Search clinical trials for: Genetic Disease
Total 381775 results
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University of RochesterNot yet recruitingAge-Related Macular Degeneration | Retinitis Pigmentosa | Retinal Dystrophies | Alcohol Use Disorder | Stargardt DiseaseUnited States
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Istituto Auxologico ItalianoRecruitingCardiovascular Diseases | Cardiomyopathies | Ischemic Heart Disease | Sudden Cardiac Death Due to Cardiac ArrhythmiaItaly
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Kathelijn FischerRadboud University Medical Center; University Medical Center Groningen; Maastricht... and other collaboratorsRecruitingAdolescent | Child | Hemophilia A With Inhibitor | Adult | Hemophilia A Without Inhibitor | Hemophilia A, SevereNetherlands
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Recruiting
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New York UniversityNot yet recruiting
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Oman Medical Speciality BoardArmed Forces Hospital, OmanNot yet recruitingSickle-Cell Disease With Crisis
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National Taiwan University HospitalRecruiting
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Assistance Publique - Hôpitaux de ParisRecruitingBrain Tumor | Brain Lesion (General)France
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Qilu Hospital of Shandong UniversityRecruitingChild | Williams Syndrome | Neurodevelopmental DelayChina
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Bioray LaboratoriesXiangya Hospital of Central South University; The 923rd Hospital of Joint Logistics...Recruiting
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Noema Pharma AGNot yet recruiting
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Societa Italiana di Dermatologia Medica, Chirurgica...Recruiting
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LEO PharmaNot yet recruiting
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Recruiting
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Maximilian Stahl, MDSyndax PharmaceuticalsNot yet recruitingAcute Myeloid Leukemia | Leukemia | AML | AML, Adult | AML With Gene MutationsUnited States
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Daniel J. WeinerRecruitingCystic FibrosisUnited States
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Niguarda HospitalIstituto di Fisiologia Clinica CNRRecruitingCoronary Artery DiseaseItaly
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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National Heart, Lung, and Blood Institute (NHLBI)Children's National Research InstituteRecruitingSickle Cell Disease | Thalassemia | HemoglobinopathyUnited States
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University of California, Los AngelesRecruitingTuberous SclerosisUnited States
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University of ValenciaAsociación de Fibrosis Quística - Comunidad ValencianaNot yet recruiting
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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University Hospital, ToulouseNot yet recruitingFamilial Adenomatous PolyposisFrance
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Lantu BiopharmaNot yet recruitingBeta-Thalassemia
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M.D. Anderson Cancer CenterNovartis PharmaceuticalsNot yet recruitingAcute Lymphoblastic Leukemia | Philadelphia Chromosome-PositiveUnited States
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argenxRecruitingThyroid Eye DiseaseUnited States
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BioMarin PharmaceuticalRecruitingIdiopathic Short StatureUnited States
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Hangzhou Yirui Pharmaceutical Technology Co., LtdNot yet recruitingAtopic DermatitisUnited States
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argenxRecruitingThyroid Eye DiseaseUnited States
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Forge Biologics, IncNot yet recruitingKrabbe DiseaseUnited States
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BioMarin PharmaceuticalRecruitingPhenylketonuria (PKU)United States
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Rady Pediatric Genomics & Systems Medicine InstituteRecruiting
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Halic UniversityRecruitingCystic Fibrosis | Cystic Fibrosis in ChildrenTurkey
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Peking University Cancer Hospital & InstituteNot yet recruitingGastric Cancer | Esophageal Cancer | Risk Stratification | Precision Screening | Sequential ScreeningChina
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Massachusetts General HospitalJohns Hopkins UniversityNot yet recruitingNeurofibromatosis 1 | Neurofibromas, CutaneousUnited States
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Inozyme PharmaGACI GlobalNot yet recruitingATP-Binding Cassette Subfamily C Member 6 Deficiency | Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
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Vertex Pharmaceuticals IncorporatedRecruiting
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Bioray LaboratoriesFirst Affiliated Hospital of Guangxi Medical UniversityNot yet recruiting
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Children's Hospital Medical Center, CincinnatiMakerere University; Ministry of Health, Uganda; Mulago Hospital, UgandaRecruiting
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University of MichiganRecruitingHealthy | Atopic Dermatitis | Food AllergyUnited States
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Kind Pharmaceuticals LLCNot yet recruiting
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Hôpital Necker-Enfants MaladesNot yet recruiting
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Bangabandhu Sheikh Mujib Medical University, Dhaka...Recruiting
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Region StockholmKarolinska InstitutetRecruiting
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ARTHEx Biotech S.L.Not yet recruitingMyotonic Dystrophy 1
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States
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Shanghai Institute Of Biological ProductsThe First Affiliated Hospital of Henan University of Science and Technology; First Affiliated Hospital Bengbu Medical College and other collaboratorsRecruiting
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metaX Institut fuer Diatetik GmbHGreat Ormond Street Hospital for Children NHS Foundation Trust; Birmingham...Not yet recruitingAlkaptonuria | Homocystine; Metabolic Disorder | Tyrosinemia, Type I | Tyrosinemia, Type II | Tyrosinemia, Type III | MSUD (Maple Syrup Urine Disease)