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Search clinical trials for: sphingolipidoses
Total 483 results
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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University Research Foundation for Lysosomal Storage...University of PittsburghCompletedGaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyWithdrawnGaucher Disease, Type 1United States, India
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCRL/MedinetTerminatedFabry Disease | Chronic Kidney Disease, Stage IV (Severe)United States
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseCzech Republic, Estonia, Poland, Slovakia
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, United Kingdom, Canada, Czech Republic, Hungary, Poland
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, France, Poland, United Kingdom
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Baylor Research InstituteNational Institute of Neurological Disorders and Stroke (NINDS)Completed
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University of CincinnatiChildren's Hospital Medical Center, CincinnatiTerminatedAdrenoleukodystrophy | Zellweger Syndrome | Infantile Refsum's Disease | Bifunctional Enzyme Deficiency
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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Children's Hospital Medical Center, CincinnatiCompletedOsteopenia | Gaucher's DiseaseIsrael, United States
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Genzyme, a Sanofi CompanyTerminatedNiemann-Pick Disease | Acid Sphingomyelinase DeficiencyUnited States
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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University of ZurichCompletedFabry DiseaseSwitzerland
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedTay Sachs Disease | Sandhoff Disease | Late Onset Tay Sachs DiseaseUnited States
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Shaare Zedek Medical CenterCompletedGaucher Disease Type 1Israel
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Shaare Zedek Medical CenterUnknownHepatitis C | Gaucher DiseaseIsrael
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Mario Negri Institute for Pharmacological ResearchTerminated
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Rigshospitalet, DenmarkCompletedFabry DiseaseDenmark
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Genzyme, a Sanofi CompanyCompleted
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Amicus TherapeuticsCompleted
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Wolfson Medical CenterUnknownFabry Disease in the Young StrokeIsrael
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University of ZurichCompleted
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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ProtalixCompleted
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Genzyme, a Sanofi CompanyWithdrawn
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ISU Abxis Co., Ltd.Completed
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, United Kingdom, Canada, Hungary, Poland, Czech Republic
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Amicus TherapeuticsCompleted
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Amicus TherapeuticsCompleted
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, France, Netherlands, Puerto Rico, United Kingdom
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University of Alabama at BirminghamCompleted
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University of Alabama at BirminghamCompletedProteinuria | Fabry DiseaseUnited States, Slovenia
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University Hospital, Clermont-FerrandUnknown
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Rambam Health Care CampusUnknown
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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ISU Abxis Co., Ltd.Completed
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Eunice Kennedy Shriver National Institute of Child...Washington University School of Medicine; University of Oxford; National Human...CompletedNiemann-Pick Disease, Type CUnited States
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University Hospital, BordeauxCompletedPain | Fabry's DiseaseFrance
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Johannes Gutenberg University MainzUnknownMucopolysaccharidosis | Fabry DiseaseGermany
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland...WithdrawnG(M2) Ganglioside | Tay-Sachs Disease Ganglioside | Sandhoff Disease GangliosideUnited States, Canada
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Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
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National Taiwan University HospitalCompleted
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Brigham and Women's HospitalGenzyme, a Sanofi CompanyUnknown