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Search clinical trials for: Familial ALS
Total 11834 results
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Verge GenomicsRecruitingAmyotrophic Lateral SclerosisCanada, Netherlands
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Peking University Third HospitalRecruitingSporadic and Familial Amyotrophic Lateral SclerosisChina
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University of British ColumbiaVancouver Coastal Health Research Institute; Genome British ColumbiaRecruitingAcute Coronary Syndrome | Familial Hypercholesterolemia | STEMI | NSTEMI - Non-ST Segment Elevation MI | Familial Hypercholesterolemia - Heterozygous | Familial Hypercholesterolemia Due to Genetic Defect of Apolipoprotein B | Familial Hypercholesterolemia Due to Heterozygous LDL Receptor Mutation and other conditionsCanada
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AL-S PharmaRecruitingAmyotrophic Lateral SclerosisKorea, Republic of, United States, Canada, Germany, Sweden, Belgium
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University of Kansas Medical CenterRecruitingPulmonary Arterial Hypertension | Pulmonary Hypertension | Chronic Thromboembolic Pulmonary Hypertension | Pulmonary Hypertension Due to Left Heart Disease | Pulmonary Hypertension, Primary, 4 | Pulmonary Hypertension, Primary, 2 | Pulmonary Hypertension, Primary, 3 | Pulmonary Hypertension, Primary and other conditionsUnited States
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University of PennsylvaniaUnited States Department of Defense; National Institutes of Health (NIH); National... and other collaboratorsRecruitingFrontotemporal Degeneration(FTD) | Primary Progressive Aphasia(PPA) | Familial Frontotemporal Lobar Degeneration (fFTLD) | Amyotrophic Lateral Sclerosis(ALS) | Lewy Body Disease(LBD) | Progressive Supranuclear Palsy(PSP) | Corticobasal Syndrome(CBS) | Posterior Cortical Atrophy(PCA) | Alzheimer's Disease(AD)United States
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Liquidia Technologies, Inc.PPDRecruitingPulmonary Arterial Hypertension | Pulmonary Hypertension Due to Lung DiseasesUnited States
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Columbia UniversityRecruiting
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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National Human Genome Research Institute (NHGRI)RecruitingArterial Calcification Due to Deficiency of CD73United States
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University of MiamiALS AssociationRecruitingAmyotrophic Lateral SclerosisUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Washington University School of MedicineEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Lou Gehrig Disease | Familial Amyotrophic Lateral Sclerosis | Motor Neuron Disease, FamilialUnited States
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State University of New York - Upstate Medical...TerminatedFamilial Encephalopathy With Neuroserpin Inclusion Bodies | X-linked Mental Retardation | Congenital Vertical Talus | Idiopathic Generalised Epilepsy | Familial DementiaUnited States
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Washington University School of MedicineMassachusetts General HospitalSuspendedAmyotrophic Lateral Sclerosis, Familial | Amyotrophic Lateral Sclerosis, SporadicUnited States
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Danish Rehabilitation Centre for Neuromuscular...CompletedCognitive Impairment | Rehabilitation | Relatives | Health Care ProvidersDenmark
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Northwestern UniversityCompletedAmyotrophic Lateral Sclerosis (ALS) | Lou Gehrig's Disease | Primary Lateral Sclerosis (PLS) | Familial Amyotrophic Lateral Sclerosis | ALS With Frontotemporal Dementia (ALS/FTD) | Motor Neuron Disease (MND) | Sporadic ALS (SALS)United States
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National Cancer Institute (NCI)CompletedFamilial Adenomatous Polyposis | Attenuated Familial Adenomatous PolyposisUnited States, Puerto Rico
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University of Massachusetts, WorcesterEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Muscular Dystrophy | Frontotemporal Dementia | Miyoshi Myopathy | Amyotrophic Lateral Sclerosis, Sporadic | PLS | Lou Gehrigs Disease | Familial Disease | Amyotrophic Lateral Sclerosis With DementiaUnited States
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Washington University School of MedicineSuspendedDiabetes Mellitus | Peripheral Arterial Disease | Critical Limb Ischemia | Lower Limb Amputation KneeUnited States
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Organon and CoTerminatedLipid Metabolism, Inborn Errors | Hypercholesterolemia, Familial
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Organon and CoCompletedHypercholesterolemia | Hypertriglyceridemia | Hyperlipidemia
