- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Bone marrow failure syndromes
Total 55769 results
-
Masonic Cancer Center, University of MinnesotaNot yet recruitingAcquired Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria | Severe Aplastic Anemia | Acquired Amegakaryocytic Thrombocytopenia
-
Sidney Kimmel Comprehensive Cancer Center at Johns...Janssen Research & Development, LLCNot yet recruitingLymphoma | Multiple Myeloma | Hodgkin Lymphoma | Myelofibrosis | Non Hodgkin Lymphoma | Chronic Myeloid Leukemia | Hematologic Malignancy | Aplastic Anemia | Myelodysplastic Syndromes (MDS) | Acute Myeloid Leukemia (AML) | Bone Marrow Transplant Rejection | Acute Lymphoblastic Leukemia (ALL), Adult
-
National Cancer Institute (NCI)Not yet recruiting
-
Peking University People's HospitalNot yet recruitingMyelodysplastic Syndromes | Acute Leukemia | Severe Aplastic Anemia
-
Hospital Universitari Vall d'Hebron Research InstituteErasme University Hospital; Cyprus Institute of Neurology and Genetics; EuroBloodNet...RecruitingIron Metabolism Disorders | Sickle Cell Disease | Thalassemia | Hemolytic; Anemia, Hereditary, Due to Enzyme Disorder | Anemia Due to Membrane Defect | CDA | Sideroblastic Anemia | Constitutional Aplastic Anemia | Hereditary AnemiaSpain
-
National Cancer Institute (NCI)RecruitingInherited Bone Marrow Failure Syndrome | Familial Platelet Disorder With Predisposition to Myeloid MalignanciesUnited States
-
UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
-
Boston Children's HospitalChildren's Hospital Medical Center, CincinnatiRecruitingShwachman-Diamond Syndrome | Shwachman-Diamond Syndrome-LikeUnited States
-
University of Alabama at BirminghamNot yet recruitingMyelodysplastic Syndromes | Primary Myelofibrosis | AML | Lymphoid Malignancies | CML | ALLUnited States
-
Masonic Cancer Center, University of MinnesotaNational Institutes of Health (NIH)RecruitingFanconi Anemia | Oral Cavity Carcinoma | Alcohol-Related CarcinomaUnited States
-
Assistance Publique - Hôpitaux de ParisNot yet recruiting
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingSteroid-refractory Diamond-Blackfan Anemia (DBA)United States
-
Shandong Qilu Stem Cells Engineering Co., Ltd.Second Affiliated Hospital of Zhengzhou University; The Second Affiliated Hospital... and other collaboratorsRecruitingBone Marrow Failure DisordersChina
-
Franziska WachterHarvard Clinical and Translational Science Center (Harvard Catalyst)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | MDS | Aml | Myeloid Neoplasm | Myeloid Malignancies | Inherited Bone Marrow Failure SyndromeUnited States
-
National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
-
Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
-
Children's Hospital Medical Center, CincinnatiRecruiting
-
Thomas Jefferson UniversityAbbVieRecruitingMyelodysplastic Syndrome | Recurrent Myelodysplastic Syndrome | Refractory Myelodysplastic SyndromeUnited States
-
Sohag UniversityAssiut University; Kyoto UniversityRecruitingInherited BMF SyndromeEgypt
-
Centre Leon BerardRecruitingMyelodysplastic Syndromes | Severe Combined Immunodeficiency | Acute Leukemia | Haematological Malignancy | Hemoglobinopathy in Children | Bone Marrow AplasiaFrance
-
Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
-
Peter MacCallum Cancer Centre, AustraliaNational Health and Medical Research Council, Australia; University of MelbourneRecruitingHematologic Diseases | Inherited Platelet Disorder | Inherited BMF SyndromeAustralia
-
Children's Hospital of PhiladelphiaNational Cancer Institute (NCI); University of Pennsylvania; City of Hope Medical... and other collaboratorsRecruitingMyelodysplastic Syndromes | Aplastic Anemia | Lymphoblastic Leukemia | Cancer SurvivorsUnited States
-
Thomas Jefferson UniversityRecruitingHematopoietic and Lymphoid Cell Neoplasm | Acute Myeloid Leukemia | Myelodysplastic Syndromes | Myeloid Leukemia | Polycythemia Vera | Essential Thrombocythemia | Hodgkin Lymphoma | Myelofibrosis | Chronic Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Non-Hodgkin Lymphoma and other conditionsUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingSevere Aplastic Anemia | Telomere Biology Disorders | Inherited Bone Marrow Failure SyndromesUnited States
-
Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Amegakaryocytic Thrombocytopenia | Paroxysmal Nocturnal Hemoglobinuria | Shwachman-Diamond Syndrome | Bone Marrow Failure Syndrome | Congenital Pure Red Cell Aplasia | Hereditary Sideroblastic Anemia | Hematologic Neoplasm With Germline GATA2 Mutation | Hematologic Neoplasm With Germline... and other conditionsUnited States
