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Search clinical trials for: Carnitine-acylcarnitine Translocase Deficiency
Total 9650 results
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West Kazakhstan Medical UniversityRecruitingOrnithine Transcarbamylase Deficiency | Biotinidase Deficiency | Citrullinemia | Glutaric Acidemia Type II | Argininosuccinic Aciduria | Maple Syrup Urine Disease | Primary Carnitine Deficiency | Homocystinuria | Carnitine Palmitoyltransferase II Deficiency | Arginase Deficiency | Very Long-chain Acyl-CoA... and other conditionsKazakhstan
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Ultragenyx Pharmaceutical IncAvailableGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)
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Ultragenyx Pharmaceutical IncCompletedCarnitine Palmitoyltransferase (CPT I or CPT II) Deficiency | Very Long Chain Acyl-CoA Dehydrogenase (VLCAD) Deficiency | Long-chain 3-hydroxy-acyl-CoA Dehydrogenase (LCHAD) Deficiency | Trifunctional Protein (TFP) Deficiency | Carnitine-acylcarnitine Translocase (CACT) DeficiencyUnited States, United Kingdom
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Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)Turkey, United Kingdom, Spain, Saudi Arabia, Poland, Czechia, Germany
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Ultragenyx Pharmaceutical IncRecruitingLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States, Canada
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Children's National Research InstituteNational Center for Advancing Translational Sciences (NCATS)RecruitingHypoxic-Ischemic Encephalopathy | Urea Cycle Disorder | Organic Acidemia | Fatty Acid Oxidation Disorder | Maple Syrup Urine Disease | Glutaric Acidemia IUnited States
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Ultragenyx Pharmaceutical IncTerminatedLong-chain Fatty Acid Oxidation Disorders (LC-FAOD)United States
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Kaleido BiosciencesTerminatedUrea Cycle DisorderBelgium, United States, Spain, United Kingdom, Germany, Switzerland, Turkey
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Policlinico HospitalRecruitingTransplantation | Ascorbic Acid DeficiencyItaly
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Vanderbilt University Medical CenterAminu Kano Teaching HospitalNot yet recruitingMalnutrition | Sickle Cell Disease
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United States Army Research Institute of Environmental...RecruitingEnergy Supply; DeficiencyUnited States
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First People's Hospital of HangzhouRecruitingColorectal Cancer | Cancer-Related FatigueChina
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MetroHealth Medical CenterKent State UniversityNot yet recruiting
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Beam Therapeutics Inc.Not yet recruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom
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Mayo ClinicRecruiting
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Changchun GeneScience Pharmaceutical Co., Ltd.Not yet recruitingPediatric Growth Hormone Deficiency (PGHD)China
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Shanghai Hutchison Pharmaceuticals LimitedNot yet recruitingCervical Spondylotic Myelopathy
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Privatpraxis für Knie- und SchulterchirurgieRecruiting
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L-Nutra IncUniversity of Tennessee Medical CenterRecruitingChemotherapy Effect | Fasting, Intermittent | Cancer, Ovarian | Calorie DeficiencyUnited States
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Liaquat University of Medical & Health SciencesNot yet recruitingVitamin B 12 DeficiencyPakistan
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University of Missouri-ColumbiaGilead SciencesRecruitingHIV Infections | ART | Noncompliance, PatientUnited States
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McGill University Health Centre/Research Institute...Not yet recruiting
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Cairo UniversityNot yet recruitingDental Caries | Vitamin Deficiency
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Apollo Therapeutics LtdNot yet recruitingMyelodysplastic Syndrome With Excess Blasts | Acute Myeloid Leukemia, in Relapse | Acute Myeloid Leukemia Refractory | Myelodysplastic Syndrome Acute Myeloid Leukemia
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Milton S. Hershey Medical CenterNot yet recruitingCardiovascular Diseases | Postmenopausal Symptoms
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University of StellenboschUniversity College London Hospitals; University of Copenhagen; Imperial College... and other collaboratorsNot yet recruiting
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Linnaeus UniversityWorld Anti-Doping Agency; Swedish Research Council for Sport Science; Swedish...RecruitingEating Disorders | RED SSweden
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University of California, Los AngelesUniversity of North Carolina, Chapel Hill; University of California, Irvine; Florida... and other collaboratorsRecruitingHIV InfectionsUnited States
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ViiV HealthcareNot yet recruiting
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bioLytical LaboratoriesNot yet recruitingHuman Immunodeficiency Virus I Infection | Human Immunodeficiency Virus II Infection
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The Cooper Health SystemWon Sook Chung FoundationNot yet recruitingVitamin D Deficiency
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Arrowhead Regional Medical CenterRecruitingIron Deficiency Anemia of PregnancyUnited States
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Sun Yat-Sen Memorial Hospital of Sun Yat-Sen UniversityRecruiting
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Ibrahim Halil SahinGlaxoSmithKlineNot yet recruitingMMR-D/MSI-H Colorectal CancersUnited States
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McGill UniversityGlobal Affairs Canada; World Vision CanadaNot yet recruitingStunting | Diet; Deficiency | Empowerment | Acceptability of Health Care | Gender EqualityBangladesh, Kenya, Tanzania
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OctapharmaNot yet recruiting
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7 Hills Pharma, LLCNot yet recruitingMelanoma | Kidney Cancer | Renal Cell Carcinoma | Hepatocellular Carcinoma | Colorectal Cancer | NSCLC | Non Small Cell Lung Cancer | Skin Cancer | Metastasis | Advanced Solid Tumor | Advanced Cancer | Renal Cell Cancer | Hepatocellular Cancer | Mismatch Repair Deficiency | Pleural Mesothelioma | MSI-High | Anaplastic Lymphoma... and other conditionsUnited States
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University of California, San FranciscoGilead SciencesRecruiting
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CHU de ReimsRecruitingPrimary Immunodeficiency | Common Variable Immunodeficiency | Igg Subclass Deficiency | Selective IgM DeficiencyFrance
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Galderma R&DRecruitingWeight Loss | Skin Laxity | Photoaging | Photodamaged Skin | Volume Deficiency of the MidfaceUnited States
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Lund UniversityRecruitingFemale | Sport Injury | Female Athlete Triad | Sports Accident | Ice-Skates AccidentSweden
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TakedaNot yet recruitingHereditary Angioedema (HAE)
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Washington University School of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development...Not yet recruiting
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University of Sao Paulo General HospitalNot yet recruitingMenopause | Testosterone Deficiency | Estrogen Deficiency
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Puerto Rico
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Louisiana State University Health Sciences Center...RecruitingAlveolar Ridge DeficiencyUnited States
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Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
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University of CalgaryMitacs; Natural Sciences and Engineering Research Council, CanadaNot yet recruitingIron Deficiencies