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Clinical Trials Sponsored by Orphan Therapeutics
Total 6594 results
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Bacainn Therapeutics, Inc.CompletedHealthy VolunteersUnited States
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Celsus Therapeutics PLCTerminatedAtopic DermatitisIsrael
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Eikon TherapeuticsImpact Therapeutics, Inc.RecruitingAdvanced Solid TumorAustralia, United States
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APRINOIA Therapeutics, LLCActive, not recruitingAlzheimer Disease | Tauopathies | Healthy VolunteersUnited States
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CRISPR Therapeutics AGActive, not recruitingRenal Cell CarcinomaUnited States, Australia, Canada, Netherlands
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CRISPR Therapeutics AGRecruitingFollicular Lymphoma | B-cell Lymphoma | Mantle Cell Lymphoma | Marginal Zone Lymphoma | Non-Hodgkin Lymphoma | B-cell Malignancy | Large B-cell Lymphoma | Chronic Lymphocytic Leukemia (CLL)/Small Lymphocytic Lymphoma (SLL)United States
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CRISPR Therapeutics AGEnrolling by invitationHematologic Malignancy | Solid MalignancyUnited States
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CRISPR Therapeutics AGActive, not recruitingMultiple MyelomaUnited States, Spain, Australia, Canada
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APRINOIA Therapeutics, LLCActive, not recruitingHealthy Volunteers | Alzheimer's Disease | Mild Cognitive Impairment Due to Alzheimer's DiseaseUnited States
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Children's Hospital Los AngelesCompletedThrombosis | Heparin-induced ThrombocytopeniaUnited States
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University of North CarolinaCompleted
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FDA Office of Orphan Products DevelopmentChildren's Hospital of PhiladelphiaCompleted
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Brigham and Women's HospitalCompletedErythropoietic Protoporphyria
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompleted
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Dr. David SpanerSwedish Orphan BiovitrumUnknownChronic Lymphocytic Leukemia
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FDA Office of Orphan Products DevelopmentUniversity of North CarolinaCompleted
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FDA Office of Orphan Products DevelopmentCase Western Reserve UniversityCompleted
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Children's Hospital of PhiladelphiaCompleted
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Children's Hospital of PhiladelphiaCompleted
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Medical College of WisconsinFDA Office of Orphan Products DevelopmentTerminatedHemangiomaUnited States
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Hanny Al-Samkari, MDSwedish Orphan BiovitrumRecruitingGastrointestinal Neoplasms | Gastrointestinal Cancer | Chemotherapy-Induced ThrombocytopeniaUnited States
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Fondazione per la Ricerca Ospedale MaggioreAOP Orphan Pharmaceuticals AGCompleted
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Swedish Orphan BiovitrumKantar Health; Cerner Enviza (former Kantar Health)CompletedHemophilia A | Hemophilia BFrance
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AOP Orphan Pharmaceuticals AGPharmaEssentia Corporation (Co-Sponsor for USA)CompletedPolycythemia VeraAustria, Bulgaria, Czech Republic, France, Hungary, Poland, Slovakia, Ukraine
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Case Western Reserve UniversityTerminated
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University of North CarolinaCompletedSickle Cell AnemiaUnited States
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FDA Office of Orphan Products DevelopmentUniversity of Massachusetts, WorcesterCompletedJuvenile Rheumatoid Arthritis
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M.D. Anderson Cancer CenterCompletedLymphoproliferative Disorders | Leukemia | Hematologic Neoplasms | Leukemia, Lymphocytic, ChronicUnited States
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University of North CarolinaCompletedOsteoporosis | Cystic FibrosisUnited States
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CRISPR Therapeutics AGViaCyteRecruitingGlucose Metabolism Disorders | Immune System Diseases | Autoimmune Diseases | Diabetes Mellitus | Endocrine System Diseases | Diabetes Mellitus, Type 1 | Metabolic DiseaseCanada
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iCell Gene TherapeuticsiCar Bio TherapeuticsNot yet recruitingHigh Risk Hematologic Malignancies | Relapsed and/or Refractory Acute Myeloid LeukemiaChina
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Melinta Therapeutics, LLCRecruitingGram Positive Bacterial InfectionsUnited States
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TenNor Therapeutics LimitedCompletedGram-Positive Bacterial Infections | Skin and Subcutaneous Tissue Bacterial InfectionsUnited States
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CRISPR Therapeutics AGViaCyteCompletedGlucose Metabolism Disorders | Immune System Diseases | Autoimmune Diseases | Diabetes Mellitus | Endocrine System Diseases | Diabetes Mellitus, Type 1 | Metabolic DiseaseCanada
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BlackThorn Therapeutics, Inc.Neumora Therapeutics, Inc.CompletedMajor Depressive DisorderUnited States
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Sirion Therapeutics, Inc.ReVision Therapeutics, Inc.CompletedGeographic Atrophy | Dry Age Related Macular Degeneration
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Skyline Therapeutics (US) Inc.RecruitingNeovascular Age-related Macular DegenerationChina, United States
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iCell Gene TherapeuticsiCar Bio TherapeuticsRecruitingRelapsed/Refractory, High Risk Hematologic Malignancies | T-ALL/LymphomaChina
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Verismo TherapeuticsRecruiting
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Ractigen Therapeutics.RecruitingNon-Muscle-Invasive Bladder Cancer (NMIBC)Australia
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NeuShen TherapeuticsNot yet recruiting
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Monopar TherapeuticsRecruitingGastric Cancer | Colorectal Cancer | Pancreatic Cancer | Ovarian Cancer | Lung Cancer | Bladder Cancer | Urothelial Carcinoma | Triple-negative Breast Cancer | Solid Tumor, AdultAustralia
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vTv TherapeuticsNot yet recruitingDiabetes Mellitus, Type 1
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Enliven TherapeuticsRecruitingColorectal Cancer | HER2-positive Breast Cancer | HER2-positive Gastric Cancer | HER2 Amplification | HER2 Positive Solid TumorsUnited States
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OX2 TherapeuticsRecruitingDiffuse Midline Glioma, H3 K27M-Mutant | Recurrent High Grade GliomaUnited States
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Transcend TherapeuticsRecruitingA Single, Ascending Dose Evaluation of the Safety, Pharmacokinetics of Methylone in Healthy SubjectsPost Traumatic Stress DisorderAustralia
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Remix TherapeuticsNot yet recruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Acute Myeloid Leukemia Refractory | Higher Risk Myelodysplastic SyndromesUnited States
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Encoded TherapeuticsRecruiting
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Dianthus TherapeuticsRecruitingMyasthenia Gravis, GeneralizedUnited States
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom