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Search clinical trials for: Progressive Myoclonic Epilepsy
Total 4703 results
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University College, LondonUniversity of North Carolina, Chapel Hill; NYU Grossman School of MedicineRecruitingDentatorubral-Pallidoluysian AtrophyUnited States, United Kingdom
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Autifony Therapeutics LimitedRecruitingMyoclonus Epilepsies, ProgressiveUnited States
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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Columbia UniversityNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial Disorders | Mitochondrial Genetic Disorders | Disorder of Mitochondrial Respiratory Chain Complexes | Deletion and Duplication of Mitochondrial DNAUnited States, Canada
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RTI InternationalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsEnrolling by invitationPrimary Hyperoxaluria Type 3 | Diabetes Mellitus | Hemophilia A | Hemophilia B | Hereditary Fructose Intolerance | Cystic Fibrosis | Factor VII Deficiency | Phenylketonurias | Sickle Cell Disease | Dravet Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Chronic Granulomatous Disease and other conditionsUnited States
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UCB PharmaCompletedUnverricht-Lundborg DiseaseUnited States, Canada, Finland, France, Israel, Russian Federation, Serbia, Tunisia
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Ionis Pharmaceuticals, Inc.CompletedLafora DiseaseUnited States, Italy, Spain
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Azienda Socio Sanitaria Territoriale di MantovaUnknownUnverricht-Lundborg Disease
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National Human Genome Research Institute (NHGRI)CompletedFamilial Dementia With Neuroserpin Inclusion Bodies | Nervous System Heredodegenerative DisorderUnited States
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UCB Pharma SACompletedUnverricht-Lundborg DiseaseFrance, Italy, Sweden, Finland, Netherlands, Tunisia, Réunion
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University of TurkuUnknownUnverricht-Lundborg SyndromeFinland
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National Institute of Neurological Disorders and...Completed
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TakedaNot yet recruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)
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TC Erciyes UniversityRecruitingEpilepsy in ChildrenTurkey
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Encoded TherapeuticsRecruiting
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UCB BIOSCIENCES, Inc.Recruiting
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Encoded TherapeuticsRecruiting
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TakedaRecruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)Spain
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Omeicos Therapeutics GmbHRecruitingPrimary Mitochondrial DiseaseGermany, Italy
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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Cook Children's Health Care SystemEncoded TherapeuticsRecruiting
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Sanguine BiosciencesRecruitingHeart Diseases | Stroke | Lymphoma | Multiple Sclerosis | Kidney Diseases | Diabetes | Leukemia | Age-Related Macular Degeneration | Cancer | Arthritis | Schizophrenia | Thyroid Diseases | Parkinson Disease | Hepatitis | Vasculitis | Psoriasis | Asthma | Amyloidosis | Fibromyalgia | Graves Disease | Alzheimer Disease | Celiac Disease | Cirr... and other conditionsUnited States
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Longboard PharmaceuticalsRecruitingDravet Syndrome | Lennox-Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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University Health Network, TorontoZogenix, Inc.Not yet recruiting
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BiocodexRecruitingDravet SyndromeUnited States
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Jazz PharmaceuticalsEvidilya S.r.l.Not yet recruitingDravet Syndrome | Lennox Gastaut SyndromeItaly
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Hospices Civils de LyonRecruitingEpilepsy | Dravet SyndromeBelgium, France, Germany
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Encoded TherapeuticsRecruiting
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TakedaRecruitingLennox Gastaut Syndrome (LGS) | Dravet Syndrome (DS)United States, China, Spain, France, Belgium, Australia, Brazil, Canada, Germany, Greece, Hungary, Italy, Japan, Latvia, Netherlands, Poland, Serbia, Mexico, Russian Federation, Ukraine
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Aga Khan UniversityNational Institute of Child Health, Karachi, PakistanNot yet recruiting
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Assistance Publique - Hôpitaux de ParisOrphelia PharmaNot yet recruitingEpilepsy | Dravet Syndrome | West SyndromeFrance
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Jazz PharmaceuticalsRecruitingTuberous Sclerosis Complex | Dravet Syndrome | Lennox Gastaut SyndromeUnited States
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Boston Children's HospitalEncoded TherapeuticsRecruitingDravet SyndromeUnited States
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Eisai Inc.RecruitingEpilepsies, MyoclonicUnited States, Canada
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Jazz PharmaceuticalsRecruitingSeizure in Participants With Tuberous Sclerosis Complex | Seizure in Participants With Dravet Syndrome | Seizure in Participants With Lennox-Gastaut SyndromeUnited States
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EpygenixForest Hills Lab; Liberyx TherapeuticsRecruitingDravet SyndromeUnited States, Canada, Spain, Georgia, Hungary
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Centre Hospitalier Universitaire, AmiensUniversity Hospital, Rouen; University Hospital, LilleRecruitingEpileptic Syndromes | Learning Disabilities | Doose SyndromeFrance
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King's College LondonKing's College Hospital NHS Trust; Charles University, Czech Republic; Hopital... and other collaboratorsRecruitingJuvenile Myoclonic EpilepsyUnited States, Canada, Czechia, Denmark, Estonia, France, Italy, Norway, United Kingdom
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Boston Children's HospitalRecruitingEpilepsy | Dravet Syndrome | Infantile Spasms | Epileptic Encephalopathy | Ohtahara Syndrome | Early Myoclonic Epileptic Encephalopathy | PCDH19-related Epilepsy and Related Conditions | KCNQ2-Related Epileptic Encephalopathy | Epilepsy of Infancy With Migrating Focal Seizures (Disorder)United States
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Sanford HealthNational Ataxia Foundation; Beyond Batten Disease Foundation; Pitt Hopkins Research... and other collaboratorsRecruitingMitochondrial Diseases | Retinitis Pigmentosa | Myasthenia Gravis | Eosinophilic Gastroenteritis | Multiple System Atrophy | Leiomyosarcoma | Leukodystrophy | Anal Fistula | Spinocerebellar Ataxia Type 3 | Friedreich Ataxia | Kennedy Disease | Lyme Disease | Hemophagocytic Lymphohistiocytosis | Spinocerebellar Ataxia... and other conditionsUnited States, Australia
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Zogenix, Inc.Zogenix International Limited, Inc., a subsidiary of Zogenix, Inc.Active, not recruitingDravet Syndrome | Epileptic Encephalopathy | Lennox Gastaut SyndromeUnited States, Australia, Belgium, Canada, Denmark, France, Germany, Italy, Mexico, Netherlands, Poland, Spain, Sweden, United Kingdom
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TakedaCompletedDravet Syndrome (DS)China, Canada, France, Hungary, Poland, United States, Spain, Greece, Australia, Brazil, Serbia, Germany, Italy, Japan, Latvia, Netherlands, Ukraine, Russian Federation
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Stoke Therapeutics, IncCompleted
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Fondazione Policlinico Universitario Agostino Gemelli...IRCCS San RaffaeleEnrolling by invitation
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Longboard PharmaceuticalsAvailableDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathiesUnited States
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TakedaActive, not recruitingEpilepsy | Dravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)United States, Canada, Australia, China, Israel, Poland, Spain, Portugal
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Longboard PharmaceuticalsCompletedDravet Syndrome | Lennox Gastaut Syndrome | Developmental and Epileptic EncephalopathyUnited States, Australia
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University of OxfordZogenix International Limited, Inc., a subsidiary of Zogenix, Inc.WithdrawnDepression | Anxiety | Dravet Syndrome
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University of British ColumbiaTerminatedJuvenile Myoclonic Epilepsy | Childhood Absence Epilepsy | Juvenile Absence EpilepsyCanada