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Organon and CoCompletedHypercholesterolemia | Hypertriglyceridemia
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Polyneuron Pharmaceuticals AGTerminatedAnti-MAG NeuropathySpain, France, Netherlands, Switzerland, United Kingdom
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Washington University School of MedicineJohns Hopkins University; Massachusetts General Hospital; Columbia University; UMC... and other collaboratorsCompletedC9ORF72 Amyotrophic Lateral Sclerosis (ALS)United States, Netherlands
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Assistance Publique - Hôpitaux de ParisWithdrawnPulmonary Arterial Hypertension With Congenital Cardiac Shunt
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AL-S PharmaUnknownAmyotrophic Lateral SclerosisCanada
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Tammie L. S. Benzinger, MD, PhDCompletedAmyotrophic Lateral Sclerosis (ALS)United States
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Complexa, Inc.Medpace, Inc.; Allegheny Singer Research Institute (also known as Allegheny... and other collaboratorsTerminated
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Complexa, Inc.Philips Healthcare; Medpace, Inc.; Allegheny Singer Research Institute (also... and other collaboratorsTerminatedPAHUnited States, United Kingdom
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Lundquist Institute for Biomedical Innovation at...University of California, Los Angeles; Los Angeles Department of Health ServicesCompletedCritical Illness | CommunicationUnited States
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Edward KasaraskisCompletedFamilial Amyotrophic Lateral SclerosisUnited States
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University of MiamiMassachusetts General HospitalCompletedAmyotrophic Lateral SclerosisUnited States
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Allegheny Singer Research Institute (also known...CompletedPulmonary Arterial HypertensionUnited States
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Weill Medical College of Cornell UniversityMuscular Dystrophy AssociationCompletedFamilial Amyotrophic Lateral SclerosisUnited States, Germany, Italy, Sweden
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MaineHealthRobert Wood Johnson FoundationCompletedDepression | Psychotic Disorders | Schizophrenia | Bipolar DisorderUnited States
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University of UtahNational Cancer Institute (NCI)CompletedAdenomatous Polyposis ColiUnited States
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI)CompletedMyocardial Ischemia | Heart Diseases | Cardiovascular Diseases | Coronary Disease | Coronary Arteriosclerosis
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Instituto Nacional de Ciencias Medicas y Nutricion...Merck Sharp & Dohme LLCWithdrawnCardiovascular Diseases | Hyperlipidemia
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Ionis Pharmaceuticals, Inc.ALS Association; Muscular Dystrophy AssociationCompletedFamilial Amyotrophic Lateral SclerosisUnited States
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Daiichi Sankyo, Inc.TerminatedAtherosclerosis | Heterozygous Familial HypercholesterolemiaUnited States, United Kingdom, Spain, South Africa, Israel, Canada, Netherlands, Norway, Sweden
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Johns Hopkins Bloomberg School of Public HealthBill and Melinda Gates Foundation; Kwame Nkrumah University of Science and...CompletedContraceptionGhana, United States
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Karolinska InstitutetNot yet recruitingParent-Child Relations | Child Behavior Problem | Oppositional Defiant Disorder | Disruptive Behavior | Conduct Problems
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Pamukkale UniversityNot yet recruitingUrinary Bladder, OveractiveTurkey
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Washington University School of MedicineAlzheimer's Association; Eisai Inc.Not yet recruitingDementia | Alzheimer's Disease | Alzheimer's Disease, FamilialUnited States, Australia, United Kingdom
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Universidad Europea de MadridRecruitingMultiple Sclerosis | Pelvic Floor Disorders | Incontinence, UrinarySpain
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Johns Hopkins UniversitySaluda Medical Pty LtdNot yet recruitingChronic Pain | Spasticity as Sequela of Stroke | Upper Motor Neuron LesionUnited States
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Fayoum University HospitalRecruiting
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Riphah International UniversityRecruiting
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University of PennsylvaniaNot yet recruitingParkinson Disease | Alzheimer Disease | ALS | Polyneuropathies | Frontotemporal Dementia | Pheochromocytoma | Thoracic Aortic Aneurysm | Paraganglioma | Genetic Predisposition | Cardiomyopathy Non-ischemic