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Search clinical trials for: Neurodevelopmental disorder with progressive spasticity and brain white matter abnormalities
Total 479012 results
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University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
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Children's Hospital of PhiladelphiaEli Lilly and Company; University of Pennsylvania; Takeda; National Institute of... and other collaboratorsRecruitingMucopolysaccharidoses | Leukoencephalopathies | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2... and other conditionsUnited States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Children's Hospital of PhiladelphiaIllumina, Inc.Active, not recruitingMucopolysaccharidoses | Leukodystrophy | Adrenoleukodystrophy | Adrenomyeloneuropathy | X-linked Adrenoleukodystrophy | Gangliosidoses | Metachromatic Leukodystrophy | Krabbe Disease | Refsum Disease | Cadasil | Sjogren-Larsson Syndrome | Allan-Herndon-Dudley Syndrome | White Matter Disease | GM2 Gangliosidosis | Zellweger... and other conditionsUnited States
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Eli Lilly and CompanyRecruitingMental Disorders | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Neurocognitive Disorders | Neurodegenerative Diseases | Dementia | Alzheimer's DiseaseUnited States, United Kingdom
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Eli Lilly and CompanyRecruitingAlzheimer's DiseaseUnited States, Japan
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingCardiovascular Disease | Arterial Stiffness | Germline Mutation in the NOTCH 3 Gene | Pathogenesis of CADASIL | Clinical Phenotype of CADASILUnited States
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Fondazione I.R.C.C.S. Istituto Neurologico Carlo...RecruitingNeurologic Disorder | Rare Diseases | Metabolic Disease | Inherited Disease | Undiagnosed Disease | Neuro-Degenerative DiseaseItaly
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Myrtelle Inc.RecruitingCanavan DiseaseUnited States
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Mayo ClinicRecruitingCerebral Small Vessel Diseases | Cerebral Autosomal Dominant Arteriopathy With Subcortical Infarcts and Leukoencephalopathy | Cerebral Microbleeding | Sporadic White Matter DiseaseUnited States
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Leipzig University Medical CenterRecruitingX-linked AdrenoleukodystrophyGermany
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Dr. Rebecca SchuleGerman Research Foundation; German Center for Neurodegenerative Diseases (DZNE)RecruitingSpastic AtaxiaCanada, France, Germany, Italy, Netherlands, Turkey, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiovascular Disease | Arterial Stiffness | Germline Mutation in the NOTCH 3 Gene | Pathogenesis of CADASIL | Clinical Phenotype of CADASILUnited States
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Leipzig University Medical CenterEuropean Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyGermany
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University of OxfordUniversity College, LondonCompletedCognitive Impairment | Dementia | Affective DisordersUnited Kingdom
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University Medical Centre LjubljanaCompletedCerebral Palsy | Metabolism, Inborn Errors | Developmental Delay | Genetic DiseaseSlovenia
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First Affiliated Hospital Xi'an Jiaotong UniversityXijing Hospital; Shaanxi Provincial People's Hospital; Second Affiliated Hospital... and other collaboratorsUnknownEffect of Erythropoietin in Premature Infants on White Matter Lesions and Neurodevelopmental OutcomeCerebral Palsy | Intracranial Hemorrhages | Premature Infants | Periventricular LeukomalaciaChina
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationCompletedLate Infantile Metachromatic LeukodystrophyFrance
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University Hospital, RouenMinistry of Health, FranceCompletedBrain Ischemia | Preterm Birth | Intracranial Hemorrhages | Periventricular LeukomalaciaFrance
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IRCCS Eugenio MedeaMinistry of Health, ItalyRecruitingAutism Spectrum Disorder | NeuroinflammationItaly
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Johns Hopkins UniversityNational Center for Complementary and Integrative Health (NCCIH); Bowdoin CollegeRecruitingTourette Syndrome | Tic Disorders | Tourette's Disorder | Persistent Tic Disorder | Chronic Motor Tic Disorder | Chronic Vocal Tic Disorder | Persistent Motor Tic Disorder | Persistent Vocal Tic DisorderUnited States
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IRCCS Eugenio MedeaRecruitingEpilepsy | Angelman Syndrome | Dup15q SyndromeItaly
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Richard FryeNot yet recruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Neurological Disorder | EEG With Periodic AbnormalitiesUnited States
