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Search clinical trials for: Mucopolysaccharidosis type VII
Total 70935 results
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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Albert Einstein College of MedicineEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationMucopolysaccharidosis II | Fabry Disease | Niemann-Pick Disease, Type C | Mucopolysaccharidosis VI | Lysosomal Acid Lipase Deficiency | Metachromatic Leukodystrophy | Gaucher Disease | Cerebrotendinous Xanthomatosis | Mucopolysaccharidosis IV A | GM1 Gangliosidosis | Mucopolysaccharidosis VII | Acid Sphingomyelinase... and other conditionsUnited States
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIIUnited States, Brazil, Mexico, Portugal
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | MPS VII | MPS 7United States
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Ultragenyx Pharmaceutical IncCompletedMucopolysaccharidosis | Sly Syndrome | Mucopolysaccharidosis VII | MPS VIISpain, United States, Portugal
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VI | Mucopolysaccharidosis Type IV | Mucopolysaccharidosis Type VIIUnited States, Canada
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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Universidad de MurciaRecruitingPeriodontitis | Periodontal Diseases | Periodontal PocketSpain
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Alexandria UniversityRecruitingOvarian Epithelial CancerEgypt
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Vastra Gotaland RegionRegion Östergötland; Region Skane; Dalarna County Council, Sweden; Region Örebro... and other collaboratorsNot yet recruitingMelanoma | Surgery
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SanofiNot yet recruiting
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University of KentuckyNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Department...RecruitingDiabetes Mellitus, Type 2United States
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National University Hospital, SingaporeRecruiting
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University of ManitobaJuvenile Diabetes Research Foundation; Canadian Institutes of Health Research...Not yet recruitingPhysical Activity | Type 1 Diabetes
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City Clinical Oncology Hospital No 1Atlas Biomed; N.N. Blokhin National Medical Research Center of Oncology; Moscow...RecruitingColorectal Neoplasms | Chemotherapy Effect | Molecular Sequence VariationRussian Federation
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Castilla-La Mancha Health ServiceRecruitingObesity | Diabetes Mellitus, Type 2Spain
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University Health Network, TorontoRecruitingSuspected SarcoidosisCanada
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University Rovira i VirgiliNot yet recruitingBalance Disorders
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Fujian Medical University Union HospitalRecruitingSurgical Incision | Minimally Invasive SurgeryChina
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Ze-yang Ding, MDGeneplus-Beijing Co. Ltd.; Chinese Cooperative Group of Liver Cancer (CCGLC)RecruitingCholangiocarcinoma Non-resectableChina
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Affiliated Hospital of Nantong UniversityRecruiting
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis Type IIIAUnited States
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University of WashingtonBreast Cancer Research FoundationNot yet recruitingAnatomic Stage III Breast Cancer AJCC v8 | Anatomic Stage IV Breast Cancer AJCC v8 | Metastatic HER2-Negative Breast Carcinoma | Metastatic Hormone Receptor-Positive Breast Carcinoma | Locally Advanced Unresectable HER2-Negative Breast Carcinoma | Locally Advanced Unresectable Hormone Receptor-Positive...United States
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University of Southern CaliforniaNot yet recruitingVestibular Schwannoma
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Centre Leon BerardNETRIS PharmaRecruitingAcute Myeloid Leukemia RefractoryFrance
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Orchard TherapeuticsRecruitingMPS-IH (Hurler Syndrome)Netherlands, United States, Italy, United Kingdom
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Peking Union Medical CollegePeking University Hospital of StomatologyRecruitingPrecision Therapy | Locally Advanced or Recurrent/Metastatic Salivary Gland Carcinoma | Neoadjuvant or Conversion TherapyChina
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City of Hope Medical CenterNational Cancer Institute (NCI)Not yet recruitingBreast Carcinoma | Colorectal CarcinomaUnited States
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Xuekui LiuNot yet recruiting
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Hee Young JuRecruitingLymphoblastic Leukemia in ChildrenKorea, Republic of
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis III-AGermany
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Jiangsu Alphamab Biopharmaceuticals Co., LtdNot yet recruiting
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Frantz Viral Therapeutics, LLCThe Cleveland ClinicRecruitingVulvar Diseases | HPV Infection | Vulvar HSIL | High Grade Intraepithelial Neoplasia | HPV Disease | Pre-Cancerous Dysplasia | Vin II | Vin III | VIN, Usual Type | VIN 2 of Usual Type | VIN 3 of Usual Type | VIN Grade 2 | VIN Grade 3United States
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Verastem, Inc.GOG Foundation; European Network of Gynaecological Oncological Trial Groups...RecruitingLow Grade Serous Ovarian CancerUnited States, United Kingdom, Australia
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Fondazione Poliambulanza Istituto OspedalieroAssociazione Italiana per la Ricerca sul CancroRecruitingAmpullary AdenocarcinomaItaly
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Mayo ClinicRecruitingMalignant Solid Neoplasm | Lymphoma | Multiple Myeloma | Hematopoietic and Lymphoid System Neoplasm | Chronic LeukemiaUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...CelltrionRecruitingBowel Disease | Inflammatory Disease | Disease CrohnNetherlands
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Ministry of Health, Saudi ArabiaNot yet recruiting
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City of Hope Medical CenterNational Cancer Institute (NCI)RecruitingMantle Cell LymphomaUnited States
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First Affiliated Hospital of Zhejiang UniversityRecruitingAcute Myeloid Leukemia | Myelodysplastic SyndromesChina
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University of North Carolina, Chapel HillRecruitingGastroparesis | Delayed Gastric EmptyingUnited States
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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McGill University Health Centre/Research Institute...Diabetes CanadaRecruiting
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The First Hospital of Jilin UniversityCSPC Ouyi Pharmaceutical Co., Ltd.Not yet recruiting