-
Porteus, Matthew, MDRecruiting
-
Assistance Publique - Hôpitaux de ParisNot yet recruiting
-
Institute of Hematology & Blood Diseases HospitalRecruitingLymphoma | Acute Myeloid Leukemia | Leukemia | Hemophilia A | Hemophilia B | Hemophilia | Multiple Myeloma | Myelodysplastic Syndrome | Bone Marrow Transplantation | MDS | Aplastic Anemia | Bleeding Disorder | Myeloma, Multiple | Myelomas, Multiple | Leukemias, Acute Myeloid | Myeloid Leukemias, Acute | Hemophilia As | Hemophilia... and other conditionsChina
-
The University of QueenslandRecruitingPulmonary Fibrosis | Dyskeratosis Congenita | Telomere Shortening | Telomere DiseaseAustralia
-
Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary AnemiasUnited States
-
Foresee Pharmaceuticals Co., Ltd.Recruiting
-
Johns Hopkins All Children's HospitalRecruitingSevere Aplastic Anemia | Bone Marrow Failure Syndrome | Hemoglobinopathy (Disorder)United States
-
Washington University School of MedicineShwachman Diamond Syndrome Foundation; Barnes-Jewish HospitalRecruiting
-
Sidney Kimmel Comprehensive Cancer Center at Johns...RecruitingPrimary Immune Deficiency Disorder | Bone Marrow Failure | Immune Deficiency DiseaseUnited States
-
Mitchell CairoRecruitingHodgkin Lymphoma | Sickle Cell Disease | Acute Leukemia | Beta-Thalassemia | Non-hodgkin Lymphoma | Severe Aplastic Anemia | Diamond Blackfan Anemia | Amegakaryocytic Thrombocytopenia | KostmannUnited States
-
National Taiwan University HospitalRecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Aplastic Anemia | Myeloproliferative NeoplasmTaiwan
-
Academic and Community Cancer Research UnitedNational Cancer Institute (NCI)RecruitingBile Duct Adenocarcinoma | Fanconi Anemia Complementation Group Gene Mutation | Metastatic Bile Duct Carcinoma | PTEN Gene DeletionUnited States
-
Case Comprehensive Cancer CenterRecruitingMyelodysplastic Syndrome (MDS)United States
-
University College, LondonMedical Research CouncilRecruitingLymphoma | Myelodysplastic Syndromes | Leukemia | Myeloma | Graft Vs Host Disease | Severe Aplastic Anemia | Primary Immune DeficiencyUnited Kingdom
-
Paul SzabolcsRecruitingSickle Cell Anemia | Diamond-blackfan Anemia | Beta-thalassemia MajorUnited States
-
M.D. Anderson Cancer CenterRecruitingFollicular Lymphoma | Acute Myeloid Leukemia | Hodgkin Lymphoma | Acute Lymphoblastic Leukemia | Mantle Cell Lymphoma | Chronic Lymphocytic Leukemia | Non-Hodgkin Lymphoma | Myelodysplastic Syndrome | Plasma Cell Myeloma | Aplastic Anemia | Myeloproliferative Neoplasm | Bone Marrow Failure | Chronic Myelogenous...United States
-
Masonic Cancer Center, University of MinnesotaRecruitingMyelodysplastic Syndromes | Fanconi Anemia | Severe Aplastic AnemiaUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic Anemia (SAA) | Hypo-Plastic Myelodysplastic Syndrome (MDS)United States
-
Masonic Cancer Center, University of MinnesotaRecruitingLymphoma | Follicular Lymphoma | Acute Myeloid Leukemia | Multiple Myeloma | Myelofibrosis | Juvenile Myelomonocytic Leukemia | Burkitt Lymphoma | Acute Lymphoblastic Leukemia | Lymphoblastic Lymphoma | Chronic Lymphocytic Leukemia | Lymphoplasmacytic Lymphoma | Acute Leukemia | Mantle-Cell Lymphoma | Chronic Myelogenous... and other conditionsUnited States
-
National Cancer Institute (NCI)Children's Oncology GroupRecruitingMalignant Solid Neoplasm | Advanced Malignant Solid Neoplasm | Refractory Malignant Solid Neoplasm | Recurrent Ependymoma | Recurrent Hepatoblastoma | Recurrent Langerhans Cell Histiocytosis | Recurrent Malignant Germ Cell Tumor | Recurrent Malignant Glioma | Recurrent Malignant Solid Neoplasm | Recurrent... and other conditionsUnited States, Puerto Rico, Australia
-
National Heart, Lung, and Blood Institute (NHLBI)Recruiting
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingMyelodysplastic Syndrome (MDS) | Severe Aplastic Anemia | Hypo-Plastic MDSUnited States
-
National Cancer Institute (NCI)RecruitingMalignant Glioma | Rhabdoid Tumor | Advanced Malignant Solid Neoplasm | Refractory Malignant Solid Neoplasm | Recurrent Ependymoma | Recurrent Ewing Sarcoma | Recurrent Hepatoblastoma | Recurrent Langerhans Cell Histiocytosis | Recurrent Malignant Germ Cell Tumor | Recurrent Malignant Solid Neoplasm | Recurrent... and other conditionsUnited States, Puerto Rico, Australia, Canada
-
Washington University School of MedicineRecruitingHemoglobinopathies | Bone Marrow Failure Syndromes | Metabolic Disorders | Non-malignant Disorders | Severe Sickle Cell Disease | Immunologic DisordersUnited States