- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials Sponsored by Rocket Pharmaceuticals Inc.
Total 5143 results
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Alkeus Pharmaceuticals, Inc.Active, not recruitingGeographic Atrophy | Age Related Macular Degeneration | AMD | Atrophy, GeographicUnited States
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Mirum Pharmaceuticals, Inc.Active, not recruitingCholestatic Liver DiseaseUnited States, France, United Kingdom, Canada, Belgium, Poland, Australia, Spain
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Arog Pharmaceuticals, Inc.CompletedPhase II Study of Crenolanib in Subjects With Relapsed/Refractory AML With FLT3 Activating MutationsRelapsed or Refractory Acute Myeloid Leukemia With FLT3 Activating MutationsUnited States
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Amphastar Pharmaceuticals, Inc.Completed
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Pacira Pharmaceuticals, IncCompleted
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Alkeus Pharmaceuticals, Inc.Enrolling by invitationStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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Cyclacel Pharmaceuticals, Inc.Completed
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Biohaven Pharmaceuticals, Inc.Active, not recruitingSpinocerebellar Ataxia Type 3 | Spinocerebellar Ataxias | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Spinocerebellar Ataxia Type 6 | Spinocerebellar Ataxia Type 10 | Spinocerebellar Ataxia Type 7 | Spinocerebellar Ataxia Type 8United States, China
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Pacira Pharmaceuticals, IncCompletedOsteoarthritis of the Hip | Osteoarthritis of the ShoulderUnited States
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Pacira Pharmaceuticals, IncTerminatedOsteoarthritis, HipUnited States
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Pacira Pharmaceuticals, IncCompletedOsteoarthritis, KneeUnited Kingdom, Spain, Canada, Austria
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Pacira Pharmaceuticals, IncCompletedOsteoarthritis of the KneeUnited States
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Pacira Pharmaceuticals, IncCompletedOsteoarthritis of the KneeUnited States
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Pacira Pharmaceuticals, IncCompletedBilateral Knee OsteoarthritisUnited States
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Pacira Pharmaceuticals, IncCompletedOsteoarthritis of the KneeUnited States
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Pacira Pharmaceuticals, IncCompleted
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Pacira Pharmaceuticals, IncCompletedOsteoarthritis, HipUnited States
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Ionis Pharmaceuticals, Inc.Active, not recruitingTransthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)United States, Australia, Spain, Canada, Germany, Japan, Italy, Israel, Argentina, France, Portugal, Austria, Brazil, Greece, United Kingdom, Czechia, Sweden, Belgium, Denmark, Poland, Puerto Rico
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Tonix Pharmaceuticals, Inc.Completed
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Alexion Pharmaceuticals, Inc.Completed
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Milestone Pharmaceuticals Inc.Enrolling by invitationParoxysmal Supraventricular TachycardiaUnited States, Canada
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ARS Pharmaceuticals, Inc.Active, not recruiting
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Rhythm Pharmaceuticals, Inc.Enrolling by invitationHypothalamic ObesityUnited States, Canada, United Kingdom, Germany, Netherlands
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, France, Netherlands, Spain, United Kingdom, Belgium, Bulgaria, Canada, Denmark, Germany, Israel, Italy, Poland, Turkey
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Crinetics Pharmaceuticals Inc.Active, not recruitingAcromegalyUnited States, Hungary, Brazil, Greece, Serbia, United Kingdom
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Ionis Pharmaceuticals, Inc.Active, not recruitingRefractory Multiple Myeloma | Relapsed Multiple MyelomaUnited States
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Alexion Pharmaceuticals, Inc.Completed
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Alexion Pharmaceuticals, Inc.CompletedHealthy ParticipantsNew Zealand
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)Italy, United States, Argentina, France, Singapore, United Kingdom, Austria, Brazil, Mexico, Lebanon, Germany, Turkey, Poland, Belgium, Canada, Colombia, Hungary
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NeuroBo Pharmaceuticals Inc.CompletedHealthyUnited States
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NeuroBo Pharmaceuticals Inc.CompletedCOVID-19United States
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Alexion Pharmaceuticals, Inc.Active, not recruitingAL AmyloidosisUnited States, Germany, Spain, United Kingdom, France, Korea, Republic of, Poland, Netherlands, Japan, Belgium, Greece, Australia, Austria, Brazil, Canada, China, Czechia, Israel, Italy, Russian Federation
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC DeficiencyNetherlands, United States, Germany, Canada, Puerto Rico, United Kingdom
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Catalyst Pharmaceuticals, Inc.TerminatedSpinal Muscular Atrophy Type 3Italy
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Arog Pharmaceuticals, Inc.CompletedAcute Myeloid Leukemia With FLT3 Activating Mutations That Has Relapsed or Been Refractory After One or More Prior TherapiesUnited States
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Biohaven Pharmaceuticals, Inc.Enrolling by invitationObsessive Compulsive DisorderCanada, United States, Spain, United Kingdom, Italy, Netherlands
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Regor Pharmaceuticals Inc.TerminatedType 2 Diabetes MellitusUnited States
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Tarsus Pharmaceuticals, Inc.CompletedMeibomian Gland Dysfunction | Blepharitis | Demodex InfestationUnited States
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Cardurion Pharmaceuticals, Inc.TerminatedHeart Diseases | Cardiovascular Diseases | Heart Failure | Heart Failure With Reduced Ejection Fraction | Heart Failure With Preserved Ejection FractionUnited States, Israel, United Kingdom, Canada
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Alexion Pharmaceuticals, Inc.CompletedWilson DiseaseUnited Kingdom
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Astex Pharmaceuticals, Inc.Active, not recruiting
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Agios Pharmaceuticals, Inc.CompletedPyruvate Kinase DeficiencyUnited States, Italy, Netherlands
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Mirum Pharmaceuticals, Inc.Active, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)United States, Argentina, France, Singapore, United Kingdom, Belgium, Turkey, Austria, Brazil, Canada, Colombia, Germany, Italy, Lebanon, Mexico, Poland
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Mirum Pharmaceuticals, Inc.CompletedInborn Errors of Bile Acid SynthesisUnited States
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Biohaven Pharmaceuticals, Inc.CompletedMultiple System AtrophyUnited States, Germany, Austria, France, Italy, United Kingdom
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Crinetics Pharmaceuticals Inc.CompletedHealthy VolunteersUnited States
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Lipomedix Pharmaceuticals Inc.TerminatedCancer | Gastro-Intestinal Intraepithelial NeoplasiaIsrael
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Catalyst Pharmaceuticals, Inc.No longer availableLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Nystagmus, AcquiredUnited States
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Agios Pharmaceuticals, Inc.TerminatedAnemia | Anemia, Hemolytic | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency AnemiaUnited States, United Kingdom, Italy, Spain, Netherlands