- ICH GCP
- US Clinical Trials Registry
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Search clinical trials for: AAV9
Total 27 results
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Benjamin GreenbergActive, not recruiting
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uniQure France SASRecruitingMesial Temporal Lobe EpilepsyUnited States
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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Prevail TherapeuticsEli Lilly and CompanyRecruitingParkinson DiseaseUnited States, Israel
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Prevail TherapeuticsEli Lilly and CompanyRecruitingFrontotemporal DementiaUnited States, Australia, Belgium, Spain, United Kingdom, France
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Novartis Gene TherapiesTerminatedSpinal Muscular AtrophyUnited States
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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AviadoBio LtdRecruitingFrontotemporal Dementia | FTD | FTD-GRN | Dementia, FrontotemporalNetherlands, Spain, Poland
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Prevail TherapeuticsEli Lilly and CompanyRecruitingGaucher Disease | Gaucher Disease, Type 1United States, Spain
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Excision BioTherapeuticsRecruiting
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Aspa TherapeuticsRecruiting
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Prevail TherapeuticsEli Lilly and CompanyActive, not recruitingGaucher Disease, Type 2United States, United Kingdom
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Shanghai Jiao Tong University School of MedicineShanghai Vitalgen BioPharma Co., Ltd.RecruitingAromatic L-amino Acid Decarboxylase (AADC) DeficiencyChina
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Grace Science, LLCRecruitingNGLY1 DeficiencyUnited States
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PfizerRecruitingHousehold ContactsUnited States
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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Excision BioTherapeuticsEnrolling by invitationHIV-1-infectionUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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Encoded TherapeuticsRecruiting
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Encoded TherapeuticsRecruiting
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National Human Genome Research Institute (NHGRI)Sio Gene TherapiesRecruitingGangliosidosis | Lysosomal Diseases | GM1United States
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, United Kingdom, France, Italy