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Search clinical trials for: Genetic lipids disorders
Total 157230 results
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolemiaSlovenia, Taiwan, Russian Federation, Canada, Netherlands, Brazil, Denmark, Mexico, Spain, Turkey
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCancer | Muscle Weakness | Skin FibroblastsUnited States
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AmgenCompletedHomozygous Familial Hypercholesterolemia HoFHIndia
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University of PennsylvaniaThe LAM FoundationCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisUnited States
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University of Eastern FinlandUniversity of Turku; Kuopio University Hospital; University of Copenhagen; University... and other collaboratorsActive, not recruitingGlucose Metabolism Disorders | Overweight | Atherosclerosis | Lipid Metabolism Disorders | Blood PressureFinland
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Jiangsu HengRui Medicine Co., Ltd.UnknownFamilial Hypercholesterolemia
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The Medicines CompanyCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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University of North Carolina, Chapel HillNational Heart, Lung, and Blood Institute (NHLBI)CompletedSickle Cell Disease | Sickle Cell NephropathyUnited States
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Antonio PersicoUniversity of Bari; Associazione Italiana Sindrome di Phelan-McDermid (AISPHEM)Enrolling by invitationAutism Spectrum Disorder | Phelan-McDermid SyndromeItaly
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Yerevan State Medical UniversityServierUnknownHypercholesterolemia | Essential Hypertension
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National Institute of Neurological Disorders and...Completed
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Rigshospitalet, DenmarkUnknownCarbohydrate Metabolism, Inborn Errors | Metabolism, Inborn Errors | Lipid Metabolism, Inborn Errors | Glycogen Storage Disease Type II | Glycogen Storage Disease Type V | VLCAD Deficiency | Glycogen Storage Disease Type III | Phosphoglycerate Kinase Deficiency | Neutral Lipid Storage Disease | Carnitine... and other conditionsDenmark
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Merck Sharp & Dohme LLCCompletedHyperlipoproteinemia Type II | Hypercholesterolemia, Familial
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Oregon Health and Science UniversityNational Heart, Lung, and Blood Institute (NHLBI)TerminatedSmith-Lemli-Opitz SyndromeUnited States
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University of California, DavisCompletedFragile X Syndrome | Genetic DiseasesUnited States
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNorway, Russian Federation, Sweden, South Africa, Czechia, United States, Canada, France, Netherlands, Spain
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St Mary's University CollegeUnknownDepression | Anxiety | Choline DeficiencyUnited Kingdom
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Montefiore Medical CenterRett Syndrome Research TrustCompleted
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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AmgenCompletedHyperlipidemiaCanada, France, Netherlands, United Kingdom, New Zealand, South Africa, Spain, United States, Australia, Germany, Sweden, Hong Kong, Switzerland, Norway
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); Helen Keller International; DSM... and other collaboratorsCompletedInflammation | Anemia | Iron Deficiency | Infection | Hemoglobin DisorderCambodia
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PfizerTerminatedCardiovascular DiseaseUnited States, Finland, Netherlands, Spain, Belgium, Germany, Czechia, Switzerland, Denmark, Australia, United Kingdom, Korea, Republic of, Hungary, Israel, Poland, Taiwan, Mexico, Turkey, Ireland, Canada, New Zealand, South Africa, Brazi... and more
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Kastle Therapeutics, LLCCompletedHypercholesterolemia | Heterozygous FamilialUnited States, Italy, Poland, Ukraine, United Kingdom, Germany, Hong Kong, Taiwan, Spain, Argentina, Belgium, Israel, Malaysia, South Africa, Turkey, Netherlands, Korea, Republic of, Canada, New Zealand, Russian Federation, Brazil, Austral... and more
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UMC UtrechtErasmus Medical Center; Academisch Medisch Centrum - Universiteit van Amsterdam... and other collaboratorsUnknownHyperlipoproteinemia Type III | Familial Dysbetalipoproteinemia
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London School of Hygiene and Tropical MedicineCompletedHyperhomocysteinemia | Micronutrient DeficienciesGambia
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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Université de SherbrookeFRAXA Research FoundationCompletedFragile X SyndromeCanada
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Oslo University HospitalUniversity of OsloCompletedOverweight and Obesity | Type IIb Hyperlipidaemia | Hypercholesterolemia AggravatedNorway
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Merck Sharp & Dohme LLCCompletedMixed Hyperlipidemia
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PfizerCompletedHyperlipidemiaFinland, Netherlands, United States, Canada, Sweden, Korea, Republic of, Singapore, Czechia, Poland, United Kingdom, Puerto Rico, Norway
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PfizerTerminatedCardiovascular DiseaseFinland, United States, Netherlands, Spain, Korea, Republic of, China, Israel, Belgium, Germany, Australia, Czechia, Taiwan, Denmark, United Kingdom, Hungary, Poland, France, Mexico, Turkey, Canada, New Zealand, Colombia, Switzerland, Irelan... and more
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ShionogiIntegriumCompletedCombined HyperlipidemiaUnited States
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Institut National de la Santé Et de la Recherche...CompletedSpastic Paraplegia, HereditaryFrance
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University of Alabama at BirminghamNational Cancer Institute (NCI); Children's Hospital of Philadelphia; Washington... and other collaboratorsCompletedNeurofibromatosis Type 1United States, Australia
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AstraZenecaCompletedHomozygous Familial Hypercholesterolemia (HoFH)Malaysia, Canada, Taiwan, Belgium, Denmark, Israel
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Ege UniversityTurkish Society of CardiologyCompletedAtherosclerosis | Familial HypercholesterolemiaTurkey
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Instituto Aragones de Ciencias de la SaludUnknownArteriosclerosis | Aortic Stenosis | Familial Hypercholesterolemia | Conventional Transthoracic EchocardiogramSpain
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National Institute of Allergy and Infectious Diseases...TerminatedIFN-Gamma Therapy | CGD Gene Mutation | CGD Response to IFNg | CGD - Chronic Granulomatous Disease | Immunodeficiency DiseaseUnited States
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Imperial College LondonUnknown
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedVascular Disease | Vascular Disease RiskUnited States
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PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
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Duke UniversityDavid Grant U.S. Air Force Medical CenterCompletedHypercholesterolemia | Hydroxy-methylglutaryl-coenzyme A (HMG Co-A) Reductase Inhibitors Adverse ReactionUnited States
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University of ManitobaCompletedHyperlipidemiaUnited States, Canada
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Brigham and Women's HospitalCompleted
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Merck Sharp & Dohme LLCCompletedPrimary Hypercholesterolemia | Mixed Hyperlipidemia
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Central South UniversityCompletedHomozygous Familial HypercholesterolemiaChina
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University of California, Los AngelesCompletedNeurofibromatosis 1United States
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Lipid Metabolism, Inborn Errors | Hypobetalipoproteinemias | Hypolipoproteinemias | Hypolipopro... and other conditionsNetherlands