- ICH GCP
- US Clinical Trials Registry
- Search trials
Search clinical trials for: Hereditary Transthyretin-mediated (hATTR) Amyloidosis
Total 3440 results
-
Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
-
Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
-
AstraZenecaRecruiting
-
Ionis Pharmaceuticals, Inc.CompletedHealthy Volunteers | hATTR AmyloidosisCanada
-
Akcea TherapeuticsRecruitingPregnancy | Hereditary Transthyretin-mediated Amyloidosis With PolyneropathyUnited States
-
Ionis Pharmaceuticals, Inc.RecruitingHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Italy, Portugal, Spain, Taiwan, Sweden, Canada, Brazil, France, New Zealand, Argentina, Cyprus, Australia, Turkey
-
The Cleveland ClinicActive, not recruitingAL Amyloidosis | Amyloidosis | Amyloid Neuropathies, Familial | Amyloid | Transthyretin Amyloidosis | Amyloid Cardiomyopathy | Amyloid - PrimaryUnited States
-
Alnylam PharmaceuticalsApproved for marketingAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
-
Alnylam PharmaceuticalsRecruitingPolyneuropathy | Hereditary Transthyretin-mediated (hATTR) AmyloidosisNetherlands, Spain, United States, Germany, France, Italy, Portugal
-
Alnylam PharmaceuticalsCompletedAmyloidosis, Familial | Transthyretin AmyloidosisFrance, Germany, Italy, Portugal, Spain, Sweden, United Kingdom
-
Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
-
CENTOGENE GmbH RostockAlnylam PharmaceuticalsRecruitingCardiomyopathies | Polyneuropathies | Transthyretin Amyloidosis | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyGermany, Austria, Switzerland
-
Alnylam PharmaceuticalsRecruitingTransthyretin-Mediated Amyloidosis | ATTR AmyloidosisIsrael, Italy, Netherlands, Spain, United States, France, Denmark, Germany, Portugal, Brazil, Taiwan
-
Alnylam PharmaceuticalsRecruitingHereditary Amyloidosis, Transthyretin-Related | Asymptomatic Carrier StateFrance
-
Rigshospitalet, DenmarkRecruitingPolyneuropathies | Diabetic Polyneuropathy | Chronic Inflammatory Demyelinating Polyneuropathy (CIDP) | POEMS Syndrome | Multifocal Motor Neuropathy | Charcot-Marie-Tooth | hATTR Amyloidosis | Vasculitic Neuropathy | Idiopathic NeuropathyDenmark
-
Alnylam PharmaceuticalsCompletedTransthyretin-mediated Amyloidosis (ATTR Amyloidosis)United Kingdom
-
AstraZenecaRecruitingCarpal Tunnel Syndrome | Amyloidosis | Polyneuropathy | Hereditary Transthyretin AmyloidosisRussian Federation
-
Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
-
UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
-
Virginia Commonwealth UniversityNot yet recruitingAmyloidosis, HereditaryUnited States
-
RwHealthNorthern Care Alliance NHS Foundation Trust; Alnylam PharmaceuticalsNot yet recruitingHereditary Amyloidosis | Guillain-Barre Syndrome | Chronic Inflammatory Demyelinating PolyneuropathyUnited Kingdom
-
Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
-
Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
-
Rennes University HospitalRecruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryFrance
-
National Institute of Allergy and Infectious Diseases...RecruitingObstructive Sleep Apnea | Sleep Disordered Breathing | Tonsillitis | Periodic Fever, Aphthous Stomatitis, Pharyngitis, And Cervical Adenitis (Pfapa) | Tonsil DisorderUnited States
-
Sanguine BiosciencesRecruitingHeart Diseases | Stroke | Lymphoma | Multiple Sclerosis | Kidney Diseases | Diabetes | Leukemia | Age-Related Macular Degeneration | Cancer | Arthritis | Schizophrenia | Thyroid Diseases | Parkinson Disease | Hepatitis | Vasculitis | Psoriasis | Asthma | Amyloidosis | Fibromyalgia | Graves Disease | Alzheimer Disease | Celiac Disease | Cirr... and other conditionsUnited States
-
University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
-
University of Sao Paulo General HospitalRecruitingMicrobial Colonization | Amyloidosis, Hereditary, Transthyretin-RelatedBrazil
-
University of Sao Paulo General HospitalFleuryNot yet recruitingAmyloid Neuropathies | Autonomic Nervous System DiseaseBrazil
-
PfizerCompletedPolyneuropathy | Hereditary Transthyretin Amyloidosis (ATTRv)Spain
-
National Institute of Allergy and Infectious Diseases...Active, not recruitingPGM3 Deficiency | Eosinophilic and/or Atopic Dermatitis | OSMR Deficiency | Primary Localized Cutaneous Amyloidosis | Hereditary Alpha-tryptasemiaUnited States
-
Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
-
Mayo ClinicActive, not recruitingAmyloidosis | Peripheral Neuropathy | Chronic Inflammatory Demyelinating Polyradiculoneuropathy | Vasculitic Neuropathy (Disorder) | Hereditary Neuropathy | Sarcoid NeuropathyUnited States
-
Ionis Pharmaceuticals, Inc.CompletedHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Spain, Taiwan, Italy, Germany, Argentina, Australia, Brazil, Canada, Cyprus, France, Greece, New Zealand, Portugal, Sweden, Turkey
-
University of PennsylvaniaAstraZeneca; Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary Amyloidosis, Transthyretin-RelatedUnited States
-
Alnylam PharmaceuticalsNo longer availableTransthyretin-mediated Amyloidosis With Cardiomyopathy | ATTR Amyloidosis With CardiomyopathyUnited States
-
Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
-
University of PennsylvaniaFox Chase Cancer CenterCompletedCardiovascular Diseases | Cancer | Hereditary Cancer | Hereditary Cardiac AmyloidosisUnited States
-
Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
-
PfizerCompletedHereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed PhenotypeUnited States
-
Alnylam PharmaceuticalsCompletedPolyneuropathy | Hereditary Transthyretin-mediated (ATTRv) AmyloidosisUnited States
-
Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
-
Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid PolyneuropathyUnited States
-
Novartis PharmaceuticalsCompletedHereditary Periodic Fevers | Systemic Juvenile Idiopathic ArthritisFrance
-
Ionis Pharmaceuticals, Inc.Approved for marketingAmyloidosis, Hereditary
-
Rabin Medical CenterUnknown
-
Novartis PharmaceuticalsCompletedPeriodic Fevers SyndromeJapan
-
Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
-
Novartis PharmaceuticalsCompletedHereditary Periodic FeversBelgium, Italy, Japan, Russian Federation, Turkey, Spain, Germany, United Kingdom, France, United States, Ireland, Israel, Canada, Hungary, Netherlands, Switzerland
-
Boston UniversityCompleted