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Search clinical trials for: Hereditary Angioedema Type I
Total 492001 results
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University of Alabama at BirminghamMemorial Sloan Kettering Cancer CenterActive, not recruitingNeurofibromatosis 2 | Progressive Vestibular Schwannoma (VS)United States
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Dermatology Specialties Limited PartnershipCompletedTuberous Sclerosis | Facial AngiofibromaUnited States, Taiwan, Serbia, Spain, Australia, Czechia, Hungary, New Zealand, Slovakia
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Peking Union Medical College Hospitalthe Second Affiliated Hospital of South China University; The Loudi Central...CompletedArtificial Intelligence | Enteroscope | Intestinal Polyposis, AdenomatousChina
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Memorial Sloan Kettering Cancer CenterEnrolling by invitationSurvivors of Unilateral RetinoblastomaUnited States
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Children's National Research InstituteBristol-Myers SquibbActive, not recruitingMelanoma | Hepatocellular Carcinoma | Osteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Relapsed Pediatric Solid Tumor | Refractory Pediatric Solid TumorUnited States
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Spectrum Health HospitalsCompleted
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AeRang KimTerminatedOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Solid Tumors | Pediatric Cancer | Rhabdomyosarcoma | Wilms Tumor | Soft Tissue Sarcomas | Germ Cell Tumors | Hepatic TumorUnited States
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Joergen SerupSahlgrenska University Hospital, SwedenActive, not recruitingCutaneous NeurofibromaDenmark, Sweden
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University of BirminghamActive, not recruitingWolfram SyndromeFrance, United Kingdom, Poland, Spain
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AstraZenecaWithdrawnNeurofibromatosis Type 1 | Plexiform Neurofibromas | Post-operativeChina
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AeRang KimActive, not recruitingOsteosarcoma | Ewing Sarcoma | Neuroblastoma | Rhabdomyosarcoma | Wilms Tumor | Desmoid Tumor | Germ Cell Tumor | Relapsed Pediatric Solid Tumors | Refractory Pediatric Solid Tumors | Hepatic TumorUnited States
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Assistance Publique - Hôpitaux de ParisNational Research Agency, FranceCompletedRheumatoid Arthritis | Uveitis | Vasculitis | Type 1 Diabetes | Crohn's Disease | Myositis | Healthy Volunteer | Ankylosing Spondylitis | FMF | Systemic Lupus Erythematosus/Antiphospholipid Syndrome | Cryopyrin-Associated Periodic Syndromes /TNF-receptor Associated Periodic Syndrome | Ulcerative Rectocolitis | Unclassified...France
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Memorial Sloan Kettering Cancer CenterActive, not recruitingMesothelioma | Wilms Tumor | Pleural MesotheliomaUnited States
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Geisinger ClinicNational Human Genome Research Institute (NHGRI)Active, not recruitingLynch Syndrome | Familial Hypercholesterolemia | Hereditary Breast and Ovarian Cancer SyndromeUnited States
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Aristotle University Of ThessalonikiTerminatedCarcinosarcoma | Melanoma (Skin) | Basal Cell Carcinoma | Squamous Cell Carcinoma | Seborrheic Keratosis | Dysplastic Nevus Syndrome | Lentigo Maligna | Lichen Planus-Like KeratosisGreece
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Amsterdam UMC, location VUmcUniversity Hospital, Essen; Institut Curie; Ligue contre le cancer, FranceCompletedRetinoblastoma | Secondary Primary Malignancies After RetinoblastomaNetherlands, France, Germany
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ShireTakeda Development Center Americas, Inc.No longer availableAngioedema | Hereditary Angioedema (HAE)United States, Canada, Germany, Hungary, Spain
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, France, Israel, Netherlands, Poland, Puerto Rico, Spain, Sweden
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Abramson Cancer Center at Penn MedicineEnrolling by invitationOvarian Cancer | Genetic Predisposition to Disease | Breast Cancer Female | Hereditary Diseases | Gene Mutation-Related Cancer | Hereditary Breast and Ovarian Cancer | Hereditary Cancer SyndromeUnited States
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | HAEUnited States, Austria, Canada, Czechia, France, Germany, Hungary, North Macedonia, Romania, Spain, United Kingdom
