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Search clinical trials for: BioMarin
Total 179 results
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BioMarin PharmaceuticalNot yet recruitingIdiopathic Short Stature
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BioMarin PharmaceuticalRecruitingIdiopathic Short StatureUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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BioMarin PharmaceuticalRecruiting
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BioMarin PharmaceuticalRecruitingHypochondroplasiaUnited States, Canada, France, Australia, Japan, Argentina, Brazil, Germany, Italy, Spain
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BioMarin PharmaceuticalPicnicHealthRecruitingAchondroplasiaUnited States
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BioMarin PharmaceuticalRecruitingNonalcoholic Fatty Liver Disease | Kidney Stone | HyperoxaluriaUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States, Germany, Italy
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University of GlasgowAker BioMarineRecruiting
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BioMarin PharmaceuticalSyneos HealthRecruitingPhenylketonuria, MaternalGermany, United States, Italy
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BioMarin PharmaceuticalRecruiting
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BioMarin PharmaceuticalRecruitingHereditary Angioedema | HAEUnited States, Spain, Australia
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Louis MessinaBioMarin PharmaceuticalRecruitingPeripheral Vascular Diseases | Peripheral Artery Disease | Claudication, IntermittentUnited States
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BioMarin PharmaceuticalRecruitingHemophilia A With Inhibitor | Hemophilia A With Anti Factor VIIIUnited States, United Kingdom, Taiwan, Israel, Korea, Republic of, South Africa, Brazil, Italy, Germany
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Emory UniversityBioMarin PharmaceuticalRecruitingPhenylketonuriasUnited States
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GOIZETBioMarin PharmaceuticalRecruiting
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BioMarin PharmaceuticalEnrolling by invitationHemophilia AUnited Kingdom, United States
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BioMarin PharmaceuticalActive, not recruitingHemophilia A | Gene Therapy | Blood Disorder | Clotting DisordersTaiwan, Korea, Republic of, United Kingdom, South Africa
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BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalActive, not recruitingHemophilia AUnited States, Australia, Taiwan, Brazil
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HaemnetBioMarin PharmaceuticalCompleted
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Johns Hopkins UniversityUniversity of Wisconsin, Madison; University of Texas; BioMarin Pharmaceutical; Alfred I. duPont Hospital for Children and other collaboratorsEnrolling by invitationAchondroplasia
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCTerminatedMucopolysaccharidosis I | Hurler's Syndrome | Hurler-Scheie Syndrome | ScheieItaly
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BioMarin PharmaceuticalActive, not recruitingLate-Infantile Neuronal Ceroid Lipofuscinosis Type 2United States
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BioMarin PharmaceuticalActive, not recruitingPhenylketonuria (PKU)United States, Germany
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BioMarin PharmaceuticalActive, not recruitingHemophilia AUnited States, Taiwan, United Kingdom, Australia, Israel, Belgium, Brazil, France, Germany, Italy, Korea, Republic of, South Africa, Spain
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BioMarin PharmaceuticalActive, not recruiting
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Germany, Spain, United Kingdom, Japan, Turkey
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, France, United Kingdom
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaUnited States, Australia, Japan, United Kingdom
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BioMarin PharmaceuticalActive, not recruitingAchondroplasiaAustralia, United Kingdom
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Boston Children's HospitalBioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
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Marinex International Sp. z o.o.Active, not recruitingNutrition, HealthyPoland
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BioMarin PharmaceuticalTerminatedAchondroplasiaUnited States
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BioMarin PharmaceuticalCompleted
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Tulane University School of MedicineBioMarin PharmaceuticalCompletedPhenylketonuria | Behavior and Behavior Mechanisms | PAH Gene ExpressionUnited States
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University of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitationPhenylketonuriasUnited States
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University of UtahBioMarin PharmaceuticalCompletedGTP Cyclohydrolase DeficiencyUnited States
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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American Thrombosis and Hemostasis NetworkBioMarin PharmaceuticalCompletedLiver Transplantation | Hemophilia A and BUnited States
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BioMarin PharmaceuticalCompletedPhenylketonuriaItaly, Spain, United Kingdom, Germany
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BioMarin PharmaceuticalCompleted
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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Aker Biomarine Antarctic ASBioTeSys GmbHCompleted
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Melinda TelliPfizer; BioMarin PharmaceuticalCompletedAdvanced Breast Cancer | HER2/Neu Negative | Triple-Negative Breast CancerUnited States
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Jessica ScherrBioMarin PharmaceuticalEnrolling by invitationBatten Disease | Neuronal Ceroid-Lipofuscinoses | CLN2United States
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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BioMarin PharmaceuticalCompletedAchondroplasiaUnited States, Australia, United Kingdom, Japan