitisUnited States
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argenxRecruitingThyroid Eye DiseaseUnited States
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Halic UniversityRecruitingCystic Fibrosis | Cystic Fibrosis in ChildrenTurkey
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Kind Pharmaceuticals LLCNot yet recruiting
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States
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ARTHEx Biotech S.L.Recruiting
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Shanghai Institute Of Biological ProductsThe First Affiliated Hospital of Henan University of Science and Technology; First Affiliated Hospital Bengbu Medical College and other collaboratorsRecruiting
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Chia Tai Tianqing Pharmaceutical Group Nanjing...Not yet recruiting
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AstraZenecaRecruiting
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GENGERecruiting
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI); Cystic Fibrosis FoundationRecruitingCystic Fibrosis | Parenthood StatusUnited States
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Istituto Auxologico ItalianoRecruitingShort Stature | Short; Stature, PsychosocialItaly
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Istituto Auxologico ItalianoRecruitingPrader-Willi SyndromeItaly
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Istituto Auxologico ItalianoRecruitingGrowth Hormone Deficiency | Short StatureItaly
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ViGeneron GmbHRecruiting
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CorrectSequence Therapeutics Co., LtdRecruitingBeta-Thalassemia MajorChina
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Children's Hospital Medical Center, CincinnatiChildren's Hospital of Philadelphia; Emory University; Nemours Children's Health...Not yet recruiting
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Rege Nephro Co., Ltd.RecruitingAutosomal Dominant Polycystic Kidney Disease (ADPKD)Japan
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University Hospital, RouenNot yet recruiting
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Eli Lilly and CompanyRecruitingElevated Lp(a) | Atherosclerotic Cardiovascular Disease (ASCVD)United States, Australia, Spain, Canada, Argentina, China, Italy, France, Japan, Taiwan, Korea, Republic of, Denmark, Germany, Hungary, Israel, Austria, Belgium, Netherlands, Brazil, Mexico, Romania, United Kingdom, Greece, Czechia, Poland and more
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Ondokuz Mayıs UniversityRecruitingQuality of Life | Urinary Incontinence | Menopause | Wolman Disease | Psychological Well-BeingTurkey
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Australasian Leukaemia and Lymphoma GroupNot yet recruitingHigh-grade B-cell Lymphoma | DLBCL - Diffuse Large B Cell Lymphoma | High Grade B-Cell Lymphoma With MYC and BCL2 or BCL6 Rearrangements | DLBCL, Nos Genetic Subtypes | High Grade B-Cell Lymphoma, Not Otherwise Specified | Follicular Large Cell Lymphoma, Relapsed | Follicular Large Cell Lymphoma
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Staidson (Beijing) Biopharmaceuticals Co., LtdRecruiting
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Asklepios Biopharmaceutical, Inc.BayerNot yet recruiting
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Agios Pharmaceuticals, Inc.Not yet recruitingSickle Cell Disease | Nephropathy
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Oslo University HospitalNorwegian National Advisory Unit on Rare Disorders, Oslo University HospitalRecruitingCystic Fibrosis in ChildrenNorway
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Kirsehir Ahi Evran UniversitesiTC Erciyes UniversityNot yet recruitingChildren | Cystic Fibrosis | Lung Functions | Mothers | Laughter Yoga | Laughter Therapy | Resilience,Psychological | Psychological HealthTurkey
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Wuhan Union Hospital, ChinaNot yet recruitingMyelodysplastic Syndromes
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Perha PharmaceuticalsGöteborg University; Proteas BioanalyticsRecruiting
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, Turkey, United Kingdom, Italy
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Eli Lilly and CompanyRecruitingAtopic DermatitisChina, Korea, Republic of
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Keymed Biosciences Co.LtdNot yet recruiting
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Lynk Pharmaceuticals Co., LtdRecruitingAtopic DermatitisChina
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The Affiliated Hospital of Xuzhou Medical UniversityRecruitingType 2 Diabetes Mellitus | Genetic Mutations | Gene Polymorphisms | Susceptibility, GeneticChina
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingBeta-ThalassemiaUnited States
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Karolinska InstitutetRecruitingTourette Syndrome | Chronic Tic DisorderSweden
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Sarepta Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Investigación en Hemofilia y FisioterapiaRecruiting
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S.LAB (SOLOWAYS)Center of New Medical TechnologiesRecruiting
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Investigación en Hemofilia y FisioterapiaRecruiting
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Université de SherbrookeCanadian Institutes of Health Research (CIHR); Centre de recherche du Centre... and other collaboratorsNot yet recruiting