- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Argininosuccinate Synthetase Deficiency
Total 9681 results
-
Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RecruitingHypoxic-Ischemic Encephalopathy | Urea Cycle Disorder | Organic Acidemia | Fatty Acid Oxidation Disorder | Maple Syrup Urine Disease | Glutaric Acidemia IUnited States
-
Cytonet GmbH & Co. KGCompletedOrnithine Transcarbamylase Deficiency | Urea Cycle Disorders | Citrullinemia | Carbamoylphosphate Synthetase I DeficiencyGermany
-
Baylor College of MedicineCompletedCitrullinemiaUnited States
-
National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
-
West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
-
Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
-
Baylor College of MedicineChildren's National Research InstituteRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Carbamyl Phosphate Synthetase Deficiency | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS Deficiency | NAGS DeficiencyUnited States
-
Polaris GroupRecruitingGlioblastoma Multiforme (GBM)Taiwan
-
Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
-
RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
-
Baylor College of MedicineRare Diseases Clinical Research Network; Neogenis LaboratoriesCompletedUrea Cycle Disorders, Inborn | Urea Cycle Disorder | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
-
Polaris GroupTerminatedHepatocellular Carcinoma | Gastric Cancer | Colorectal Cancer | Advanced Gastrointestinal (GI) MalignanciesUnited States, Taiwan, Korea, Republic of, United Kingdom, China, Italy
-
Kaleido BiosciencesTerminatedUrea Cycle DisorderBelgium, United States, Spain, United Kingdom, Germany, Switzerland, Turkey
-
Horizon Therapeutics, LLCTerminatedUrea Cycle DisorderUnited States
-
Polaris GroupCompleted
-
Polaris GroupCompletedAdvanced Pancreatic CancerUnited States
-
Polaris GroupTerminatedGlioma | Hepatocellular Carcinoma | Uveal Melanoma | Sarcomatoid Carcinoma | Pleural Mesothelioma Malignant Advanced | Peritoneal Mesothelioma Malignant Advanced | Non-squamous Non-small Cell Lung CarcinomaUnited States, United Kingdom
-
Baylor College of MedicineCompletedUrea Cycle Disorders | Argininosuccinic Aciduria | Argininosuccinate Lyase DeficiencyUnited States
-
Polaris GroupCompletedNon-Hodgkin's LymphomaTaiwan
-
The First Hospital of Jilin UniversityNational Natural Science Foundation of ChinaUnknownGenetic Diseases, Inborn | Asparagine Synthetase DeficiencyChina
-
University Hospital, Strasbourg, FranceUnknownThe Glutathione Synthetase DeficiencyFrance
-
Polaris GroupCompletedHepatocellular CarcinomaUnited States
-
Polaris GroupCompletedCutaneous Melanoma, Uveal Melanoma, Ovarian Carcinoma or Other Advanced Solid TumorsTaiwan, United States
-
Uta Lichter-KoneckiMedical College of Wisconsin; Children's National Research InstituteCompletedUrea Cycle Disorders | Organic AcidemiasUnited States
-
Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...WithdrawnUrea Cycle Disorders, Inborn | Inborn Errors of Metabolism | Propionic Acidemia | Methylmalonic Acidemia | Carbamyl Phosphate Synthetase Deficiency
-
Polaris GroupCompletedArgininosuccinate Synthetase DeficientUnited States
-
Policlinico HospitalRecruitingTransplantation | Ascorbic Acid DeficiencyItaly
-
Vanderbilt University Medical CenterAminu Kano Teaching HospitalNot yet recruitingMalnutrition | Sickle Cell Disease
-
United States Army Research Institute of Environmental...RecruitingEnergy Supply; DeficiencyUnited States
-
First People's Hospital of HangzhouRecruitingColorectal Cancer | Cancer-Related FatigueChina
-
MetroHealth Medical CenterKent State UniversityNot yet recruiting
-
Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
-
Mayo ClinicRecruiting
-
Changchun GeneScience Pharmaceutical Co., Ltd.Not yet recruitingPediatric Growth Hormone Deficiency (PGHD)China
-
Shanghai Hutchison Pharmaceuticals LimitedNot yet recruitingCervical Spondylotic Myelopathy
-
Privatpraxis für Knie- und SchulterchirurgieRecruiting
-
L-Nutra IncUniversity of Tennessee Medical CenterRecruitingChemotherapy Effect | Fasting, Intermittent | Cancer, Ovarian | Calorie DeficiencyUnited States
-
Liaquat University of Medical & Health SciencesNot yet recruitingVitamin B 12 DeficiencyPakistan
-
University of Missouri-ColumbiaGilead SciencesRecruitingHIV Infections | ART | Noncompliance, PatientUnited States
-
McGill University Health Centre/Research Institute...Not yet recruiting
-
Cairo UniversityNot yet recruitingDental Caries | Vitamin Deficiency
-
Apollo Therapeutics LtdNot yet recruitingMyelodysplastic Syndrome With Excess Blasts | Acute Myeloid Leukemia, in Relapse | Acute Myeloid Leukemia Refractory | Myelodysplastic Syndrome Acute Myeloid Leukemia
-
Milton S. Hershey Medical CenterNot yet recruitingCardiovascular Diseases | Postmenopausal Symptoms
-
University of StellenboschUniversity College London Hospitals; University of Copenhagen; Imperial College... and other collaboratorsNot yet recruiting
-
Linnaeus UniversityWorld Anti-Doping Agency; Swedish Research Council for Sport Science; Swedish...RecruitingEating Disorders | RED SSweden
-
University of California, Los AngelesUniversity of North Carolina, Chapel Hill; University of California, Irvine; Florida... and other collaboratorsRecruitingHIV InfectionsUnited States
-
ViiV HealthcareNot yet recruiting
-
bioLytical LaboratoriesNot yet recruitingHuman Immunodeficiency Virus I Infection | Human Immunodeficiency Virus II Infection
-
The Cooper Health SystemWon Sook Chung FoundationNot yet recruitingVitamin D Deficiency
-
Arrowhead Regional Medical CenterRecruitingIron Deficiency Anemia of PregnancyUnited States