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Karamanoğlu Mehmetbey UniversityRecruitingWolff-Parkinson-White SyndromeTurkey
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Acumen PharmaceuticalsRecruitingAlzheimer DiseaseUnited States, France, Italy, Germany, Spain, Canada, Poland, United Kingdom
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Noema Pharma AGNot yet recruiting
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Karolinska InstitutetRecruitingTourette Syndrome | Chronic Tic DisorderSweden
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Université du Québec à ChicoutimiMcGill University; Université de Sherbrooke; University of Alberta; University... and other collaboratorsRecruitingAutosomal Recessive Spastic Ataxia of Charlevoix-Saguenay | Spastic Paraplegia 7Canada
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
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University Hospital, Clermont-FerrandNot yet recruiting
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Anagnostou, Evdokia, M.D.The Hospital for Sick Children; Canadian Institutes of Health Research (CIHR); Alberta Health services and other collaboratorsNot yet recruitingAnxiety Disorders | Generalized Anxiety Disorder | Anxiety | Tuberous Sclerosis | ADHD | Neurodevelopmental Disorders | Autism Spectrum Disorder | Fragile X Syndrome | Social Anxiety | Social Anxiety Disorder | Agoraphobia | Tourette Syndrome | Tic Disorders | Autism | ADHD Predominantly Inattentive Type | ADHD - Combined... and other conditionsCanada
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Emalex Biosciences Inc.RecruitingTourette SyndromeUnited States, Canada
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Beijing Tiantan HospitalNot yet recruitingMild Cognitive Impairment | Cerebral Small Vessel Diseases | Postmenopausal Symptoms | White Matter HyperintensityChina
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Novartis PharmaceuticalsRecruitingPolymyalgia RheumaticaUnited States, Australia, Germany, Belgium, France, Spain, Italy, Lebanon, Switzerland, Japan, Israel, Denmark, Argentina, Netherlands, Colombia, Chile, Hungary, Poland, Turkey, Czechia, Brazil, South Africa, Mexico, Canada, United Kingdom
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University of Texas at AustinHospital Clinic of Barcelona; Fundació Institut de Recerca de l'Hospital de...RecruitingNeurocognitive Disorders | Neurodegenerative Diseases | Dementia | Alzheimer Disease | Language Disorders | Communication Disorders | Primary Progressive Aphasia | Aphasia | Speech Disorders | Frontotemporal Lobar Degeneration | Dysarthria | Apraxia, Motor | Dementia, Frontotemporal | Bilingual AphasiaSpain, United States
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University Hospital, BordeauxRecruitingIntellectual Disability | Cystic Fibrosis | Neurodegeneration With Brain Iron Accumulation (NBIA) | Congenital Heart Defect | Albinism | Rubinstein-Taybi Syndrome | Periventricular Nodular HeterotopiaFrance
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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University Hospital, Basel, SwitzerlandEuropean Pain FederationRecruitingCentral Post-stroke PainSwitzerland
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Kuwait UniversityNot yet recruitingCerebral Palsy | Neurodevelopmental DisordersKuwait
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Cognito Therapeutics, Inc.RecruitingCognitive Impairment | Dementia | Alzheimer Disease | Mild Cognitive Impairment | Cognitive Decline | Alzheimer Disease, Early Onset | Alzheimer Disease, Late Onset | MCI | Dementia Alzheimers | Mild Dementia | Dementia of Alzheimer Type | Cognitive Impairment, Mild | Alzheimer Disease 1 | Dementia, Mild | Alzheimer... and other conditionsUnited States
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National Taipei University of Nursing and Health...Ministry of Science and Technology, Taiwan; Chang Gung Children's HospitalRecruitingDepression | Tourette Syndrome in Adolescence | Mental Health Issue | Social AdjustmentTaiwan
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University of California, Los AngelesBrain & Behavior Research FoundationRecruitingInsomnia | Tourette's DisorderUnited States
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Tasly Pharmaceuticals, Inc.Not yet recruitingTourette Syndrome in Children | Tourette Syndrome in AdolescenceUnited States
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Tasly Pharmaceuticals, Inc.Not yet recruitingTourette SyndromeUnited States
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MapLight TherapeuticsRecruitingAutism Spectrum DisorderUnited States, Australia, Canada
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Assistance Publique - Hôpitaux de ParisRecruitingSpinocerebellar Ataxias | Inherited Movement Disorders | Hyperkinetic DisordersFrance
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Eli Lilly and CompanyRecruitingAlzheimer DiseaseUnited States, Japan, Puerto Rico
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States