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Clinical Trials Sponsored by Myasthenia Gravis Rare Disease Network
Total 88 results
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Myasthenia Gravis Rare Disease NetworkRecruitingMyasthenia Gravis | MuSK Myasthenia Gravis | MuSK MGUnited States
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Huashan HospitalChina Alliance for Rare Diseases; National Center for Neurological Disorders... and other collaboratorsRecruiting
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic SyndromeUnited States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknownMyelodysplastic Syndromes | Purpura, Thrombocytopenic | Anemia, Aplastic | Red-Cell Aplasia, Pure | Bone Marrow Failure Syndromes | Hemoglobinuria, Paroxysmal | Leukemia, LymphocyticUnited States
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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University of California, Los AngelesRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedCerebellar Diseases | Episodic Ataxia SyndromeUnited States, Canada, United Kingdom
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Assistance Publique - Hôpitaux de ParisFrench rare diseases Healthcare Network; The French Foundation for Rare DiseasesActive, not recruitingAmelogenesis Imperfecta | Dentinogenesis Imperfecta | Dentin AnomaliesFrance
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletedUrea Cycle Disorders, Inborn | Urea Cycle Disorder | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
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University of RochesterNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedAndersen-Tawil Syndrome | Andersen SyndromeUnited States, Canada, Italy, United Kingdom
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University of California, DavisPediatric Emergency Care Applied Research NetworkNot yet recruitingBrain Injuries | Intracranial Hemorrhages | Diffuse Axonal Injury | Head Injury | Skull Fractures | Head Injury Trauma | Brain Injury Traumatic Mild | Brain Injuries, Acute | Head Injury With Intracranial Hemorrhage | Brain Injury Traumatic Focal With Loss of ConsciousnessUnited States
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTemporal ArteritisUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedPolyarteritis NodosaUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsRecruitingGiant Cell Arteritis | Microscopic Polyangiitis | Polyarteritis Nodosa | Takayasu's Arteritis | Eosinophilic Granulomatosis With Polyangiitis (Churg-Strauss) | Granulomatosis With Polyangiitis (Wegener's)United States, Canada, Turkey
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National Institute of Arthritis and Musculoskeletal...The Cleveland Clinic; Rare Diseases Clinical Research Network; Office of Rare...CompletedGiant Cell Arteritis | Takayasu's ArteritisUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedWegener's GranulomatosisUnited States
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMicroscopic Polyangiitis | Granulomatosis With Polyangiitis | Wegener'sUnited States, Canada
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University of PennsylvaniaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTakayasu's ArteritisUnited States, Canada
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... and other collaboratorsTerminatedAndersen-Tawil SyndromeUnited States
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Peter MerkelNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedTakayasu ArteritisUnited States, Canada
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Andrea GropmanNational Center for Research Resources (NCRR); Rare Diseases Clinical Research... and other collaboratorsCompletedBrain Diseases, Metabolic, Inborn | Ornithine Transcarbamylase Deficiency | Urea Cycle DisorderUnited States
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University of South FloridaNational Institutes of Health (NIH); Rare Diseases Clinical Research NetworkCompletedOsteogenesis Imperfecta | Brittle Bone DisordersUnited States
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University of South FloridaNational Institutes of Health (NIH); Rare Diseases Clinical Research NetworkCompletedOsteogenesis Imperfecta | Brittle Bone DisordersUnited States
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... and other collaboratorsCompletedErythropoietic Protoporphyria | EPP | XLP | X-Linked Protoporphyria | XLPP | X-Linked Dominant Erythropoietic Protoporphyria | XLEPP | XLDPUnited States
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University Hospital, LilleFAI²R (Auto-immune and auto-inflammatory rare diseases French network)TerminatedCovid19 | Inflammatory Rheumatism | Systemic Autoimmune Disease | Auto Inflammatory DiseasesFrance
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University Hospital, LilleFAI²R (Auto-immune and auto-inflammatory rare diseases French network)UnknownAutoimmune Diseases | Sars-CoV2 | Chronic Inflammatory RheumatismFrance
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University of ManitobaCanadian Primary Care Sentinel Surveillance Network; Canadians Seeking Solutions... and other collaboratorsRecruiting
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University of FloridaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedObesity | Prader-Willi SyndromeUnited States
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Hospital Universitari Vall d'Hebron Research InstituteERN-EuroBloodNet (European Reference Network on Rare Hematological DiseasesRecruitingLeukemia | Anemia | Iron Metabolism Disorders | Anemia, Sickle Cell | Thalassemia | Bleeding Disorder | Myeloma | Lymphoid Neoplasm | Blood Cancer | Bone Marrow Failure | Red Cell Membrane and Enzyme Abnormalities | Myeloma, MalignantSpain
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedPulmonary Langerhans Cell HistiocytosisUnited States
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University of CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedBirt-Hogg-Dube SyndromeUnited States
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...CompletedWiskott-Aldrich SyndromeUnited States, Canada
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National Institute of Allergy and Infectious Diseases...Rare Diseases Clinical Research Network; Primary Immune Deficiency Treatment...Enrolling by invitationGranulomatous Disease, ChronicUnited States, Canada
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Assistance Publique - Hôpitaux de ParisFAI²R (Auto-immune and auto-inflammatory rare diseases French network)Not yet recruitingAutoimmune Diseases | Rare Diseases | SARS-CoV2 Infection | Chronic Inflammatory RheumatismFrance
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RecruitingPyruvate Dehydrogenase Complex Deficiency DiseaseUnited States
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Children's Hospital Medical Center, CincinnatiNational Center for Research Resources (NCRR); Rare Diseases Clinical Research...CompletedPulmonary Alveolar ProteinosisUnited States, Germany, Italy, Japan
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Daniel Nishijima, MD, MASPediatric Emergency Care Applied Research NetworkNot yet recruitingHemorrhage | Brain Injuries, Traumatic | Trauma Injury | Wounds and Injury
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Daniel Nishijima, MD, MASPediatric Emergency Care Applied Research NetworkCompletedWounds and Injuries | Brain Injuries | HemorrhageUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type IUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGaucher Disease Type 1United States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsRecruitingGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Late Onset Tay-Sachs DiseaseUnited States
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EusaPharma (UK) LimitedUniversity of Sheffield (ScHARR); KMC Health Care; Castleman Disease Collaborative...Not yet recruitingIdiopathic Multicentric Castleman's Disease
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsTerminatedTay-Sachs Disease | Sandhoff Disease | GM1 Gangliosidoses | GM2 GangliosidosesUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown
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Brendan LeeEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedAmino Acid Metabolism, Inborn Errors | Urea Cycle Disorders | Argininosuccinic AciduriaUnited States
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Children's Hospital Medical Center, CincinnatiRare Diseases Clinical Research Network; National Center for Advancing Translational...CompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Rare Diseases Clinical Research...CompletedAutoimmune Pulmonary Alveolar ProteinosisUnited States
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Icahn School of Medicine at Mount SinaiEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedApparent Mineralocorticoid Excess SyndromeUnited States, Brazil, France
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompleted