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Search clinical trials for: Live Birth Rates
Total 52282 results
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University of FloridaRecruitingAlpha-1 Antitrypsin Deficiency | Cystic Fibrosis (CF) | AATD | AAT DeficiencyUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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McGill University Health Centre/Research Institute...RecruitingPeroxisome Biogenesis Disorder | Zellweger Spectrum Disorder | RCDP - Rhizomelic Chondrodysplasia Punctata | D-Bifunctional Protein Deficiency | Alpha-Methylacyl-CoA Racemase Deficiency | Peroxisomal Acyl-CoA Oxidase Deficiency | Peroxisomal Acyl-CoA Oxidase 2 Deficiency | ATP Binding Cassette Subfamily... and other conditionsCanada
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CHDI Foundation, Inc.RecruitingHuntington's DiseaseUnited States, Canada, Belgium, Spain, Australia, Germany, France, Netherlands, United Kingdom, New Zealand, Argentina, Austria, Chile, Colombia, Denmark, Ireland, Italy, Poland, Portugal, Switzerland
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Icahn School of Medicine at Mount SinaiRecruiting
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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University of FloridaRecruitingAlpha-1 Antitrypsin DeficiencyUnited States
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National Institute of Diabetes and Digestive and...RecruitingDiabetes | Cystic Fibrosis | Liver Disease or Abnormalities | Pancreatic Insufficiency (Exocrine and Endocrine)United States
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AmgenActive, not recruitingAtopic DermatitisKorea, Republic of, United States, Turkey, Hong Kong, United Kingdom, Australia, Brazil, Canada, Argentina
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TC Erciyes UniversityCompleted
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Australia, Belgium, Bulgaria, Canada, China, Denmark, France, Germany, Hungary, Italy, Korea, Republic of, Mexico, Netherlands, Poland, Portugal, Puerto Rico, Romania, Slovakia, South Africa, Spain, Sweden, Switzerland, Taiwa... and more
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W.L.Gore & AssociatesActive, not recruitingMigraine | Patent Foramen Ovale | PFO - Patent Foramen OvaleUnited States
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Alnylam PharmaceuticalsApproved for marketingAcute Hepatic Porphyria
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TC Erciyes UniversityCompletedFatigue | Anxiety | BirthTurkey
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National Cancer Institute (NCI)Active, not recruitingSoft Tissue Sarcoma | Renal Cell Carcinoma | Hepatocellular Carcinoma | Osteosarcoma | Ewing Sarcoma | Recurrent Renal Cell Carcinoma | Refractory Malignant Solid Neoplasm | Rhabdomyosarcoma | Recurrent Ewing Sarcoma | Recurrent Hepatoblastoma | Recurrent Malignant Solid Neoplasm | Recurrent Osteosarcoma | Recurrent... and other conditionsUnited States
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Zogenix, Inc.Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.Active, not recruitingDravet Syndrome | Epileptic Encephalopathy | Lennox Gastaut SyndromeUnited States, Australia, Belgium, Canada, Denmark, France, Germany, Italy, Mexico, Netherlands, Poland, Spain, Sweden, United Kingdom
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PTC TherapeuticsCooperative International Neuromuscular Research Group; The John Walton Muscular...Active, not recruitingMuscular Dystrophy, DuchenneGermany, France, United Kingdom, Brazil, Italy, Austria, Sweden, Czechia, Greece, Hungary, Israel, Latvia, Norway, Portugal, Romania, Slovenia
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Novartis PharmaceuticalsActive, not recruitingTuberous Sclerosis ComplexUnited States, Spain, Belgium, Taiwan, Turkey, Australia, Korea, Republic of, Thailand, France, Hungary, United Kingdom, Italy, Japan, Canada, Russian Federation, Poland, Mexico, Colombia
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisBelgium, Netherlands, Japan, Spain, Switzerland, United Kingdom, Germany, France, Austria, Russian Federation, Poland, Italy, Brazil, Finland
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University of Wisconsin, MadisonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Stanford...Completed
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Nordlandssykehuset HFThe Royal Norwegian Ministry of HealthActive, not recruitingAcute Intermittent PorphyriaNorway
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisCanada, France, United Kingdom, Israel, Australia, Spain, Germany, Netherlands, Denmark, Switzerland
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National Institute of Allergy and Infectious Diseases...Active, not recruitingImmune Deficiency | Eosinophilic Disease | HaTS | Urticaria Anaphylaxis | Elevated IgE LevelUnited States