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TakedaCompletedHereditary AngioedemaBelgium, Bulgaria, Estonia, Spain, Hungary, Israel, Germany, Czechia, Portugal, Greece, Lithuania, Poland, Latvia, Croatia, Slovakia, Austria, Canada, Ireland, North Macedonia, Romania, Serbia, Slovenia
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TakedaCompletedHereditary AngioedemaJapan
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Istituto Ortopedico RizzoliCompletedExostoses, Multiple HereditaryItaly
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BioCryst PharmaceuticalsCompletedHereditary Angioedema | Prophylaxis | HAEAustria, Denmark, France, Germany, Hungary, Israel, Italy, North Macedonia, Poland, Switzerland, United Kingdom, United States, Australia, Hong Kong, Korea, Republic of, New Zealand, Serbia, Slovakia, South Africa, Spain
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Eastern Cooperative Oncology GroupNational Cancer Institute (NCI)CompletedMelanoma (Skin)United States
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ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
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Oslo University HospitalEnrolling by invitation
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Janssen Research & Development, LLCCompletedAdenomatous Polyposis ColiUnited States, Germany, Korea, Republic of, France, Netherlands, Spain, Puerto Rico
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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Sol-Gel Technologies, Ltd.TerminatedBasal Cell Nevus SyndromeUnited States, France, Belgium, Denmark, Germany, Italy, Netherlands, Spain, United Kingdom
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University of Alabama at BirminghamCompletedNeurofibromatosis | Plexiform Neurofibromas | NF1United States
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BioCryst PharmaceuticalsActive, not recruitingHereditary Angioedema | HAEFrance, North Macedonia, Poland, Korea, Republic of, Slovakia, South Africa, Czechia
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Jonsson Comprehensive Cancer CenterBeiGene; Driven To CureWithdrawnMetastatic Renal Cell Carcinoma | Stage IV Renal Cell Cancer AJCC v8 | Papillary Renal Cell Carcinoma | Collecting Duct Carcinoma | Unresectable Renal Cell Carcinoma | Hereditary Leiomyomatosis and Renal Cell Carcinoma | Clear Cell Papillary Renal Neoplasm | Hereditary Papillary Renal Cell Carcinoma and other conditionsUnited States
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Vanderbilt UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1 | Reading DisabilitiesUnited States
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University Hospital, GrenobleCompletedHereditary AngioedemaFrance
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Duke UniversityNational Cancer Institute (NCI)CompletedBurkitt Lymphoma | Retinoblastoma | Diffuse Large B-cell LymphomaTanzania
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Murdoch Childrens Research InstituteCompletedHypertension | Blood Pressure | Neurofibromatosis 1Australia
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Talaris Therapeutics Inc.Duke UniversityTerminatedNiemann-Pick Disease | Alpha-mannosidosis | Tay Sachs Disease | Sandhoff Disease | Metachromatic Leukodystrophy (MLD) | Hurler-Scheie Syndrome | Hurler Syndrome (MPS I) | Hunter Syndrome (MPS II) | Sanfilippo Syndrome (MPS III) | Krabbe Disease (Globoid Leukodystrophy) | Adrenoleukodystrophy (ALD and AMN) | Pelizaeus...United States
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Mario Negri Institute for Pharmacological ResearchCompletedAlport SyndromeItaly
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Ionis Pharmaceuticals, Inc.CompletedHereditary AngioedemaUnited States, Netherlands
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Aucta Pharmaceuticals, IncTerminatedTuberous Sclerosis | Angiofibroma of FaceUnited States, China
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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National Cancer Institute (NCI)CompletedKidney CancerUnited States
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Assistance Publique - Hôpitaux de ParisCompletedNeurofibromatosis Type 1France
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Massachusetts Eye and Ear InfirmaryEnrolling by invitationDizziness | Neurofibromatosis 2 | Vestibular Schwannoma | Vestibular Disorder | Inner Ear DiseaseUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedIntraocular RetinoblastomaUnited States