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Search clinical trials for: AAV2 Vectors
Total 86 results
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MeiraGTx, LLCRecruitingGrade 2 and 3 Late Xerostomia Caused by Radiotherapy for Cancers of the Upper Aerodigestive Tract, Excluding the Parotid GlandsUnited States, Canada
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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Neurocrine BiosciencesVoyager TherapeuticsCompletedBrain Diseases | Central Nervous System Diseases | Nervous System Diseases | Parkinson's Disease | Parkinsonian Disorders | Movement Disorders | Neurodegenerative Diseases | Idiopathic Parkinson's Disease | Basal Ganglia DiseaseUnited States
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Neurocrine BiosciencesOregon Health and Science University; University of California, San Francisco; Veristat, Inc... and other collaboratorsCompletedParkinson's DiseaseUnited States
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ViGeneron GmbHRecruiting
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eyeDNA TherapeuticsRecruitingRetinitis PigmentosaFrance
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Spark TherapeuticsActive, not recruitingConfirmed Biallelic RPE65 Mutation-associated Retinal DystrophyUnited States
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Spark TherapeuticsActive, not recruitingLeber Congenital AmaurosisUnited States
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Spark TherapeuticsCompleted
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Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
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Genzyme, a Sanofi CompanyCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Gene Therapy | Age-Related Maculopathies | Age-Related Maculopathy | Retinal Neovascularization | Maculopathies, Age-Related | Maculopathy, Age-Related | Therapy, GeneUnited States
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BiogenCompletedChoroideremiaUnited States, Finland, France, Denmark, Netherlands, Germany, United Kingdom, Canada
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MeiraGTx UK II LtdSyne Qua Non Limited; Bionical EmasCompletedGene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)X-Linked Retinitis PigmentosaUnited Kingdom, United States
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Sangamo TherapeuticsCeregeneCompletedParkinson's DiseaseUnited States
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Spark TherapeuticsActive, not recruitingInherited Retinal Dystrophy Due to RPE65 Mutations
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National Institute of Neurological Disorders and...Completed
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BiogenCompletedChoroideremiaUnited States, Germany, France
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NightstaRx Ltd, a Biogen CompanyEnrolling by invitationChoroideremia | X-Linked Retinitis PigmentosaUnited States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
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Brain Neurotherapy Bio, Inc.California Institute for Regenerative Medicine (CIRM); Asklepios Biopharmaceutical...Active, not recruiting
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Asklepios Biopharmaceutical, Inc.BayerNot yet recruiting
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University College, LondonMedical Research CouncilRecruiting
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Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
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Sangamo TherapeuticsCeregeneCompletedIdiopathic Parkinson's DiseaseUnited States
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Brain Neurotherapy Bio, Inc.Recruiting
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Fondazione TelethonActive, not recruitingMucopolysaccharidosis Type VIItaly, Turkey
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic Amino Acid Decarboxylase DeficiencyTaiwan
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National Taiwan University HospitalPTC TherapeuticsCompletedAromatic L-amino Acid Decarboxylase (AADC) DeficiencyTaiwan
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Asklepios Biopharmaceutical, Inc.Active, not recruiting
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Sangamo TherapeuticsCompletedIdiopathic Parkinson's DiseaseUnited States
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Shanghai General Hospital, Shanghai Jiao Tong University...Not yet recruitingTo Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
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Mark TuszynskiOhio State UniversityRecruitingMild Cognitive Impairment | Alzheimer's DiseaseUnited States
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PfizerActive, not recruitingHemophilia ASpain, Taiwan, Australia, United States, Japan, France, Turkey, Germany, Korea, Republic of, United Kingdom, Saudi Arabia, Canada, Greece, Sweden, Brazil, Italy
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Spark TherapeuticsChildren's Hospital of Philadelphia; Royal Prince Alfred Hospital, Sydney,... and other collaboratorsCompleted
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Krzysztof BankiewiczNational Institute of Neurological Disorders and Stroke (NINDS); University...Recruiting
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PfizerActive, not recruiting
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Sangamo TherapeuticsActive, not recruitingFabry DiseaseUnited States, United Kingdom, Taiwan, Australia, Germany, Italy, Canada
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Neurocrine BiosciencesVoyager TherapeuticsCompletedParkinson's DiseaseUnited States
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Neurocrine BiosciencesVoyager TherapeuticsActive, not recruitingParkinson's DiseaseUnited States
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, Germany, Italy, France
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GenSight BiologicsNo longer availableLeber Hereditary Optic Neuropathy (Optic, Atrophy, Hereditary, Leber)
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
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GenSight BiologicsCompletedOptic, Atrophy, Hereditary, LeberUnited Kingdom, United States, France, Germany, Italy
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GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
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GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
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Alimentiv Inc.TakedaNot yet recruitingCrohn Disease | Moderately to Severely Active Crohn's Disease | Disease Crohn
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University of Notre DameInfectious Diseases Research Collaboration, Uganda; SC Johnson, A Family Company and other collaboratorsNot yet recruiting
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Virion TherapeuticsRecruitingChronic Hepatitis BHong Kong, New Zealand
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University of Notre DameUniversity of Washington; SC Johnson, A Family Company; fhiClinical; Ministry of... and other collaboratorsRecruitingArbovirus InfectionsSri Lanka
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University of ChicagoRecruitingHead and Neck Cancer | HPV Positive Oropharyngeal Squamous Cell Carcinoma | HPV | Human Papilloma VirusUnited States