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University of MichiganTerminatedObesity | Diabetes Mellitus Type 2 | Non Alcoholic Fatty Liver DiseaseUnited States
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Spanish Foundation for Neurometrics DevelopmentFundacion para la Salud Materno InfantilEnrolling by invitationSocial Behavior | Attention | EEG With Periodic Abnormalities | Visual Perceptual Weakness | Fluency DisorderUnited Kingdom
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Ultragenyx Pharmaceutical IncActive, not recruitingWilson DiseaseUnited States, Canada, Spain, Portugal, United Kingdom
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Assistance Publique - Hôpitaux de ParisActive, not recruitingReproductive MedicineFrance
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BayerUltragenix pharmaceuticalActive, not recruitingHemophilia ANetherlands, United States, Germany, United Kingdom, France, Bulgaria
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Royal College of Surgeons, IrelandThe Hospital for Sick Children; Imperial College London; Erasmus Medical Center; University College Dublin and other collaboratorsActive, not recruitingCystic Fibrosis | Adherence, Medication | Cystic Fibrosis Gastrointestinal Disease | Cystic Fibrosis in Children | Cystic Fibrosis Liver DiseaseUnited Kingdom, Ireland
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Manchester University NHS Foundation TrustCompletedCystic Fibrosis | Liver Fibroses | Cystic Fibrosis Liver DiseaseUnited Kingdom
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OrphalanCompletedWilson's DiseaseUnited Kingdom
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AlbireoActive, not recruitingAlagille SyndromeUnited Kingdom, United States, France, Germany, Netherlands, Italy, Belgium, Malaysia, Poland, Turkey
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UCB Biopharma SRLActive, not recruitingAtopic DermatitisBulgaria, Germany, Netherlands, United Kingdom
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Novo Nordisk A/SActive, not recruitingGrowth Hormone Deficiency in ChildrenUnited States, Korea, Republic of, United Kingdom, Canada, Russian Federation, India, Spain, Italy, Algeria, Austria, France, Ireland, Israel, Japan, Latvia, Poland, Serbia, Thailand, Ukraine, Germany, Slovenia, Switzerland
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Vertex Pharmaceuticals IncorporatedActive, not recruitingCystic FibrosisUnited States, United Kingdom, Canada, Australia, Germany
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Janssen Research & Development, LLCActive, not recruitingHemolytic Disease of the Fetus and NewbornUnited States, Canada, Netherlands, Belgium, Germany, Spain, Sweden, United Kingdom, Australia
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Vertex Pharmaceuticals IncorporatedActive, not recruitingAlpha-1 Antitrypsin DeficiencyUnited States, United Kingdom, Germany, Ireland
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Janssen Research & Development, LLCCompletedErythroblastosis, Fetal | Early Onset Severe Hemolytic Disease of the Fetus and Newborn (EOS-HDFN)United States, Canada, Netherlands, Belgium, Australia, Germany, Spain, Sweden, United Kingdom
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Alnylam PharmaceuticalsCompletedAmyloidosis, Familial | Transthyretin AmyloidosisFrance, Germany, Italy, Portugal, Spain, Sweden, United Kingdom
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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CSL BehringActive, not recruitingAlpha-1 Antitrypsin DeficiencyFrance
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Soleno Therapeutics, Inc.CompletedPrader-Willi SyndromeUnited States, United Kingdom
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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The University of Texas Medical Branch, GalvestonTerminatedHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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The University of Texas Medical Branch, GalvestonActive, not recruitingHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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Disc Medicine, IncActive, not recruitingErythropoietic ProtoporphyriaUnited States
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Barts & The London NHS TrustLiverpool Heart and Chest Hospital NHS Foundation Trust; Aortic Dissection...CompletedMarfan Syndrome | Marfan Syndrome Cardiovascular ManifestationsUnited Kingdom
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Murdoch Childrens Research InstituteUniversity of Sydney; Sydney Children's Hospitals Network; Women's and Children... and other collaboratorsActive, not recruitingAutosomal Recessive Disorder | X-Linked Genetic DiseasesAustralia
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Zealand PharmaActive, not recruitingCongenital HyperinsulinismUnited States, United Kingdom, Germany, Israel