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Search clinical trials for: Myotonic Dystrophy, Congenital
Total 9277 results
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IRCCS Eugenio MedeaRecruiting
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Assistance Publique - Hôpitaux de ParisNot yet recruitingHemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditionsFrance
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Laurent ServaisSYSNAVRecruitingDuchenne Muscular Dystrophy | Myotonic Dystrophy 1 | Congenital Muscular Dystrophy | Centronuclear Myopathy | Charcot-Marie-Tooth | Fascioscapulohumeral Muscular DystrophyBelgium
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Sanguine BiosciencesCompletedDepression | Melanoma | Epilepsy | Lymphoma | Multiple Sclerosis | Kidney Cancer | Cervical Cancer | Diabetes Mellitus | Leukemia | Breast Cancer | Chronic Kidney Diseases | Chronic Obstructive Pulmonary Disease | Parkinson's Disease | Systemic Lupus Erythematosus | Multiple Myeloma | Hepatitis B | Insomnia | Colorectal Cancer | HIV/AID... and other conditionsUnited States
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione... and other collaboratorsActive, not recruiting
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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University Hospital, MontpellierAgence de La BiomédecineActive, not recruitingFragile X Syndrome | Huntington Disease | Myotonic Dystrophy 1France
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ResMedClinical Trial Center North Hamburg Germany; CRI-The Clinical Research Institute...TerminatedPulmonary Disease, Chronic Obstructive | Amyotrophic Lateral Sclerosis | Muscular Dystrophies | Duchenne Muscular Dystrophy | Myotonic Dystrophy | Spinal Cord Injury | Obesity Hypoventilation Syndrome | Kyphoscoliosis | Congenital Central Hypoventilation Syndrome | MyopathiesGermany
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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Nantes University HospitalUniversity of Angers - Pays de la Loire psychology laboratoryNot yet recruitingCongenital Heart Defects | Neurodevelopmental DisorderFrance
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Teva takedaNot yet recruitingA Survey of Recombinant ADAMTS13 in Participants With Congenital Thrombotic Thrombocytopenic PurpuraThrombotic Thrombocytopenic Purpura (TTP)
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St. Jude Children's Research HospitalBioLineRx, Ltd.Not yet recruiting
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Sohag UniversityNot yet recruiting
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Assiut UniversityNot yet recruitingKidney Congenital Anomalies
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Novartis PharmaceuticalsNot yet recruiting
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Başakşehir Çam & Sakura City HospitalNot yet recruitingPectus ExcavatumTurkey
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Xuanwu Hospital, BeijingNot yet recruitingEpilepsy, Drug ResistantChina
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argenxNot yet recruiting
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West China HospitalRecruitingLymphatic MalformationChina
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Boston Children's HospitalNot yet recruitingThrombosis | Congenital Heart Disease | Single-ventricleUnited States
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Cantonal Hospital GraubuendenUniversity of ZurichNot yet recruitingAutosomal Dominant Polycystic Kidney DiseaseSwitzerland
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Novo Nordisk A/SNot yet recruitingHealthy Volunteers Sickle Cell Disease, ThalassemiaUnited States
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Assiut UniversityNot yet recruitingEKLF Mutations in Beta Thalassemia Patients
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Ankara Yildirim Beyazıt UniversityNot yet recruitingCongenital Heart Disease in AdolescenceTurkey
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University Hospital, MontpellierNot yet recruitingNeurodevelopmental Disorders | Congenital Heart Disease in ChildrenFrance
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Tanta UniversityRecruitingAtrial Septal Defect | Ketamine | General Anesthesia | Dexmedetomidine | Local InfiltrationEgypt
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University Hospital, CaenRecruitingEar MalformationFrance
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University of Sao PauloNot yet recruitingMolar Incisor Hypomineralization
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Stanford UniversityAmerican Heart AssociationNot yet recruitingAngina Pectoris | Microvascular Angina | Vasospastic Angina | Myocardial Bridge of Coronary ArteryUnited States
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Enyo PharmaRecruitingAlport SyndromeGermany, Spain, United States, France
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Assistance Publique - Hôpitaux de ParisNot yet recruitingCongenital Lung Malformations
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Simon AnnaheimUniversity Children's Hospital, ZurichRecruitingSkin Abnormalities | Skin; Injury, Superficial | Skin; Ulcer, DecubitusSwitzerland
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University of Texas Southwestern Medical CenterNational Institute on Disability, Independent Living, and Rehabilitation...Not yet recruitingPlagiocephaly | Brachycephaly | Deformational Plagiocephaly | Deformational Posterior Plagiocephaly
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DK Medical Technology (Suzhou) Co., Ltd.Not yet recruitingArteriovenous Fistula StenosisChina
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Rocket Pharmaceuticals Inc.Not yet recruitingPyruvate Kinase DeficiencySpain, United States
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Amryt PharmaChiesi Farmaceutici S.p.A.Not yet recruitingEpidermolysis Bullosa, Junctional | Epidermolysis Bullosa, Dystrophic
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Medical University of South CarolinaNot yet recruiting
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Regeneron PharmaceuticalsNot yet recruitingNon-transfusion Dependent Beta-thalassemia (NTDT)
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Children's Hospital of Fudan UniversityNot yet recruitingCongenital Heart Disease | Transition to Adult CareChina
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Zhujiang HospitalRecruitingCholedochal Cyst | Congenital Biliary DilatationChina
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University of St. Augustine for Health SciencesRecruitingSpina BifidaUnited States
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Necmi Kadıoğlu HospitalRecruitingChildren | Hypospadias | Hypospadias, Coronal | Caudal AnesthesiaNorth Macedonia, Russian Federation, Turkey